PABPN1 gene therapy for oculopharyngeal muscular dystrophy
Malerba, A., Klein, P., Bachtarzi, H., Jarmin, S. A., Cordova, G., Ferry, A., Strings, V., Espinoza, M. Polay, Mamchaoui, K., Blumen, S. C., St Guily, J. Lacau, Mouly, V., Graham, M., Butler-Browne, G., Suhy, D. A., Trollet, C., Dickson, G.
Published in Nature communications (31.03.2017)
Published in Nature communications (31.03.2017)
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Generation of High-Titer Neutralizing Antibodies against Botulinum Toxins A, B, and E by DNA Electrotransfer
TROLLET, C, PEREIRA, Y, BURGAIN, A, LITZLER, E, MEZRAHI, M, SEGUIN, J, MANICH, M, POPOFF, M. R, SCHERMAN, D, BIGEY, P
Published in Infection and Immunity (01.05.2009)
Published in Infection and Immunity (01.05.2009)
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Gene replacement therapy as a novel approach for the treatment of oculopharyngeal muscular dystrophy
Malerba, A, Klein, P, Bachtarzi, H, Jarmin, S, Ferry, A, Graham, M, Strings, V, Butler-Browne, G, Suhy, D, Dickson, G, Trollet, C
Published in Neuromuscular disorders : NMD (01.10.2016)
Published in Neuromuscular disorders : NMD (01.10.2016)
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P9 Adeno-associated virus (AAV)-mediated RNA interference to PABPN1 combined with an optimised resistant transgene for rescue of the muscle specific disease oculopharyngeal muscular dystrophy (OPMD)
Bachtarzi, H, Malerba, A, Jarmin, S, Trollet, C, Graham, M, Dickson, J.G
Published in Neuromuscular disorders : NMD (01.03.2014)
Published in Neuromuscular disorders : NMD (01.03.2014)
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G.O.5
Trollet, C, Chartier, A, Klein, P, Barbezier, N, Gidaro, T, Casas, F, Carberry, S, Dowling, P, Maynadier, L, Dickson, G, Mouly, V, Ohlendieck, K, Butler-Browne, G, Simonelig, M
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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O01 Autologous cell therapy in oculopharyngeal muscular dystrophy (OPMD)
Périé, S, Trollet, C, Mouly, V, Larghero, J, Mamchaoui, K, Bouazza, B, Toy-Miou, M, Marolleau, J.P, Eymard, B, Laforêt, P, Chapon, F, Butler-Browne, G, Guily, J. Lacau St
Published in Neuromuscular disorders : NMD (01.03.2014)
Published in Neuromuscular disorders : NMD (01.03.2014)
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P.16.12 OPMD from the myoblast’s and fibroblast’s point of view
Gidaro, T, Negroni, E, Klein, P, Oloko, M, Lesnik, M, Bigot, A, Mamchaoui, K, Périé, S, Guily, J.L. St, Butler-Browne, G, Mouly, V, Trollet, C
Published in Neuromuscular disorders : NMD (01.10.2013)
Published in Neuromuscular disorders : NMD (01.10.2013)
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G.P.106 Immunohistochemical study of cricopharyngeal muscle in oculopharyngeal muscular dystrophy
Gidaro, T, Perié, S, Lesnik, M, Negroni, E, Oloko, M, st Guily, J. Lacau, Butler-Browne, G, Mouly, V, Trollet, C
Published in Neuromuscular disorders : NMD (01.10.2012)
Published in Neuromuscular disorders : NMD (01.10.2012)
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P2.45 Proteomic studies of muscle progenitor cells in affected and non-affected oculopharyngeal muscular dystrophy muscles
Gidaro, T, Mamchaoui, K, Bouazza, B, Perié, S, Svinartchouk, F, Blumen, S, Guily, J.J.S, Butler-Browne, G, Mouly, V, Trollet, C
Published in Neuromuscular disorders : NMD (01.10.2011)
Published in Neuromuscular disorders : NMD (01.10.2011)
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D.P.4.11 Expression and siRNA targeting of PABPN1 as a model for oculopharyngeal muscular dystrophy (OPMD)
Trollet, C, Benstead, J, Graham, I, Yáñez, R, Antoniou, M, Dickson, G
Published in Neuromuscular disorders : NMD (01.10.2008)
Published in Neuromuscular disorders : NMD (01.10.2008)
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G.P.8.08 Codon optimisation of microdystrophin results in improvements in expression and physiological outcome in the mdx mouse following AAV8 gene transfer
Foster, H, Wells, D.J, Trollet, C, Athanasopoulos, T, Graham, I, Foster, K, Dickson, J.G
Published in Neuromuscular disorders : NMD (01.10.2008)
Published in Neuromuscular disorders : NMD (01.10.2008)
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Optical imaging of luminescence for in vivo quantification of gene electrotransfer in mouse muscle and knee
Bloquel, C, Trollet, C, Pradines, E, Seguin, J, Scherman, D, Bureau, M F
Published in BMC biotechnology (08.03.2006)
Published in BMC biotechnology (08.03.2006)
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G.P.8.09 Evaluating the potential of AAV8 mediated intravenous transfer of myostatin propeptide to ameliorate the muscle pathology in mdx mouse
Foster, K, Graham, I, Foster, H, Trollet, C, Yaworsky, P, Walsh, F, Sharp, P, Wells, D, Dickson, G
Published in Neuromuscular disorders : NMD (01.10.2008)
Published in Neuromuscular disorders : NMD (01.10.2008)
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T.P.1.09 Oculopharyngeal muscular dystrophy (OPMD): Physiopathological mechanisms and gene therapy approaches
Trollet, C, Bales, O, Anvar, Y, Foster, K, Mamchaoui, K, t Hoen, P.A, Raz, V, van der Maarel, S, Antoniou, M, Mouly, V, Butler-Browne, G, Dickson, G
Published in Neuromuscular disorders : NMD (01.09.2009)
Published in Neuromuscular disorders : NMD (01.09.2009)
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P176 Immortalized human muscle cells: easy-to-use models to study neuromuscular diseases
Butler-Browne, G., Ohana, J., Mamchaoui, K., Bensalah, M., Negroni, E., Trollet, C., Bigot, A., Mouly, V.
Published in Neuromuscular disorders : NMD (01.10.2023)
Published in Neuromuscular disorders : NMD (01.10.2023)
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594P FUS/TLS as a potential regulator of PABPN1 in skeletal muscle?
Mouigni, H., Altin, N., Ohana, J., Kondili, M., Dhiab, J., Muraine, L., Lemaitre, M., Meunier, P., Butler-Browne, G., Mouly, V., Bigot, A., Negroni, E., Trollet, C.
Published in Neuromuscular disorders : NMD (01.10.2024)
Published in Neuromuscular disorders : NMD (01.10.2024)
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268P Age and sex affect human skeletal muscle secretome
Crisol, B., Pinzon, N., Orio, J., Gaut-Serey, L., Ohana, J., Bensalah, M., Peterson, C., Butler-Browne, G., Mouly, V., Bigot, A., Trollet, C.
Published in Neuromuscular disorders : NMD (01.10.2024)
Published in Neuromuscular disorders : NMD (01.10.2024)
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Saving dopaminergic neurons from endoplasmic reticulum (ER) stress - A breakthrough approach to fight Parkinson's disease
Gentile, L., Nasir, A., Sinane, M., Conan, P., Ückert, A.-K., Leist, M., Friocourt, G., Trollet, C., Bihel, F., Voisset, C.
Published in Parkinsonism & related disorders (01.05.2024)
Published in Parkinsonism & related disorders (01.05.2024)
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P166 Deciphering the genetic cause of oculopharyngodistal myopathy in a French cohort using Cas9-targeted long-read sequencing
Benarroch, L., Nelson, I., Stojkovic, T., Oumoussa, B Mohand, Madry, H., Boelle, P., Labreche, K., Tomé, S., Trollet, C., Bonne, G.
Published in Neuromuscular disorders : NMD (01.10.2023)
Published in Neuromuscular disorders : NMD (01.10.2023)
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