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Measuring the impact of newborn screening on survival after hematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium

by Thakar, Monica S., Logan, Brent R., Puck, Jennifer M., Dunn, Elizabeth A., Buckley, Rebecca H., Cowan, Morton J., O’Reilly, Richard J., Kapoor, Neena, Satter, Lisa Forbes, Pai, Sung-Yun, Heimall, Jennifer, Chandra, Sharat, Ebens, Christen L., Chellapandian, Deepak, Williams, Olatundun, Burroughs, Lauri M., Saldana, Blachy Davila, Rayes, Ahmad, Madden, Lisa M., Chandrakasan, Shanmuganathan, Bednarski, Jeffrey J., DeSantes, Kenneth B., Cuvelier, Geoffrey D. E., Teira, Pierre, Gillio, Alfred P., Eissa, Hesham, Knutsen, Alan P., Goldman, Frederick D., Aquino, Victor M., Shereck, Evan B., Moore, Theodore B, Caywood, Emi H., Vander Lugt, Mark T., Rozmus, Jacob, Broglie, Larisa, Yu, Lolie C., Shah, Ami J., Andolina, Jeffrey R., Liu, Xuerong, Parrott, Roberta E., Dara, Jasmeen, Prockop, Susan, Martinez, Caridad A., Kapadia, Malika, Jyonouchi, Soma C., Sullivan, Kathleen E., Bleesing, Jack J., Chaudhury, Sonali, Petrovic, Aleksandra, Keller, Michael D., Quigg, Troy C., Parikh, Suhag, Shenoy, Shalini, Seroogy, Christine, Rubin, Tamar, Decaluwe, Hélène, Routes, John M., Torgerson, Troy R., Leiding, Jennifer W., Pulsipher, Michael A., Kohn, Donald B., Griffith, Linda M., Haddad, Elie, Dvorak, Christopher C., Notarangelo, Luigi D.
Published in The Lancet (British edition) (20.06.2023)

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