Laronidase-loaded liposomes reach the brain and other hard-to-treat organs after noninvasive nasal administration
Schuh, Roselena Silvestri, Franceschi, Eduarda Piovesan, Brum, Bruna Brazeiro, Fachel, Flávia Nathiely Silveira, Poletto, Édina, Vera, Luisa Natália Pimentel, Santos, Hallana Souza, Medeiros-Neves, Bruna, Monteagudo de Barros, Vinicius, Helena da Rosa Paz, Ana, Baldo, Guilherme, Matte, Ursula, Giugliani, Roberto, Ferreira Teixeira, Helder
Published in International journal of pharmaceutics (20.07.2024)
Published in International journal of pharmaceutics (20.07.2024)
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CNS-wide repopulation by hematopoietic-derived microglia-like cells corrects progranulin deficiency in mice
Colella, Pasqualina, Sayana, Ruhi, Suarez-Nieto, Maria Valentina, Sarno, Jolanda, Nyame, Kwamina, Xiong, Jian, Pimentel Vera, Luisa Natalia, Arozqueta Basurto, Jessica, Corbo, Marco, Limaye, Anay, Davis, Kara L., Abu-Remaileh, Monther, Gomez-Ospina, Natalia
Published in Nature communications (05.07.2024)
Published in Nature communications (05.07.2024)
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Neonatal nonviral gene editing with the CRISPR/Cas9 system improves some cardiovascular, respiratory, and bone disease features of the mucopolysaccharidosis I phenotype in mice
Schuh, Roselena Silvestri, Gonzalez, Esteban Alberto, Tavares, Angela Maria Vicente, Seolin, Bruna Gazzi, Elias, Lais de Souza, Vera, Luisa Natalia Pimentel, Kubaski, Francyne, Poletto, Edina, Giugliani, Roberto, Teixeira, Helder Ferreira, Matte, Ursula, Baldo, Guilherme
Published in Gene therapy (01.02.2020)
Published in Gene therapy (01.02.2020)
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Journal Article
Brain and visceral gene editing of mucopolysaccharidosis I mice by nasal delivery of the CRISPR/Cas9 system
Vera, Luisa Natalia Pimentel, Schuh, Roselena Silvestri, Fachel, Flavia Nathielly Silveira, Poletto, Edina, Piovesan, Eduarda, Kubaski, Francyne, Couto, Eduarda, Brum, Bruna, Rodrigues, Graziella, Souza, Hallana, Giugliani, Roberto, Matte, Ursula, Baldo, Guilherme, Teixeira, Helder F.
Published in The journal of gene medicine (01.04.2022)
Published in The journal of gene medicine (01.04.2022)
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Identification of Ezetimibe and Pranlukast as Pharmacological Chaperones for the Treatment of the Rare Disease Mucopolysaccharidosis Type IVA
Alméciga-Diaz, Carlos J, Hidalgo, Oscar A, Olarte-Avellaneda, Sergio, Rodríguez-López, Alexander, Guzman, Esteban, Garzón, Rafael, Pimentel-Vera, Luisa Natalia, Puentes-Tellez, María Alejandra, Rojas-Rodriguez, Andrés Felipe, Gorshkov, Kirill, Li, Rong, Zheng, Wei
Published in Journal of medicinal chemistry (11.07.2019)
Published in Journal of medicinal chemistry (11.07.2019)
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Effect of genistein and coenzyme Q10 in oxidative damage and mitochondrial membrane potential in an attenuated type II mucopolysaccharidosis cellular model
Delgado, Camila Aguilar, Poletto, Edina, Vera, Luisa Natalia Pimentel, Jacques, Carlos Eduardo Diaz, Vianna, Priscila, Reinhardt, Luiza Steffens, Baldo, Guilherme, Vargas, Carmen Regla
Published in Cell biochemistry and function (01.03.2024)
Published in Cell biochemistry and function (01.03.2024)
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Journal Article
In Situ Gene Therapy
Santos, Hallana Souza, Rodrigues, Luiza, Vera, Luisa Natalia Pimentel, Poletto, Edina, Filippi-Chiela, Eduardo, Dos Santos Bruschi, Lia Franciê Ribeiro, Schuh, Roselena, Baldo, Guilherme
Published in Current gene therapy (01.01.2021)
Published in Current gene therapy (01.01.2021)
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Comparison of different DNA preservation solutions for oral cytological samples
Nunes, Júlia Silveira, Pimentel-Vera, Luisa Natalia, Silva, Sabrina Barcelos, de Bem Prunes, Bianca, Rados, Pantelis Varvaki, Visioli, Fernanda
Published in Archives of oral biology (01.02.2024)
Published in Archives of oral biology (01.02.2024)
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Evaluation of oxidative stress and mitochondrial function in a type II mucopolysaccharidosis cellular model: in vitro effects of genistein and coenzyme Q10
Jacques, Carlos Eduardo Diaz, Lopes, Franciele Fátima, Poletto, Edina, Vera, Luisa Natalia Pimentel, Vianna, Priscila, Reinhardt, Luiza Steffens, Baldo, Guilherme, Vargas, Carmen Regla
Published in Metabolic brain disease (01.02.2023)
Published in Metabolic brain disease (01.02.2023)
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Journal Article
CNS Repopulation by Hematopoietic-Derived Microglia-Like Cells Corrects Progranulin deficiency
Colella, Pasqualina, Sayana, Ruhi, Suarez-Nieto, Maria Valentina, Sarno, Jolanda, Nyame, Kwamina, Xiong, Jian, Vera, Luisa Natalia Pimentel, Basurto, Jessica Arozqueta, Corbo, Marco, Limaye, Anay, Davis, Kara Lynn, Abu-Remaileh, Monther, Gomez-Ospina, Natalia
Published in Research square (12.09.2023)
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Published in Research square (12.09.2023)
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