Intraparenchymal convection enhanced delivery of AAV in sheep to treat Mucopolysaccharidosis IIIC
O'Leary, Claire, Forte, Gabriella, Mitchell, Nadia L, Youshani, Amir Saam, Dyer, Adam, Wellby, Martin P, Russell, Katharina N, Murray, Samantha J, Jolinon, Nelly, Jones, Simon A, Stacey, Kevin, Davis, Daniel M, Henckaerts, Els, Palmer, David N, Kamaly-Asl, Ian, Bigger, Brian W
Published in Journal of translational medicine (05.07.2023)
Published in Journal of translational medicine (05.07.2023)
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Journal Article
Efficacy of dual intracerebroventricular and intravitreal CLN5 gene therapy in sheep prompts the first clinical trial to treat CLN5 Batten disease
Murray, Samantha J., Wellby, Martin P., Barrell, Graham K., Russell, Katharina N., Deane, Ashley R., Wynyard, John R., Gray, Steven J., Palmer, David N., Mitchell, Nadia L.
Published in Frontiers in pharmacology (24.10.2023)
Published in Frontiers in pharmacology (24.10.2023)
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Long-term safety and dose escalation of intracerebroventricular CLN5 gene therapy in sheep supports clinical translation for CLN5 Batten disease
Mitchell, Nadia L, Murray, Samantha J, Wellby, Martin P, Barrell, Graham K, Russell, Katharina N, Deane, Ashley R, Wynyard, John R, Palmer, Madeleine J, Pulickan, Anila, Prendergast, Phillipa M, Casy, Widler, Gray, Steven J, Palmer, David N
Published in Frontiers in genetics (08.08.2023)
Published in Frontiers in genetics (08.08.2023)
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Electroretinography data from ovine models of CLN5 and CLN6 neuronal ceroid lipofuscinoses
Russell, Katharina N., Mitchell, Nadia L., Wellby, Martin P., Barrell, Graham K., Palmer, David N.
Published in Data in brief (01.08.2021)
Published in Data in brief (01.08.2021)
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Journal Article
Longitudinal In Vivo Monitoring of the CNS Demonstrates the Efficacy of Gene Therapy in a Sheep Model of CLN5 Batten Disease
Mitchell, Nadia L., Russell, Katharina N., Wellby, Martin P., Wicky, Hollie E., Schoderboeck, Lucia, Barrell, Graham K., Melzer, Tracy R., Gray, Steven J., Hughes, Stephanie M., Palmer, David N.
Published in Molecular therapy (03.10.2018)
Published in Molecular therapy (03.10.2018)
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Journal Article
Computed tomography provides enhanced techniques for longitudinal monitoring of progressive intracranial volume loss associated with regional neurodegeneration in ovine neuronal ceroid lipofuscinoses
Russell, Katharina N., Mitchell, Nadia L., Anderson, Nigel G., Bunt, Craig R., Wellby, Martin P., Melzer, Tracy R., Barrell, Graham K., Palmer, David N.
Published in Brain and behavior (01.09.2018)
Published in Brain and behavior (01.09.2018)
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Differential expression of a gene homologous to a G-α protein gene in neonatal mouse skin during development of hair follicles
Su, Hung-Yi, Palmer, Barry R, Wellby, Martin P, Bickerstaffe, Roy, Hickford, Jonathan G.H
Published in Journal of dermatological science (2001)
Published in Journal of dermatological science (2001)
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