Hematopoietic stem cell gene therapy ameliorates CNS involvement in murine model of GM1-gangliosidosis
Tsunogai, Toshiki, Ohashi, Toya, Shimada, Yohta, Higuchi, Takashi, Kimura, Ayaka, Watabe, Ayako M., Kato, Fusao, Ida, Hiroyuki, Kobayashi, Hiroshi
Published in Molecular therapy. Methods & clinical development (09.06.2022)
Published in Molecular therapy. Methods & clinical development (09.06.2022)
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Journal Article
Hematopoietic stem cell gene therapy ameliorates CNS involvement in murine model of GM1-gangliosidosis
Tsunogai, Toshiki, Ohashi, Toya, Shimada, Yohta, Higuchi, Takashi, Kimura, Ayaka, Watabe, Ayako M., Kato, Fusao, Ida, Hiroyuki, Kobayashi, Hiroshi
Published in Molecular therapy. Methods & clinical development (08.12.2022)
Published in Molecular therapy. Methods & clinical development (08.12.2022)
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Journal Article
A novel NR3C2 mutation in a Japanese patient with the renal form of pseudohypoaldosteronism type 1
Tsunogai, Toshiki, Miyata, Ichiro, Kotake, Saori, Matsuura, Ryuki, Takagi, Ken, Nanba, Hiroyuki, Takahata, Noriko, Tajima, Toshihiro, Wada, Yasuyuki
Published in Clinical Pediatric Endocrinology (01.01.2016)
Published in Clinical Pediatric Endocrinology (01.01.2016)
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Journal Article
A novel NR3C2 mutation in a Japanese patient with the renal form of pseudohypoaldosteronism type 1
Toshiki Tsunogai, Ichiro Miyata, Saori Kotake, Ryuki Matsuura, Ken Takagi, Hiroyuki Nanba, Noriko Takahata, Toshihiro Tajima, Yasuyuki Wada
Published in Clinical Pediatric Endocrinology (01.07.2016)
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Published in Clinical Pediatric Endocrinology (01.07.2016)
Journal Article
Erratum: Hematopoietic stem cell gene therapy ameliorates CNS involvement in murine model of GM1-gangliosidosis
Tsunogai, Toshiki, Ohashi, Toya, Shimada, Yohta, Higuchi, Takashi, Kimura, Ayaka, Watabe, Ayako M, Kato, Fusao, Ida, Hiroyuki, Kobayashi, Hiroshi
Published in Molecular therapy. Methods & clinical development (08.12.2022)
Published in Molecular therapy. Methods & clinical development (08.12.2022)
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Journal Article
Aggressive B-Cell Lymphoma Involving the Appendix and Bilateral Ovaries in an 11-Year-Old Girl
Tsunogai, Toshiki, Yamaoka, Masayoshi, Ohyama, Wataru, Honda, Takaya, Kusuhara, Atsuko, Akiyama, Masaharu
Published in Journal of pediatric & adolescent gynecology (01.08.2020)
Published in Journal of pediatric & adolescent gynecology (01.08.2020)
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