Predictors of Loss of Ambulation in Duchenne Muscular Dystrophy: A Systematic Review and Meta-Analysis
Landfeldt, E, Alemán, A, Abner, S, Zhang, R, Werner, C, Tomazos, I, Ferizovic, N, Lochmüller, H, Kirschner, J
Published in Journal of neuromuscular diseases (01.01.2024)
Published in Journal of neuromuscular diseases (01.01.2024)
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Journal Article
Factors Associated with Respiratory Health and Function in Duchenne Muscular Dystrophy: A Systematic Review and Evidence Grading
Landfeldt, E, Aleman, A, Abner, S, Zhang, R, Werner, C, Tomazos, I, Lochmüller, H, Quinlivan, R M
Published in Journal of neuromuscular diseases (01.01.2024)
Published in Journal of neuromuscular diseases (01.01.2024)
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Journal Article
PB1934: REAL‐WORLD OUTCOMES OF ECULIZUMAB TREATMENT IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINUREA: A SYSTEMATIC LITERATURE REVIEW AND EVIDENCE SYNTHESIS
Nishimura, J.‐I., Popoff, E., Cheung, A., Wang, A., Tomazos, I., Szer, J.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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Low Rate of Clinically Evident Extravascular Hemolysis in Patients with Paroxysmal Nocturnal Hemoglobinuria Treated with a Complement C5 Inhibitor: Results from a Large, Multicenter, US Real-World Study
Shammo, Jamile, Gajra, Ajeet, Patel, Yogesh, Tomazos, Ioannis, Kish, Jonathan, Hill, Anita, Sierra, J. Rafael, Araten, David
Published in Journal of blood medicine (01.01.2022)
Published in Journal of blood medicine (01.01.2022)
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P813: EFFICACY, TREATMENT ADMINISTRATION SATISFACTION AND SAFETY OF SUBCUTANEOUS RAVULIZUMAB THROUGH 1 YEAR IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA WHO RECEIVED PRIOR INTRAVENOUS ECULIZUMAB
Yenerel, M. N., Sicre de Fontbrune, F., Piatek, C., Sahin, F., Füreder, W., Ogawa, M., Tomazos, I., Doll, H., Ozol-Godfrey, A., Sierra, J. R., Szer, J.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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CO160 Relationship between Loss of Ambulation (LoA), Disease Burden, and Physical Functioning Among Boys with Duchenne Muscular Dystrophy (DMD)
Gordish-Dressman, H.., Zhang, R., Kamstra, R., Werner, C., Liu, E., Morrison, K., Tomazos, I.
Published in Value in health (01.06.2024)
Published in Value in health (01.06.2024)
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Journal Article
CO120 Progression of Disease Burden Among Boys with Duchenne Muscular Dystrophy (DMD) According to Ambulatory Status and Age at Loss of Ambulation (LoA)
Gordish-Dressman, H.., Zhang, R., Kamstra, R., Werner, C., Liu, E., Morrison, K., Tomazos, I.
Published in Value in health (01.06.2024)
Published in Value in health (01.06.2024)
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Journal Article
CO142 A Retrospective Study Characterizing Age at Key Clinical Disease Indicators Among Patients With Friedreich Ataxia Using Health Administrative Claims Data in the United States
Salvucci, A., Qian, C., Powell, L., Lynch, D., Vasco, G., Johnston, K., Tomazos, I.
Published in Value in health (01.12.2023)
Published in Value in health (01.12.2023)
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Journal Article
CO105 A Retrospective Study Characterizing Age at Loss of Ambulation Among Patients With Friedreich Ataxia Using Health Administrative Claims Data in the United States
Salvucci, A., Qian, C., Powell, L., Lynch, D., Vasco, G., Johnston, K., Tomazos, I.
Published in Value in health (01.12.2023)
Published in Value in health (01.12.2023)
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Journal Article
PCR139 'We Have Conversations That Other Couples Don′t Have to Have:' A Qualitative Study of the Impact of Caregiving in Friedreich Ataxia (FA)
Szabo, S., Bever, A., Lynch, D., Vasco, G., Giunti, P., Vallortigara, J., Tomazos, I.
Published in Value in health (01.12.2023)
Published in Value in health (01.12.2023)
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Journal Article
PCR84 The Daily Life and Psychosocial Impacts of Friedreich Ataxia: A Qualitative Study of Patient Lived Experiences
Bever, A., Szabo, S., Vallortigara, J., Giunti, P., Lynch, D., Vasco, G., Tomazos, I.
Published in Value in health (01.12.2023)
Published in Value in health (01.12.2023)
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Journal Article
RWD59 Association of Time of Loss of Ambulation with Severity of Respiratory Symptoms in Patients with Nonsense Mutation Duchenne Muscular Dystrophy (NMDMD)
Tulinius, M., Zhang, R., Lee, B., Madin-Warburton, M., Werner, C., Tomazos, I.
Published in Value in health (01.06.2023)
Published in Value in health (01.06.2023)
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SA70 Patient-Reported Outcomes and Daily Activity Assessed with a Digital Wearable Device (FITBIT™) in Patients with Paroxysmal Nocturnal Hemoglobinuria Treated with Ravulizumab: The Reveal Study
Griffiths, E.A, Wang, A., Tomazos, I., Min, J.S, Lee, W.N, Patel, Y., Yu, J., Dingli, D.
Published in Value in health (01.06.2023)
Published in Value in health (01.06.2023)
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Journal Article
RWD99 The Clinical Burden of Friedreich Ataxia: A Retrospective Claims Analysis in the United States
Powell, L., Lynch, D., Qian, C., Salvucci, A., Vasco, G., Johnston, K.M, Tomazos, I.
Published in Value in health (01.06.2023)
Published in Value in health (01.06.2023)
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