A lung tropic AAV vector improves survival in a mouse model of surfactant B deficiency
Kang, Martin H, van Lieshout, Laura P, Xu, Liqun, Domm, Jakob M, Vadivel, Arul, Renesme, Laurent, Mühlfeld, Christian, Hurskainen, Maria, Mižíková, Ivana, Pei, Yanlong, van Vloten, Jacob P, Thomas, Sylvia P, Milazzo, Claudia, Cyr-Depauw, Chanèle, Whitsett, Jeffrey A, Nogee, Lawrence M, Wootton, Sarah K, Thébaud, Bernard
Published in Nature communications (06.08.2020)
Published in Nature communications (06.08.2020)
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Journal Article
A promoterless AAV6.2FF-based lung gene editing platform for the correction of surfactant protein B deficiency
Thomas, Sylvia P., Domm, Jakob M., van Vloten, Jacob P., Xu, Liqun, Vadivel, Arul, Yates, Jacob G.E., Pei, Yanlong, Ingrao, Joelle, van P. Lieshout, Laura, Jackson, Sergio R., Minott, Jessica A., Achuthan, Adithya, Mehrani, Yeganeh, McAusland, Thomas M., Zhang, Wei, Karimi, Khalil, Vaughan, Andrew E., de Jong, Jondavid, Kang, Martin H., Thebaud, Bernard, Wootton, Sarah K.
Published in Molecular therapy (06.12.2023)
Published in Molecular therapy (06.12.2023)
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Journal Article
AAV vector distribution in the mouse respiratory tract following four different methods of administration
Santry, Lisa A, Ingrao, Joelle C, Yu, Darrick L, de Jong, Jondavid G, van Lieshout, Laura P, Wood, Geoffrey A, Wootton, Sarah K
Published in BMC biotechnology (15.05.2017)
Published in BMC biotechnology (15.05.2017)
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Journal Article
A Novel Triple-Mutant AAV6 Capsid Induces Rapid and Potent Transgene Expression in the Muscle and Respiratory Tract of Mice
van Lieshout, Laura P, Domm, Jakob M, Rindler, Tara N, Frost, Kathy L, Sorensen, Debra L, Medina, Sarah J, Booth, Stephanie A, Bridges, James P, Wootton, Sarah K
Published in Molecular therapy. Methods & clinical development (15.06.2018)
Published in Molecular therapy. Methods & clinical development (15.06.2018)
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Journal Article
AAV Vectors Pseudotyped with Capsids from Porcine and Bovine Species Mediate In Vitro and In Vivo Gene Delivery
Yu, Darrick L, van Lieshout, Laura P, Stevens, Brenna A Y, Near, Kelsie J Jagt, Stodola, Jenny K, Stinson, Kevin J, Slavic, Durda, Wootton, Sarah K
Published in Viruses (29.12.2023)
Published in Viruses (29.12.2023)
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Journal Article
A novel dual-plasmid platform provides scalable transfection yielding improved productivity and packaging across multiple AAV serotypes and genomes
van Lieshout, Laura P., Rubin, Miranda, Costa-Grant, Katrina, Ota, Stacy, Golebiowski, Diane, Panico, Troy, Wiberg, Eli, Szymczak, Klaudia, Gilmore, Richard, Stanvick, Marissa, Burnham, Brenda, Gagnon, Jeff, Iwuchukwu, Ifeyinwa, Yang, Guang, Ghazi, Iraj, Meola, Alex, Dickerson, Ryan, Thiers, Thomas, Mustich, Luke, Hayes, April, Rivas, Israel, Lotterhand, Jason, Avila, Nancy, McGivney, James, Yin, Jin, Kelly, Tim
Published in Molecular therapy. Methods & clinical development (08.06.2023)
Published in Molecular therapy. Methods & clinical development (08.06.2023)
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Journal Article
TLR4 inhibition impairs bacterial clearance in a therapeutic setting in murine abdominal sepsis
van Lieshout, Miriam H. P., van der Poll, Tom, van’t Veer, Cornelis
Published in Inflammation research (01.11.2014)
Published in Inflammation research (01.11.2014)
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Journal Article
AAV-monoclonal antibody expression protects mice from Ebola virus without impeding the endogenous antibody response to heterologous challenge
van Lieshout, Laura P., Rghei, Amira D., Cao, Wenguang, He, Shihua, Soule, Geoff, Zhu, Wenjun, Thomas, Sylvia P., Sorensen, Debra, Frost, Kathy, Tierney, Kevin, Thompson, Brad, Booth, Stephanie, Safronetz, David, Kulkarni, Raveendra R., Bridle, Byram W., Qiu, Xiangguo, Banadyga, Logan, Wootton, Sarah K.
Published in Molecular therapy. Methods & clinical development (08.09.2022)
Published in Molecular therapy. Methods & clinical development (08.09.2022)
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Journal Article
AAV Vectored Immunoprophylaxis for Filovirus Infections
Rghei, Amira D., van Lieshout, Laura P., Santry, Lisa A., Guilleman, Matthew M., Thomas, Sylvia P., Susta, Leonardo, Karimi, Khalil, Bridle, Byram W., Wootton, Sarah K.
Published in Tropical medicine and infectious disease (09.11.2020)
Published in Tropical medicine and infectious disease (09.11.2020)
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Journal Article
The U3 and Env Proteins of Jaagsiekte Sheep Retrovirus and Enzootic Nasal Tumor Virus Both Contribute to Tissue Tropism
Rosales Gerpe, María C, van Lieshout, Laura P, Domm, Jakob M, Ingrao, Joelle C, Datu, Jodre, Walsh, Scott R, Yu, Darrick L, Jong, Jondavid de, Krell, Peter J, Wootton, Sarah K
Published in Viruses (14.11.2019)
Published in Viruses (14.11.2019)
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Journal Article
ASC and NLRP3 impair host defense during lethal pneumonia caused by serotype 3 Streptococcus pneumoniae in mice
Lieshout, Miriam H.P., Vos, Alex F., Dessing, Mark C., Porto, Alexander P.N.A., Boer, Onno J., Beer, Regina, Terpstra, Sanne, Florquin, Sandrine, van't Veer, Cornelis, der Poll, Tom
Published in European journal of immunology (01.01.2018)
Published in European journal of immunology (01.01.2018)
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Journal Article
Safety and Tolerability of the Adeno-Associated Virus Vector, AAV6.2FF, Expressing a Monoclonal Antibody in Murine and Ovine Animal Models
Rghei, Amira D., van Lieshout, Laura P., McLeod, Benjamin M., Pei, Yanlong, Lopes, Jordyn A., Zielinska, Nicole, Baracuhy, Enzo M., Stevens, Brenna A. Y., Thomas, Sylvia P., Yates, Jacob G. E., Warner, Bryce M., Kobasa, Darwyn, Fausther-Bovendo, Hugues, Kobinger, Gary P., Karimi, Khalil, Thompson, Brad, Bridle, Byram W., Susta, Leonardo, Wootton, Sarah K.
Published in Biomedicines (09.09.2021)
Published in Biomedicines (09.09.2021)
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Journal Article
Hematopoietic but not endothelial cell MyD88 contributes to host defense during gram-negative pneumonia derived sepsis
van Lieshout, Miriam H P, Anas, Adam A, Florquin, Sandrine, Hou, Baidong, van't Veer, Cornelis, de Vos, Alex F, van der Poll, Tom
Published in PLoS pathogens (01.09.2014)
Published in PLoS pathogens (01.09.2014)
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Journal Article
A novel baseline model-based technique for condition monitoring of wind turbine components
Hills, A F, Lang, Z Q, Soua, S, Gan, T-H, Perera, A, van Lieshout, P, Grainger, B
Published in Insight (Northampton) (01.08.2011)
Published in Insight (Northampton) (01.08.2011)
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Journal Article
R-roscovitine reduces lung inflammation induced by lipoteichoic acid and Streptococcus pneumoniae
Hoogendijk, Arie J, Roelofs, Joris J T H, Duitman, Janwillem, van Lieshout, Miriam H P, Blok, Dana C, van der Poll, Tom, Wieland, Catharina W
Published in Molecular medicine (Cambridge, Mass.) (01.07.2012)
Published in Molecular medicine (Cambridge, Mass.) (01.07.2012)
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