Therapeutic potential of highly functional codon-optimized microutrophin for muscle-specific expression
Starikova, Anna V, Skopenkova, Victoria V, Polikarpova, Anna V, Reshetov, Denis A, Vassilieva, Svetlana G, Velyaev, Oleg A, Shmidt, Anna A, Savchenko, Irina M, Soldatov, Vladislav O, Egorova, Tatiana V, Bardina, Maryana V
Published in Scientific reports (17.01.2022)
Published in Scientific reports (17.01.2022)
Get full text
Journal Article
In-Frame Deletion of Dystrophin Exons 8-50 Results in DMD Phenotype
Egorova, Tatiana V, Galkin, Ivan I, Velyaev, Oleg A, Vassilieva, Svetlana G, Savchenko, Irina M, Loginov, Vyacheslav A, Dzhenkova, Marina A, Korshunova, Diana S, Kozlova, Olga S, Ivankov, Dmitry N, Polikarpova, Anna V
Published in International journal of molecular sciences (23.05.2023)
Published in International journal of molecular sciences (23.05.2023)
Get full text
Journal Article
In vitro assay for the efficacy assessment of AAV vectors expressing microdystrophin
Danilov, Kirill A., Vassilieva, Svetlana G., Polikarpova, Anna V., Starikova, Anna V., Shmidt, Anna A., Galkin, Ivan I., Tsitrina, Alexandra A., Egorova, Tatiana V., Orlov, Sergei N., Kotelevtsev, Yuri V.
Published in Experimental cell research (15.07.2020)
Published in Experimental cell research (15.07.2020)
Get full text
Journal Article
CRISPR/Cas9-generated mouse model of Duchenne muscular dystrophy recapitulating a newly identified large 430 kb deletion in the human DMD gene
Egorova, Tatiana V, Zotova, Evgenia D, Reshetov, Denis A, Polikarpova, Anna V, Vassilieva, Svetlana G, Vlodavets, Dmitry V, Gavrilov, Alexey A, Ulianov, Sergey V, Buchman, Vladimir L, Deykin, Alexei V
Published in Disease models & mechanisms (01.04.2019)
Published in Disease models & mechanisms (01.04.2019)
Get full text
Journal Article
CRISPR-Cas9 correction in the DMD mouse model is accompanied by upregulation of Dp71f protein
Egorova, Tatiana V., Polikarpova, Anna V., Vassilieva, Svetlana G., Dzhenkova, Marina A., Savchenko, Irina M., Velyaev, Oleg A., Shmidt, Anna A., Soldatov, Vladislav O., Pokrovskii, Mikhail V., Deykin, Alexey V., Bardina, Maryana V.
Published in Molecular therapy. Methods & clinical development (14.09.2023)
Published in Molecular therapy. Methods & clinical development (14.09.2023)
Get full text
Journal Article
CRISPR/Cas9-generated mouse model with humanizing single-base substitution in the Gnao1 for safety studies of RNA therapeutics
Polikarpova, Anna V, Egorova, Tatiana V, Lunev, Evgenii A, Tsitrina, Alexandra A, Vassilieva, Svetlana G, Savchenko, Irina M, Silaeva, Yuliya Y, Deykin, Alexey V, Bardina, Maryana V
Published in Frontiers in genome editing (03.04.2023)
Published in Frontiers in genome editing (03.04.2023)
Get full text
Journal Article
RNA Interference Effectors Selectively Silence the Pathogenic Variant GNAO1 c.607 G > A In Vitro
Klementieva, Natalia V, Lunev, Evgenii A, Shmidt, Anna A, Loseva, Elizaveta M, Savchenko, Irina M, Svetlova, Ekaterina A, Galkin, Ivan I, Polikarpova, Anna V, Usachev, Evgeny V, Vassilieva, Svetlana G, Marina, Valeria I, Dzhenkova, Marina A, Romanova, Anna D, Agutin, Anton V, Timakova, Anna A, Reshetov, Denis A, Egorova, Tatiana V, Bardina, Maryana V
Published in Nucleic acid therapeutics (01.04.2024)
Published in Nucleic acid therapeutics (01.04.2024)
Get more information
Journal Article