Stem cell-based therapies for Duchenne muscular dystrophy
Sun, Congshan, Serra, Carlo, Lee, Gabsang, Wagner, Kathryn R.
Published in Experimental neurology (01.01.2020)
Published in Experimental neurology (01.01.2020)
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The role of paid family leave in labor supply responses to a spouse's disability or health shock
Anand, Priyanka, Dague, Laura, Wagner, Kathryn L.
Published in Journal of health economics (01.05.2022)
Published in Journal of health economics (01.05.2022)
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Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and neuromuscular, rehabilitation, endocrine, and gastrointestinal and nutritional management
Birnkrant, David J, Bushby, Katharine, Bann, Carla M, Apkon, Susan D, Blackwell, Angela, Brumbaugh, David, Case, Laura E, Clemens, Paula R, Hadjiyannakis, Stasia, Pandya, Shree, Street, Natalie, Tomezsko, Jean, Wagner, Kathryn R, Ward, Leanne M, Weber, David R
Published in Lancet neurology (01.03.2018)
Published in Lancet neurology (01.03.2018)
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Safety, tolerability, and pharmacokinetics of casimersen in patients with Duchenne muscular dystrophy amenable to exon 45 skipping: A randomized, double‐blind, placebo‐controlled, dose‐titration trial
Wagner, Kathryn R., Kuntz, Nancy L., Koenig, Erica, East, Lilly, Upadhyay, Sameer, Han, Baoguang, Shieh, Perry B.
Published in Muscle & nerve (01.09.2021)
Published in Muscle & nerve (01.09.2021)
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Developing a pro-regenerative biomaterial scaffold microenvironment requires T helper 2 cells
Sadtler, Kaitlyn, Estrellas, Kenneth, Allen, Brian W., Wolf, Matthew T., Fan, Hongni, Tam, Ada J., Patel, Chirag H., Luber, Brandon S., Wang, Hao, Wagner, Kathryn R., Powell, Jonathan D., Housseau, Franck, Pardoll, Drew M., Elisseeff, Jennifer H.
Published in Science (American Association for the Advancement of Science) (15.04.2016)
Published in Science (American Association for the Advancement of Science) (15.04.2016)
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Myostatin Directly Regulates Skeletal Muscle Fibrosis
Li, Zhao Bo, Kollias, Helen D., Wagner, Kathryn R.
Published in The Journal of biological chemistry (11.07.2008)
Published in The Journal of biological chemistry (11.07.2008)
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Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial
Muntoni, Francesco, Guglieri, Michela, Mah, Jean K., Wagner, Kathryn R., Brandsema, John F., Butterfield, Russell J., McDonald, Craig M., Mayhew, Anna G., Palmer, Jeffrey P., Marraffino, Shannon, Charnas, Lawrence, Mercuri, Eugenio
Published in PloS one (23.08.2022)
Published in PloS one (23.08.2022)
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Concordant but Varied Phenotypes among Duchenne Muscular Dystrophy Patient-Specific Myoblasts Derived using a Human iPSC-Based Model
Choi, In Young, Lim, HoTae, Estrellas, Kenneth, Mula, Jyothi, Cohen, Tatiana V., Zhang, Yuanfan, Donnelly, Christopher J., Richard, Jean-Philippe, Kim, Yong Jun, Kim, Hyesoo, Kazuki, Yasuhiro, Oshimura, Mitsuo, Li, Hongmei Lisa, Hotta, Akitsu, Rothstein, Jeffrey, Maragakis, Nicholas, Wagner, Kathryn R., Lee, Gabsang
Published in Cell reports (Cambridge) (07.06.2016)
Published in Cell reports (Cambridge) (07.06.2016)
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Microdystrophin Expression as a Surrogate Endpoint for Duchenne Muscular Dystrophy Clinical Trials
Chamberlain, Jeffrey S, Robb, Melissa, Braun, Serge, Brown, Kristy J, Danos, Olivier, Ganot, Annie, Gonzalez-Alegre, Pedro, Hunter, Nina, McDonald, Craig, Morris, Carl, Tobolowsky, Mark, Wagner, Kathryn R, Ziolkowski, Olivia, Duan, Dongsheng
Published in Human gene therapy (01.05.2023)
Published in Human gene therapy (01.05.2023)
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Morpholino-mediated Knockdown of DUX4 Toward Facioscapulohumeral Muscular Dystrophy Therapeutics
Chen, Jennifer CJ, King, Oliver D, Zhang, Yuanfan, Clayton, Nicholas P, Spencer, Carrie, Wentworth, Bruce M, Emerson, Charles P, Wagner, Kathryn R
Published in Molecular therapy (01.08.2016)
Published in Molecular therapy (01.08.2016)
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Journal Article
Contemporary Cardiac Issues in Duchenne Muscular Dystrophy
McNally, Elizabeth M, Kaltman, Jonathan R, Benson, D Woodrow, Canter, Charles E, Cripe, Linda H, Duan, Dongsheng, Finder, Jonathan D, Hoffman, Eric P, Judge, Daniel P, Kertesz, Naomi, Kinnett, Kathi, Kirsch, Roxanne, Metzger, Joseph M, Pearson, Gail D, Rafael-Fortney, Jill A, Raman, Subha V, Spurney, Christopher F, Targum, Shari L, Wagner, Kathryn R, Markham, Larry W
Published in Circulation (New York, N.Y.) (05.05.2015)
Published in Circulation (New York, N.Y.) (05.05.2015)
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Cardiac Management of the Patient With Duchenne Muscular Dystrophy
Buddhe, Sujatha, Cripe, Linda, Friedland-Little, Joshua, Kertesz, Naomi, Eghtesady, Pirooz, Finder, Jonathan, Hor, Kan, Judge, Daniel P, Kinnett, Kathi, McNally, Elizabeth M, Raman, Subha, Thompson, W Reid, Wagner, Kathryn R, Olson, Aaron K
Published in Pediatrics (Evanston) (01.10.2018)
Published in Pediatrics (Evanston) (01.10.2018)
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