How can we deliver on the promise of precision medicine in oncology and beyond? A practical roadmap for action
Baird, Anne‐Marie, Westphalen, C. Benedikt, Blum, Sandra, Nafria, Begonya, Knott, Tanya, Sargeant, Ify, Harnik, Helena, Brooke, Nicholas, Wicki, Nicole, Wong‐Rieger, Durhane
Published in Health science reports (01.06.2023)
Published in Health science reports (01.06.2023)
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Journal Article
Review of 11 national policies for rare diseases in the context of key patient needs
Dharssi, Safiyya, Wong-Rieger, Durhane, Harold, Matthew, Terry, Sharon
Published in Orphanet journal of rare diseases (31.03.2017)
Published in Orphanet journal of rare diseases (31.03.2017)
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Journal Article
An international comparative analysis of public reimbursement of orphan drugs in Canadian provinces compared to European countries
Ward, Leanne Marie, Chambers, Alexandra, Mechichi, Emine, Wong-Rieger, Durhane, Campbell, Craig
Published in Orphanet journal of rare diseases (04.03.2022)
Published in Orphanet journal of rare diseases (04.03.2022)
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Journal Article
Research on rare diseases: ten years of progress and challenges at IRDiRC
Monaco, Lucia, Zanello, Galliano, Baynam, Gareth, Jonker, Anneliene H., Julkowska, Daria, Hartman, Adam L., O’Connor, Daniel, Wang, Chiuhui Mary, Wong-Rieger, Durhane, Pearce, David A.
Published in Nature reviews. Drug discovery (01.05.2022)
Published in Nature reviews. Drug discovery (01.05.2022)
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Journal Article
Essential list of medicinal products for rare diseases: recommendations from the IRDiRC Rare Disease Treatment Access Working Group
Gahl, William A, Wong-Rieger, Durhane, Hivert, Virginie, Yang, Rachel, Zanello, Galliano, Groft, Stephen
Published in Orphanet journal of rare diseases (13.07.2021)
Published in Orphanet journal of rare diseases (13.07.2021)
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Journal Article
Strengthening health systems for access to gene therapy in rare genetic disorders
Bhatia, Sonal, Le Cam, Yann, Carrion, Juan, Diamond, Lauren, Fennessy, Paul, Gassman, Safiyya, Gutzwiller, Felix, Kagan, Stephen, Pankevich, Diana, Young Maloney, Jennifer, Mahadev, Nitin, Schulz, Martin, Wong-Rieger, Durhane, Morgese, Paolo
Published in Molecular therapy. Methods & clinical development (13.06.2024)
Published in Molecular therapy. Methods & clinical development (13.06.2024)
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Journal Article
Health Coaching in Diabetes: Empowering Patients to Self-Manage
Wong-Rieger, Durhane, PhD, Rieger, Francis P., PhD
Published in Canadian journal of diabetes (01.02.2013)
Published in Canadian journal of diabetes (01.02.2013)
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Journal Article
Validation and reliability of a disease‐specific quality of life measure (the TranQol) in adults and children with thalassaemia major
Klaassen, Robert J., Barrowman, Nicholas, Merelles‐Pulcini, Manuela, Vichinsky, Elliott P., Sweeters, Nancy, Kirby‐Allen, Melanie, Neufeld, Ellis J., Kwiatkowski, Janet L., Wu, John, Vickars, Linda, Blanchette, Victor S., Forgie, Melissa, Yamashita, Robert, Wong‐Rieger, Durhane, Young, Nancy L.
Published in British journal of haematology (01.02.2014)
Published in British journal of haematology (01.02.2014)
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Journal Article
Model consent clauses for rare disease research
Nguyen, Minh Thu, Goldblatt, Jack, Isasi, Rosario, Jagut, Marlene, Jonker, Anneliene Hechtelt, Kaufmann, Petra, Ouillade, Laetitia, Molnar-Gabor, Fruszina, Shabani, Mahsa, Sid, Eric, Tassé, Anne Marie, Wong-Rieger, Durhane, Knoppers, Bartha Maria
Published in BMC medical ethics (01.08.2019)
Published in BMC medical ethics (01.08.2019)
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Journal Article
Quality Indicators as a Tool in Improving the Introduction of New Medicines
Campbell, Stephen M., Godman, Brian, Diogene, Eduardo, Fürst, Jurij, Gustafsson, Lars L., MacBride‐Stewart, Sean, Malmström, Rickard E., Pedersen, Hanne, Selke, Gisbert, Vlahović‐Palčevski, Vera, Woerkom, Menno, Wong‐Rieger, Durhane, Wettermark, Björn
Published in Basic & clinical pharmacology & toxicology (01.02.2015)
Published in Basic & clinical pharmacology & toxicology (01.02.2015)
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Journal Article
Returning incidental findings from genetic research to children: views of parents of children affected by rare diseases
Kleiderman, Erika, Knoppers, Bartha Maria, Fernandez, Conrad V, Boycott, Kym M, Ouellette, Gail, Wong-Rieger, Durhane, Adam, Shelin, Richer, Julie, Avard, Denise
Published in Journal of medical ethics (01.10.2014)
Published in Journal of medical ethics (01.10.2014)
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Journal Article
Familial hypercholesterolaemia patient support groups and advocacy: A multinational perspective
Payne, Jules, Williams, Simon, Maxwell, Diana, Pariente, Ma Teresa, Olivares, Raquel Arroyo, Janssen ten Haaf, Marlieke, Wong-Rieger, Durhane, Rieger, Fritz, Covato, Angela, Wong-Rieger, Hilary, Cermakova, Luba, Wilemon, Katherine
Published in Atherosclerosis (01.10.2018)
Published in Atherosclerosis (01.10.2018)
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Journal Article