Correction of the F508del-CFTR protein processing defect in vitro by the investigational drug VX-809
Van Goor, Fredrick, Hadida, Sabine, Grootenhuis, Peter D. J, Burton, Bill, Stack, Jeffrey H, Straley, Kimberly S, Decker, Caroline J, Miller, Mark, McCartney, Jason, Olson, Eric R, Wine, Jeffrey J, Frizzell, Ray A, Ashlock, Melissa, Negulescu, Paul A
Published in Proceedings of the National Academy of Sciences - PNAS (15.11.2011)
Published in Proceedings of the National Academy of Sciences - PNAS (15.11.2011)
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The normal trachea is cleaned by MUC5B mucin bundles from the submucosal glands coated with the MUC5AC mucin
Ermund, Anna, Meiss, Lauren N., Rodriguez-Pineiro, Ana M., Bähr, Andrea, Nilsson, Harriet E., Trillo-Muyo, Sergio, Ridley, Caroline, Thornton, David J., Wine, Jeffrey J., Hebert, Hans, Klymiuk, Nikolai, Hansson, Gunnar C.
Published in Biochemical and biophysical research communications (21.10.2017)
Published in Biochemical and biophysical research communications (21.10.2017)
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Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770
Van Goor, Fredrick, Hadida, Sabine, Grootenhuis, Peter D.J, Burton, Bill, Cao, Dong, Neuberger, Tim, Turnbull, Amanda, Singh, Ashvani, Joubran, John, Hazlewood, Anna, Zhou, Jinglan, McCartney, Jason, Arumugam, Vijayalaksmi, Decker, Caroline, Yang, Jennifer, Young, Chris, Olson, Eric R, Wine, Jeffery J, Frizzell, Raymond A, Ashlock, Melissa, Negulescu, Paul
Published in Proceedings of the National Academy of Sciences - PNAS (03.11.2009)
Published in Proceedings of the National Academy of Sciences - PNAS (03.11.2009)
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Journal Article
High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia
Vaidyanathan, Sriram, Salahudeen, Ameen A., Sellers, Zachary M., Bravo, Dawn T., Choi, Shannon S., Batish, Arpit, Le, Wei, Baik, Ron, de la O, Sean, Kaushik, Milan P., Galper, Noah, Lee, Ciaran M., Teran, Christopher A., Yoo, Jessica H., Bao, Gang, Chang, Eugene H., Patel, Zara M., Hwang, Peter H., Wine, Jeffrey J., Milla, Carlos E., Desai, Tushar J., Nayak, Jayakar V., Kuo, Calvin J., Porteus, Matthew H.
Published in Cell stem cell (06.02.2020)
Published in Cell stem cell (06.02.2020)
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Disease phenotype of a ferret CFTR-knockout model of cystic fibrosis
Sun, Xingshen, Sui, Hongshu, Fisher, John T, Yan, Ziying, Liu, Xiaoming, Cho, Hyung-Ju, Joo, Nam Soo, Zhang, Yulong, Zhou, Weihong, Yi, Yaling, Kinyon, Joann M, Lei-Butters, Diana C, Griffin, Michelle A, Naumann, Paul, Luo, Meihui, Ascher, Jill, Wang, Kai, Frana, Timothy, Wine, Jeffrey J, Meyerholz, David K, Engelhardt, John F
Published in The Journal of clinical investigation (01.09.2010)
Published in The Journal of clinical investigation (01.09.2010)
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Progress in understanding mucus abnormalities in cystic fibrosis airways
Wine, Jeffrey J., Hansson, Gunnar C., König, Peter, Joo, Nam Soo, Ermund, Anna, Pieper, Mario
Published in Journal of cystic fibrosis (01.03.2018)
Published in Journal of cystic fibrosis (01.03.2018)
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Variation in CFTR-dependent 'β-sweating' among healthy adults
DeRose, Lesje, Kim, Jeeyeon, Farahmand, Miesha, Shinbashi, Meagan Y, Joo, Nam Soo, Wine, Jeffrey J
Published in PloS one (01.03.2022)
Published in PloS one (01.03.2022)
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Journal Article
Hyposecretion of fluid from tracheal submucosal glands of CFTR-deficient pigs
Joo, Nam Soo, Cho, Hyung-Ju, Khansaheb, Monal, Wine, Jeffrey J
Published in The Journal of clinical investigation (01.09.2010)
Published in The Journal of clinical investigation (01.09.2010)
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Journal Article
Granule-stored MUC5B mucins are packed by the non-covalent formation of N-terminal head-to-head tetramers
Trillo-Muyo, Sergio, Nilsson, Harriet E., Recktenwald, Christian V., Ermund, Anna, Ridley, Caroline, Meiss, Lauren N., Bähr, Andrea, Klymiuk, Nikolai, Wine, Jeffrey J., Koeck, Philip J.B., Thornton, David J., Hebert, Hans, Hansson, Gunnar C.
Published in The Journal of biological chemistry (13.04.2018)
Published in The Journal of biological chemistry (13.04.2018)
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Evaporimeter and Bubble-Imaging Measures of Sweat Gland Secretion Rates
Kim, Jeeyeon, Farahmand, Miesha, Dunn, Colleen, Davies, Zoe, Frisbee, Eric, Milla, Carlos, Wine, Jeffrey J
Published in PloS one (21.10.2016)
Published in PloS one (21.10.2016)
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Proteomic analysis of pure human airway gland mucus reveals a large component of protective proteins
Joo, Nam Soo, Evans, Idil Apak T, Cho, Hyung-Ju, Park, Il-Ho, Engelhardt, John F, Wine, Jeffrey J
Published in PloS one (23.02.2015)
Published in PloS one (23.02.2015)
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Journal Article
In vivo readout of CFTR function: ratiometric measurement of CFTR-dependent secretion by individual, identifiable human sweat glands
Wine, Jeffrey J, Char, Jessica E, Chen, Jonathan, Cho, Hyung-Ju, Dunn, Colleen, Frisbee, Eric, Joo, Nam Soo, Milla, Carlos, Modlin, Sara E, Park, Il-Ho, Thomas, Ewart A C, Tran, Kim V, Verma, Rohan, Wolfe, Marlene H
Published in PloS one (24.10.2013)
Published in PloS one (24.10.2013)
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Journal Article
A little CFTR goes a long way: CFTR-dependent sweat secretion from G551D and R117H-5T cystic fibrosis subjects taking ivacaftor
Char, Jessica E, Wolfe, Marlene H, Cho, Hyung-Ju, Park, Il-Ho, Jeong, Jin Hyeok, Frisbee, Eric, Dunn, Colleen, Davies, Zoe, Milla, Carlos, Moss, Richard B, Thomas, Ewart A C, Wine, Jeffrey J
Published in PloS one (10.02.2014)
Published in PloS one (10.02.2014)
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Journal Article
The magnitude of ivacaftor effects on fluid secretion via R117H-CFTR channels: Human in vivo measurements
Char, Jessica E, Dunn, Colleen, Davies, Zoe, Milla, Carlos, Moss, Richard B, Wine, Jeffrey J
Published in PloS one (18.04.2017)
Published in PloS one (18.04.2017)
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