Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial
Kerem, Eitan, Konstan, Michael W, De Boeck, Kris, Accurso, Frank J, Sermet-Gaudelus, Isabelle, Wilschanski, Michael, Elborn, J Stuart, Melotti, Paola, Bronsveld, Inez, Fajac, Isabelle, Malfroot, Anne, Rosenbluth, Daniel B, Walker, Patricia A, McColley, Susanna A, Knoop, Christiane, Quattrucci, Serena, Rietschel, Ernst, Zeitlin, Pamela L, Barth, Jay, Elfring, Gary L, Welch, Ellen M, Branstrom, Arthur, Spiegel, Robert J, Peltz, Stuart W, Ajayi, Temitayo, Rowe, Steven M
Published in The lancet respiratory medicine (01.07.2014)
Published in The lancet respiratory medicine (01.07.2014)
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Bortezomib-based antibody depletion for refractory autoimmune hematological diseases
Ratnasingam, Sumita, Walker, Patricia A., Tran, Huy, Kaplan, Zane S., McFadyen, James D., Tran, Huyen, Teh, Tse-Chieh, Fleming, Shaun, Catalano, John V., Chunilal, Sanjeev D., Johnston, Anna, Opat, Stephen S., Shortt, Jake
Published in Blood advances (29.11.2016)
Published in Blood advances (29.11.2016)
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Center-level self-study identifies opportunities to advance equity in cystic fibrosis clinical trial participation
Januska, Megan N, Langfelder-Schwind, Elinor, Plachta, Amy, Demarco, Teresa, Walker, Patricia A, Berdella, Maria N
Published in Journal of cystic fibrosis (01.07.2023)
Published in Journal of cystic fibrosis (01.07.2023)
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The CFTR variant profile of Hispanic patients with cystic fibrosis: Impact on access to effective screening, diagnosis, and personalized medicine
Januska, Megan N., Marx, Laura, Walker, Patricia A., Berdella, Maria N., Langfelder‐Schwind, Elinor
Published in Journal of genetic counseling (01.08.2020)
Published in Journal of genetic counseling (01.08.2020)
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Unilateral internal jugular venous thrombosis in a young trauma patient
Ackland, Helen M, Marshall, Nina L, Hall, Nicholas D.P, Walker, Patricia A, Varma, Dinesh K
Published in Injury extra (01.11.2009)
Published in Injury extra (01.11.2009)
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Acalabrutinib ± Obinutuzumab Vs Obinutuzumab + Chlorambucil in Treatment-Naive Chronic Lymphocytic Leukemia: 6-Year Follow-up of Elevate-TN
Sharman, Jeff P., Egyed, Miklos, Jurczak, Wojciech, Skarbnik, Alan, Patel, Krish, Flinn, Ian W., Kamdar, Manali, Munir, Talha, Walewska, Renata, Hughes, Marie, Fogliatto, Laura Maria, Herishanu, Yair, Banerji, Versha, Follows, George, Walker, Patricia A., Karlsson, Karin, Ghia, Paolo, Janssens, Ann, Cymbalista, Florence, Byrd, John C., Ferrant, Emmanuelle, Ferrajoli, Alessandra, Wierda, William G., Munugalavadla, Veerendra, Wachira, Catherine Wangui, Wun, Chuan-Chuan, Woyach, Jennifer A.
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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A 2-Stage Phase II Study of Panobinostat Consolidation in Multiple Myeloma (MM) Patients with < CR Following Single High-Dose Chemotherapy (HDT) Conditioned Autologous Stem Cell Transplantation (ASCT) As Part of First Line Therapy
Kalff, Anna, Mithraprabhu, Sridurga, Khong, Tiffany T., Ramachandran, Malarmathy, Reed, Kate, Quach, Hang, Walker, Patricia A., Bergin, Krystal, Spencer, Andrew
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Post-Allogeneic Stem Cell Transplant Surveillance of CD34+ Sorted Peripheral Blood to Quantify Emergent DNMT3A, IDH and NPM1 clones and Correlation with Clinical Outcome
Fleming, Shaun, Cummings, Nik, Das, Tongted, Ivey, Adam, McManus, Julie, Avery, Sharon, Patil, Sushrut S., Walker, Patricia A., Curtis, David J., Spencer, Andrew, Wei, Andrew
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Addition of elotuzumab to lenalidomide and dexamethasone for patients with newly diagnosed, transplantation ineligible multiple myeloma (ELOQUENT-1): an open-label, multicentre, randomised, phase 3 trial
Dimopoulos, Meletios A, Richardson, Paul G, Bahlis, Nizar J, Grosicki, Sebastian, Cavo, Michele, Beksaç, Meral, Legieć, Wojciech, Liberati, Anna M, Goldschmidt, Hartmut, Belch, Andrew, Magen, Hila, Larocca, Alessandra, Laubach, Jacob P, Petrucci, Maria T, Reece, Donna, White, Darrell, Mateos, María-Victoria, Špička, Ivan, Lazaroiu, Mihaela, Berdeja, Jesús, Kaufman, Jonathan L, Jou, Ying-Ming, Ganetsky, Alex, Popa McKiver, Mihaela, Lonial, Sagar, Weisel, Katja
Published in The Lancet. Haematology (01.06.2022)
Published in The Lancet. Haematology (01.06.2022)
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High Risk Multiple Myeloma: Better Outcomes with Upfront Tandem Autologous- Non-Myelo Ablative Allogeneic Stem Cell Transplantation Compared to Upfront Autologous Stem Cell Transplantation
Nair, Anish Puliyayil, Lee, Cindy, Kalff, Anna, Walker, Patricia A., Bergin, Krystal, Hocking, Jay, Morgan, Sue, Klarica, Daniela, Muirhead, Jenny, Spencer, Andrew, Lee, Oi Lin, Horvath, Noemi
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Comparison of Cyclophosphamide/Total Body Irradiation (Cy/TBI) and Etoposide/Total Body Irradiation (Etop/TBI) Conditioned Allogeneic Stem Cell Transplant (alloHSCT) for Adult Acute Lymphoblastic Leukaemia (ALL), Data from an Australian Tertiary Care Centre
Nair, Anish Puliyayil, Fleming, Shaun, Avery, Sharon, Curtis, David J., Patil, Sushrut S., Walker, Patricia A., Wei, Andrew, Muirhead, Jenny, Spencer, Andrew
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Autologous Stem Cell Transplantation (ASCT) Followed By Outpatient-Based Non-Myeloblative Allogeneic (NMA) Stem Cell Transplantation (Tandem Auto-Allo) for Biologically Adverse Multiple Myeloma (MM). a Single Centre Experience from Australia
Nair, Anish Puliyayil, Walker, Patricia A., Kalff, Anna, Bergin, Krystal, Avery, Sharon, Curtis, David J., Patil, Sushrut S., Muirhead, Jenny, Phomoonna, Tongted, Klarica, Daniela, Spencer, Andrew
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Bortezomib Yields High Response Rates in Antibody-Mediated Autoimmune Hematological Diseases Refractory to Conventional Immunosuppression
Ratnasingam, Sumita, Walker, Patricia A., Tran, Huy, Kaplan, Zane, McFadyen, James David, Tran, Huyen, Teh, Tse-Chieh, Wood, Erica M., Catalano, John V., Opat, Stephen, Shortt, Jake
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Outpatient Non-Myeloablative Allogeneic Stem Cell Transplantation For Myeloma Is Feasible, Efficacious and Associated With Low Transplant-Related Morbidity and Mortality
Campbell, Philip, Walker, Patricia A., Avery, Sharon, Patil, Sushrut S., Curtis, David J., Schwarer, Anthony P., Wei, Andrew H, Kalff, Anna, Muirhead, Jenny, Spencer, Andrew
Published in Blood (15.11.2013)
Published in Blood (15.11.2013)
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Incidence and Kinetics Of Full Donor Chimerism and The Impact Of Minimal Residual Disease Status Following Outpatient Non-Myeloablative Allogeneic Stem Cell Transplantation For Myeloma
Campbell, Philip, Das, Tongted, Kipp, David, Walker, Patricia A., Muirhead, Jenny, Avery, Sharon, Patil, Sushrut S., Curtis, David J., Schwarer, Anthony P., Kalff, Anna, Spencer, Andrew
Published in Blood (15.11.2013)
Published in Blood (15.11.2013)
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Leopard: A Phase II Study of Maintenance Lenalidomide and Prednisolone Post Autologous Stem Cell Transplantation (ASCT) for Myeloma, Incorporating Minimal Residual Disease Assessments
Kalff, Anna, Kennedy, Nola, Walker, Patricia A., Khong, Tiffany T., Schwarer, Anthony, Roberts, Andrew W., Campbell, Philip, Filshie, Robin, Smiley, Angela, Gorniak, Malgorzata, Black, Marion, Jenkins, Nicole, Raines, Geoffrey, Spencer, Andrew
Published in Blood (06.12.2014)
Published in Blood (06.12.2014)
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Leopard: A Phase II Study Of Post Autologous Stem Cell Transplantation (ASCT) Maintenance Lenalidomide and Prednisolone For Myeloma (MM), Incorporating Minimal Residual Disease (MRD) Assessments
Kalff, Anna, Kennedy, Nola, Walker, Patricia A., Black, Marion, Youdell, Odette, Gorniak, Malgorzata, Khong, Tiffany T., Estifo, Lona, Smiley, Angela, Schwarer, Anthony P., Roberts, Andrew W., Campbell, Philip, Flishie, Robin, Spencer, Andrew
Published in Blood (15.11.2013)
Published in Blood (15.11.2013)
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Initial Remission Duration Is the Most Important Predictor of Outcome Following FLAG-Amsacrine Salvage of AML in First Relapse
Fong, Chun Yew, Grigoriadis, George, Hocking, Jay, Campbell, Philip, Schwarer, Anthony P., Walker, Patricia A., Avery, Sharon, Patil, Sushrut S., Salem, Hatem H., Spencer, Andrew, Wei, Andrew H
Published in Blood (18.11.2011)
Published in Blood (18.11.2011)
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Azacitidine in Combination with the mTOR Inhibitor Everolimus in Relapsed and Refractory AML
Wei, Andrew H, Tan, Peter T., Catalano, John, Walker, Patricia A., Schwarer, Anthony P., Avery, Sharon, Patil, Sushrut S., Opat, Stephen, Cummings, Nik, Spencer, Andrew
Published in Blood (18.11.2011)
Published in Blood (18.11.2011)
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