Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery
Cukras, Catherine, Wiley, Henry E., Jeffrey, Brett G., Sen, H. Nida, Turriff, Amy, Zeng, Yong, Vijayasarathy, Camasamudram, Marangoni, Dario, Ziccardi, Lucia, Kjellstrom, Sten, Park, Tae Kwon, Hiriyanna, Suja, Wright, J. Fraser, Colosi, Peter, Wu, Zhijian, Bush, Ronald A., Wei, Lisa L., Sieving, Paul A.
Published in Molecular therapy (05.09.2018)
Published in Molecular therapy (05.09.2018)
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X-Linked Retinoschisis
Ku, Cristy A, Wei, Lisa W, Sieving, Paul A
Published in Cold Spring Harbor perspectives in biology (01.09.2023)
Published in Cold Spring Harbor perspectives in biology (01.09.2023)
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Immune function in X-linked retinoschisis subjects in an AAV8-RS1 phase I/IIa gene therapy trial
Mishra, Alaknanda, Vijayasarathy, Camasamudram, Cukras, Catherine A., Wiley, Henry E., Sen, H. Nida, Zeng, Yong, Wei, Lisa L., Sieving, Paul A.
Published in Molecular therapy (02.06.2021)
Published in Molecular therapy (02.06.2021)
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COLD MOLECULAR GAS ALONG THE COOLING X-RAY FILAMENT IN A1795
McDonald, Michael, Wei, Lisa H, Veilleux, Sylvain
Published in Astrophysical journal. Letters (20.08.2012)
Published in Astrophysical journal. Letters (20.08.2012)
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Identification and Analyses of Extra-Cranial and Cranial Rhabdoid Tumor Molecular Subgroups Reveal Tumors with Cytotoxic T Cell Infiltration
Chun, Hye-Jung E., Johann, Pascal D., Milne, Katy, Zapatka, Marc, Buellesbach, Annette, Ishaque, Naveed, Iskar, Murat, Erkek, Serap, Wei, Lisa, Tessier-Cloutier, Basile, Lever, Jake, Titmuss, Emma, Topham, James T., Bowlby, Reanne, Chuah, Eric, Mungall, Karen L., Ma, Yussanne, Mungall, Andrew J., Moore, Richard A., Taylor, Michael D., Gerhard, Daniela S., Jones, Steven J.M., Korshunov, Andrey, Gessler, Manfred, Kerl, Kornelius, Hasselblatt, Martin, Frühwald, Michael C., Perlman, Elizabeth J., Nelson, Brad H., Pfister, Stefan M., Marra, Marco A., Kool, Marcel
Published in Cell reports (Cambridge) (19.11.2019)
Published in Cell reports (Cambridge) (19.11.2019)
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THE RESOLVE SURVEY ATOMIC GAS CENSUS AND ENVIRONMENTAL INFLUENCES ON GALAXY GAS RESERVOIRS
Stark, David V., Kannappan, Sheila J., Eckert, Kathleen D., Florez, Jonathan, Hall, Kirsten R., Watson, Linda C., Hoversten, Erik A., Burchett, Joseph N., Guynn, David T., Baker, Ashley D., Moffett, Amanda J., Berlind, Andreas A., Norris, Mark A., Haynes, Martha P., Giovanelli, Riccardo, Leroy, Adam K., Pisano, D. J., Wei, Lisa H., Gonzalez, Roberto E., Calderon, Victor F.
Published in The Astrophysical journal (01.12.2016)
Published in The Astrophysical journal (01.12.2016)
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Ocular localization and transduction by adenoviral vectors are serotype-dependent and can be modified by inclusion of RGD fiber modifications
Ueyama, Kazuhiro, Mori, Keisuke, Shoji, Takuhei, Omata, Hidekazu, Gehlbach, Peter L, Brough, Douglas E, Wei, Lisa L, Yoneya, Shin
Published in PloS one (18.09.2014)
Published in PloS one (18.09.2014)
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THE STATE OF THE WARM AND COLD GAS IN THE EXTREME STARBURST AT THE CORE OF THE PHOENIX GALAXY CLUSTER (SPT-CLJ2344-4243)
McDonald, Michael, Swinbank, Mark, Edge, Alastair C, Wiener, David J, Veilleux, Sylvain, Benson, Bradford A, Hogan, Michael T, Marrone, Daniel P, McNamara, Brian R, Wei, Lisa H, Bayliss, Matthew B, Bautz, Marshall W
Published in The Astrophysical journal (20.03.2014)
Published in The Astrophysical journal (20.03.2014)
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Integrated stem cell signature and cytomolecular risk determination in pediatric acute myeloid leukemia
Huang, Benjamin J., Smith, Jenny L., Farrar, Jason E., Wang, Yi-Cheng, Umeda, Masayuki, Ries, Rhonda E., Leonti, Amanda R., Crowgey, Erin, Furlan, Scott N., Tarlock, Katherine, Armendariz, Marcos, Liu, Yanling, Shaw, Timothy I., Wei, Lisa, Gerbing, Robert B., Cooper, Todd M., Gamis, Alan S., Aplenc, Richard, Kolb, E. Anders, Rubnitz, Jeffrey, Ma, Jing, Klco, Jeffery M., Ma, Xiaotu, Alonzo, Todd A., Triche, Timothy, Meshinchi, Soheil
Published in Nature communications (19.09.2022)
Published in Nature communications (19.09.2022)
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CONNECTING TRANSITIONS IN GALAXY PROPERTIES TO REFUELING
Kannappan, Sheila J, Stark, David V, Eckert, Kathleen D, Moffett, Amanda J, Wei, Lisa H, Pisano, D J, Baker, Andrew J, Vogel, Stuart N, Fabricant, Daniel G, Laine, Seppo, Norris, Mark A, Jogee, Shardha, Lepore, Natasha, Hough, Loren E, Weinberg-Wolf, Jennifer
Published in The Astrophysical journal (01.11.2013)
Published in The Astrophysical journal (01.11.2013)
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CNGB3-achromatopsia clinical trial with CNTF: diminished rod pathway responses with no evidence of improvement in cone function
Zein, Wadih M, Jeffrey, Brett G, Wiley, Henry E, Turriff, Amy E, Tumminia, Santa J, Tao, Weng, Bush, Ronald A, Marangoni, Dario, Wen, Rong, Wei, Lisa L, Sieving, Paul A
Published in Investigative ophthalmology & visual science (01.10.2014)
Published in Investigative ophthalmology & visual science (01.10.2014)
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Intravitreal Ciliary Neurotrophic Factor Transiently Improves Cone-Mediated Function in a CNGB3-/- Mouse Model of Achromatopsia
Marangoni, Dario, Vijayasarathy, Camasamudram, Bush, Ronald A, Wei, Lisa L, Wen, Rong, Sieving, Paul A
Published in Investigative ophthalmology & visual science (01.10.2015)
Published in Investigative ophthalmology & visual science (01.10.2015)
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Gas Mass Fractions and Star Formation in Blue-Sequence E/S0 Galaxies
Wei, Lisa H, Kannappan, Sheila J, Vogel, Stuart N, Baker, Andrew J
Published in The Astrophysical journal (01.01.2010)
Published in The Astrophysical journal (01.01.2010)
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Convergence of Human Genetics and Animal Studies: Gene Therapy for X-Linked Retinoschisis
Bush, Ronald A, Wei, Lisa L, Sieving, Paul A
Published in Cold Spring Harbor perspectives in medicine (01.08.2015)
Published in Cold Spring Harbor perspectives in medicine (01.08.2015)
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Adenoviral vector-delivered pigment epithelium-derived factor for neovascular age-related macular degeneration: results of a phase I clinical trial
Campochiaro, Peter A, Nguyen, Quan Dong, Shah, Syed Mahmood, Klein, Michael L, Holz, Eric, Frank, Robert N, Saperstein, David A, Gupta, Anurag, Stout, J Timothy, Macko, Jennifer, DiBartolomeo, Robert, Wei, Lisa L
Published in Human gene therapy (01.02.2006)
Published in Human gene therapy (01.02.2006)
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“Para-retinal” Vector Administration into the Deep Vitreous Enhances Retinal Transgene Expression
Zeng, Yong, Boyd, Ryan, Bartoe, Joshua, Wiley, Henry E., Marangoni, Dario, Wei, Lisa L., Sieving, Paul A.
Published in Molecular therapy. Methods & clinical development (11.09.2020)
Published in Molecular therapy. Methods & clinical development (11.09.2020)
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A Galactic O Star Catalog
Maíz-Apellániz, Jesús, Walborn, Nolan R, Galué, Héctor Á, Wei, Lisa H
Published in The Astrophysical journal. Supplement series (01.03.2004)
Published in The Astrophysical journal. Supplement series (01.03.2004)
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