Structural and microstructural neuroimaging signature of C9orf72-associated ALS: A multiparametric MRI study
Wiesenfarth, Maximilian, Huppertz, Hans-Jürgen, Dorst, Johannes, Lulé, Dorothée, Ludolph, Albert C., Müller, Hans-Peter, Kassubek, Jan
Published in NeuroImage clinical (01.01.2023)
Published in NeuroImage clinical (01.01.2023)
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Journal Article
Neurological manifestation of HEV infection: still a rare disease entity?
Wiesenfarth, Maximilian, Stamminger, Thomas, Zizer, Eugen, Tumani, Hayrettin, Ludolph, Albert C.
Published in Journal of neurology (01.01.2024)
Published in Journal of neurology (01.01.2024)
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Journal Article
Clinical and patient‐reported outcomes and neurofilament response during tofersen treatment in SOD1‐related ALS—A multicenter observational study over 18months
Meyer, Thomas, Schumann, Peggy, Weydt, Patrick, Petri, Susanne, Weishaupt, Jochen H, Weyen, Ute, Koch, Jan C, Günther, René, Regensburger, Martin, Boentert, Matthias, Wiesenfarth, Maximilian, Koc, Yasemin, Kolzarek, Felix, Kettemann, Dagmar, Norden, Jenny, Bernsen, Sarah, Elmas, Zeynep, Conrad, Julian, Valkadinov, Ivan, Vidovic, Maximilian, Dorst, Johannes, Ludolph, Albert C, Jasper Hesebeck‐Brinckmann, Spittel, Susanne, Münch, Christoph, Maier, André, Körtvélyessy, Péter
Published in Muscle & nerve (01.09.2024)
Published in Muscle & nerve (01.09.2024)
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Journal Article
Clinical and patient‐reported outcomes and neurofilament response during tofersen treatment in SOD1‐related ALS—A multicenter observational study over 18 months
Meyer, Thomas, Schumann, Peggy, Weydt, Patrick, Petri, Susanne, Weishaupt, Jochen H., Weyen, Ute, Koch, Jan C., Günther, René, Regensburger, Martin, Boentert, Matthias, Wiesenfarth, Maximilian, Koc, Yasemin, Kolzarek, Felix, Kettemann, Dagmar, Norden, Jenny, Bernsen, Sarah, Elmas, Zeynep, Conrad, Julian, Valkadinov, Ivan, Vidovic, Maximilian, Dorst, Johannes, Ludolph, Albert C., Hesebeck‐Brinckmann, Jasper, Spittel, Susanne, Münch, Christoph, Maier, André, Körtvélyessy, Péter
Published in Muscle & nerve (01.09.2024)
Published in Muscle & nerve (01.09.2024)
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Journal Article
Clinical characterization of common pathogenic variants of SOD1-ALS in Germany
Wiesenfarth, Maximilian, ouhideh-Wiesenfarth, Yalda, Elmas, Zeynep, Parlak, Özlem, Weiland, Ulrike, Herrmann, Christine, Schuster, Joachim, Freischmidt, Axel, Müller, Kathrin, Siebert, Reiner, Günther, Kornelia, Fröhlich, Elke, Knehr, Antje, Simak, Tatiana, Bachhuber, Franziska, Regensburger, Martin, Petri, Susanne, Klopstock, Thomas, Reilich, Peter, Schöberl, Florian, Schumann, Peggy, Körtvélyessy, Peter, Meyer, Thomas, Ruf, Wolfgang P, Witzel, Simon, Tumani, Hayrettin, Brenner, David, Dorst, Johannes, Ludolph, Albert C
Published in Journal of neurology (14.08.2024)
Published in Journal of neurology (14.08.2024)
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Journal Article
Metabolic alterations precede neurofilament changes in presymptomatic ALS gene carriers
Dorst, Johannes, Weydt, Patrick, Brenner, David, Witzel, Simon, Kandler, Katharina, Huss, André, Herrmann, Christine, Wiesenfarth, Maximilian, Knehr, Antje, Günther, Kornelia, Müller, Kathrin, Weishaupt, Jochen H., Prudlo, Johannes, Forsberg, Karin, Andersen, Peter M., Rosenbohm, Angela, Schuster, Joachim, Roselli, Francesco, Dupuis, Luc, Mayer, Benjamin, Tumani, Hayrettin, Kassubek, Jan, Ludolph, Albert C.
Published in EBioMedicine (01.04.2023)
Published in EBioMedicine (01.04.2023)
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Journal Article
A randomized double-blind clinical trial on safety and efficacy of tauroursodeoxycholic acid (TUDCA) as add-on treatment in patients affected by amyotrophic lateral sclerosis (ALS): the statistical analysis plan of TUDCA-ALS trial
Lombardo, Flavia L, Spila Alegiani, Stefania, Mayer, Flavia, Cipriani, Marta, Lo Giudice, Maria, Ludolph, Albert Christian, McDermott, Christopher J, Corcia, Philippe, Van Damme, Philip, Van den Berg, Leonard H, Hardiman, Orla, Nicolini, Gabriele, Vanacore, Nicola, Dickie, Brian, Albanese, Alberto, Puopolo, Maria
Published in Current controlled trials in cardiovascular medicine (05.12.2023)
Published in Current controlled trials in cardiovascular medicine (05.12.2023)
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Journal Article
Effects of tofersen treatment in patients with SOD1-ALS in a “real-world” setting – a 12-month multicenter cohort study from the German early access program
Wiesenfarth, Maximilian, Dorst, Johannes, Brenner, David, Elmas, Zeynep, Parlak, Özlem, Uzelac, Zeljko, Kandler, Katharina, Mayer, Kristina, Weiland, Ulrike, Herrmann, Christine, Schuster, Joachim, Freischmidt, Axel, Müller, Kathrin, Siebert, Reiner, Bachhuber, Franziska, Simak, Tatiana, Günther, Kornelia, Fröhlich, Elke, Knehr, Antje, Regensburger, Martin, German, Alexander, Petri, Susanne, Grosskreutz, Julian, Klopstock, Thomas, Reilich, Peter, Schöberl, Florian, Hagenacker, Tim, Weyen, Ute, Günther, René, Vidovic, Maximilian, Jentsch, Martin, Haarmeier, Thomas, Weydt, Patrick, Valkadinov, Ivan, Hesebeck-Brinckmann, Jasper, Conrad, Julian, Weishaupt, Jochen Hans, Schumann, Peggy, Körtvélyessy, Peter, Meyer, Thomas, Ruf, Wolfgang Philipp, Witzel, Simon, Senel, Makbule, Tumani, Hayrettin, Ludolph, Albert Christian
Published in EClinicalMedicine (01.03.2024)
Published in EClinicalMedicine (01.03.2024)
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Journal Article
A randomized double-blind clinical trial on safety and efficacy of tauroursodeoxycholic acid : the statistical analysis plan of TUDCA-ALS trial
Lombardo, Flavia L, Spila Alegiani, Stefania, Mayer, Flavia, Cipriani, Marta, Lo Giudice, Maria, Ludolph, Albert Christian, McDermott, Christopher J, Corcia, Philippe, Van Damme, Philip, Van den Berg, Leonard H, Hardiman, Orla, Nicolini, Gabriele, Vanacore, Nicola, Dickie, Brian, Albanese, Alberto, Puopolo, Maria, Tornese, Paolo, Cocco, Antoniangela, Matteoli, Michela, Lauranzano, Eliana, Malosio, Maria Luisa, Elia, Chiara Adriana, Chiò, Adriano, Manera, Umberto, Moglia, Cristina, Calvo, Andrea, Salamone, Paolina, Fuda, Giuseppe, Colosimo, Carlo, Spera, Cristina, Ranchicchio, Prabha Cristina, Stipa, Giuseppe, Frondizi, Domenico, Lunetta, Christian, Sansone, Valeria, Tarlarini, Claudia, Gerardi, Francesca, Silani, Vincenzo, Doretti, Alberto, Colombo, Eleonora, Demirtzidis, Gianluca, Tedeschi, Gioacchino, Trojsi, Francesca, Passaniti, Carla, Ballestrero, Stefania, Dorst, Johannes, Weiland, Ulrike, Fromm, Andrea, Wiesenfarth, Maximilian, Kandler, Katharina, Witzel, Simon, Otto, Markus, Schuster, Joachim, Meyer, Thomas, Maier, André, Kettemann, Dagmar, Petri, Susanne, Müschen, Lars, Wohnrade, Camilla, Sarikidi, Anastasia, Osmanovic, Alma, Grosskreutz, Julian, Rödiger, Annekathrin, Steinbach, Robert, Ilse, Benjamin, Smesny, Uta, Untucht, Robert, Günther, René, Vidovic, Maximilian, Shaw, Pamela, Collins, Alexis, Wollff, Helen, Walsh, Theresa, Tuddenham, Lee, Kazoka, Mbombe, White, David, Young, Stacy, Thompson, Benjamin, Madarshahian, Daniel, Chhetri, Suresh K, Chaouch, Amina, Young, Carolyn A, Arndt, Heike, Hanemann, Coliver, Lambert, Thomas, Beltran, Stephane, Couratier, Philippe, Esselin, Florence, Camu, William, De La Cruz, Elisa, Lemasson, Gwendal, Masrori, Pegah, Maguire, Sinead, Fogarty, Liz, Atoyebi, Toyosi, Obáin, Niamh Ní
Published in Trials (05.12.2023)
Published in Trials (05.12.2023)
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Journal Article
Tauroursodeoxycholic acid in patients with amyotrophic lateral sclerosis: The TUDCA-ALS trial protocol
Albanese, Alberto, Ludolph, Albert Christian, McDermott, Christopher J, Corcia, Philippe, Van Damme, Philip, Van den Berg, Leonard H, Hardiman, Orla, Rinaldi, Gilberto, Vanacore, Nicola, Dickie, Brian
Published in Frontiers in neurology (27.09.2022)
Published in Frontiers in neurology (27.09.2022)
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Journal Article
Metabolic alterations precede neurofilament changes in presymptomatic ALS gene carriersResearch in context
Johannes Dorst, Patrick Weydt, David Brenner, Simon Witzel, Katharina Kandler, André Huss, Christine Herrmann, Maximilian Wiesenfarth, Antje Knehr, Kornelia Günther, Kathrin Müller, Jochen H. Weishaupt, Johannes Prudlo, Karin Forsberg, Peter M. Andersen, Angela Rosenbohm, Joachim Schuster, Francesco Roselli, Luc Dupuis, Benjamin Mayer, Hayrettin Tumani, Jan Kassubek, Albert C. Ludolph
Published in EBioMedicine (01.04.2023)
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Published in EBioMedicine (01.04.2023)
Journal Article
Effects of tofersen treatment in patients with SOD1-ALS in a “real-world” setting – a 12-month multicenter cohort study from the German early access programResearch in context
Maximilian Wiesenfarth, Johannes Dorst, David Brenner, Zeynep Elmas, Özlem Parlak, Zeljko Uzelac, Katharina Kandler, Kristina Mayer, Ulrike Weiland, Christine Herrmann, Joachim Schuster, Axel Freischmidt, Kathrin Müller, Reiner Siebert, Franziska Bachhuber, Tatiana Simak, Kornelia Günther, Elke Fröhlich, Antje Knehr, Martin Regensburger, Alexander German, Susanne Petri, Julian Grosskreutz, Thomas Klopstock, Peter Reilich, Florian Schöberl, Tim Hagenacker, Ute Weyen, René Günther, Maximilian Vidovic, Martin Jentsch, Thomas Haarmeier, Patrick Weydt, Ivan Valkadinov, Jasper Hesebeck-Brinckmann, Julian Conrad, Jochen Hans Weishaupt, Peggy Schumann, Peter Körtvélyessy, Thomas Meyer, Wolfgang Philipp Ruf, Simon Witzel, Makbule Senel, Hayrettin Tumani, Albert Christian Ludolph
Published in EClinicalMedicine (01.03.2024)
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Published in EClinicalMedicine (01.03.2024)
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