Replacing the enzyme alpha-L-iduronidase at birth ameliorates symptoms in the brain and periphery of dogs with mucopolysaccharidosis type I
Dierenfeld, Ashley D, McEntee, Michael F, Vogler, Carole A, Vite, Charles H, Chen, Agnes H, Passage, Merry, Le, Steven, Shah, Sahil, Jens, Jackie K, Snella, Elizabeth M, Kline, Karen L, Parkes, Jennifer D, Ware, Wendy A, Moran, Lori E, Fales-Williams, Amanda J, Wengert, Jane A, Whitley, R David, Betts, Daniel M, Boal, Amy M, Riedesel, Elizabeth A, Gross, William, Ellinwood, N Matthew, Dickson, Patricia I
Published in Science translational medicine (01.12.2010)
Published in Science translational medicine (01.12.2010)
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