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Published in JAMA neurology (01.02.2013)
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Antisense oligonucleotide therapy for neurodegenerative disease
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Published in The Journal of clinical investigation (01.08.2006)
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Effect of dose and plasma concentration on liver uptake and pharmacologic activity of a 2′-methoxyethyl modified chimeric antisense oligonucleotide targeting PTEN
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Published in Biochemical pharmacology (01.08.2009)
Published in Biochemical pharmacology (01.08.2009)
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Intracerebral Infusion of Antisense Oligonucleotides Into Prion-infected Mice
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Published in Molecular therapy. Nucleic acids (01.02.2012)
Published in Molecular therapy. Nucleic acids (01.02.2012)
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Time-dependent, bidirectional, anti- and pro-spinal hyper-reflexia and muscle spasticity effect after chronic spinal glycine transporter 2 (GlyT2) oligonucleotide-induced downregulation
Kamizato, Kota, Marsala, Silvia, Navarro, Michael, Kakinohana, Manabu, Platoshyn, Oleksandr, Yoshizumi, Tetsuya, Lukacova, Nadezda, Wancewicz, Ed, Powers, Berit, Mazur, Curt, Marsala, Martin
Published in Experimental neurology (01.07.2018)
Published in Experimental neurology (01.07.2018)
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Effect of dose and plasma concentration on liver uptake and pharmacologic activity of a 2+IBk--methoxyethyl modified chimeric antisense oligonucleotide targeting PTEN
Geary, Richard S, Wancewicz, Ed, Matson, John, Pearce, Megan, Siwkowski, Andrew, Swayze, Eric, Bennett, Frank
Published in Biochemical pharmacology (01.08.2009)
Published in Biochemical pharmacology (01.08.2009)
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2‘-O-Aminopropyl Ribonucleotides: A Zwitterionic Modification That Enhances the Exonuclease Resistance and Biological Activity of Antisense Oligonucleotides
Griffey, Richard H., Monia, Brett P., Cummins, Lendall L., Freier, Susan, Greig, Michael J., Guinosso, Charles J., Lesnik, Elena, Manalili, Sherilynn M., Mohan, Venkatraman, Owens, Steven, Ross, Bruce R., Sasmor, Henri, Wancewicz, Ed, Weiler, Kurt, Wheeler, Patrick D., Cook, P. Dan
Published in Journal of medicinal chemistry (20.12.1996)
Published in Journal of medicinal chemistry (20.12.1996)
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SOD1 in Cerebral Spinal Fluid as a Pharmacodynamic Marker for Antisense Oligonucleotide Therapy
Winer, Leah, Srinivasan, Dushyanth, Chun, Seung, Lacomis, David, Jaffa, Matthew, Fagan, Anne, Holtzman, David M, Wancewicz, Ed, Bennett, C Frank, Bowser, Robert, Cudkowicz, Merit, Miller, Timothy M
Published in Archives of neurology (Chicago) (01.02.2013)
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Published in Archives of neurology (Chicago) (01.02.2013)
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