Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNA
Dupont, Jean-Baptiste, Tournaire, Benoit, Georger, Christophe, Marolleau, Béatrice, Jeanson-Leh, Laurence, Ledevin, Mireille, Lindenbaum, Pierre, Lecomte, Emilie, Cogné, Benjamin, Dubreil, Laurence, Larcher, Thibaut, Gjata, Bernard, Van Wittenberghe, Laetitia, Le Guiner, Caroline, Penaud-Budloo, Magalie, Snyder, Richard O, Moullier, Philippe, Léger, Adrien
Published in Molecular therapy. Methods & clinical development (01.01.2015)
Published in Molecular therapy. Methods & clinical development (01.01.2015)
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Advanced Characterization of DNA Molecules in rAAV Vector Preparations by Single-stranded Virus Next-generation Sequencing
Lecomte, Emilie, Tournaire, Benoît, Cogné, Benjamin, Dupont, Jean-Baptiste, Lindenbaum, Pierre, Martin-Fontaine, Mélanie, Broucque, Frédéric, Robin, Cécile, Hebben, Matthias, Merten, Otto-Wilhelm, Blouin, Véronique, François, Achille, Redon, Richard, Moullier, Philippe, Léger, Adrien
Published in Molecular therapy. Nucleic acids (27.10.2015)
Published in Molecular therapy. Nucleic acids (27.10.2015)
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Accurate Identification and Quantification of DNA Species by Next-Generation Sequencing in Adeno-Associated Viral Vectors Produced in Insect Cells
Penaud-Budloo, Magalie, Lecomte, Emilie, Guy-Duché, Aurélien, Saleun, Sylvie, Roulet, Alain, Lopez-Roques, Céline, Tournaire, Benoît, Cogné, Benjamin, Léger, Adrien, Blouin, Véronique, Lindenbaum, Pierre, Moullier, Philippe, Ayuso, Eduard
Published in Human gene therapy. Part B. Methods (01.06.2017)
Published in Human gene therapy. Part B. Methods (01.06.2017)
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Journal Article
390. Impact of a Treatment with Antioxidant on Gene Transfer Efficiency After Recombinant Adeno-Associated Vector Injection in a Mouse Model of Duchenne Muscular Dystrophy
Dupont, Jean-Baptiste, Tournaire, Benoît, Durand, Romain, Marolleau, Béatrice, Bertil, Emilie, Georger, Christophe, Lecomte, Emilie, Cogné, Benjamin, Gjata, Bernard, vanWittenberghe, Laetitia, Vignaud, Alban, Snyder, Richard O., Moullier, Philippe, Léger, Adrien
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
Impact d’un traitement antioxydant sur le transfert de gène par un vecteur AAVr dans un modèle murin de la dystrophie musculaire de Duchenne
Dupont, Jean-Baptiste, Tournaire, Benoît, Durand, Romain, Marolleau, Béatrice, Bertil, Émilie, Georger, Christophe, Lecomte, Émilie, Cogné, Benjamin, Gjata, Bernard, Van Wittenberghe, Laetitia, Vignaud, Alban, Snyder, Richard O., Moullier, Philippe, Léger, Adrien
Published in Les Cahiers de Myologie (01.06.2016)
Published in Les Cahiers de Myologie (01.06.2016)
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Journal Article
Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNA
Dupont, Jean-Baptiste, Tournaire, Benoit, Georger, Christophe, Marolleau, Béatrice, Jeanson-Leh, Laurence, Ledevin, Mireille, Lindenbaum, Pierre, Lecomte, Emilie, Cogné, Benjamin, Dubreil, Laurence, Larcher, Thibaut, Gjata, Bernard, Van Wittenberghe, Laetitia, Le Guiner, Caroline, Penaud-Budloo, Magalie, Snyder, Richard O, Moullier, Philippe, Léger, Adrien
Published in Molecular therapy. Methods and clinical development (2), 15010. (2015) (2015)
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Published in Molecular therapy. Methods and clinical development (2), 15010. (2015) (2015)
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Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNA
Dupont, Jean-Baptiste, Tournaire, Benoit, Georger, Christophe, Marolleau, Béatrice, Jeanson-Leh, Laurence, Ledevin, Mireille, Lindenbaum, Pierre, Lecomte, Emilie, Cogné, Benjamin, Dubreil, Laurence, Larcher, Thibaut, Gjata, Bernard, Van Wittenberghe, Laetitia, Le Guiner, Caroline, Penaud-Budloo, Magalie, Snyder, Richard O, Moullier, Philippe, Léger, Adrien
Published in Molecular therapy. Methods and clinical development (2), 15010. (2015) (2015)
Get more information
Published in Molecular therapy. Methods and clinical development (2), 15010. (2015) (2015)
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