Ocular Inflammatory Response to Intravitreal Injection of Adeno-Associated Virus Vector: Relative Contribution of Genome and Capsid
Timmers, Adrian M, Newmark, Judith A, Turunen, Heikki T, Farivar, Tanaz, Liu, Jilin, Song, Chunjuan, Ye, Guo-Jie, Pennock, Steven, Gaskin, Chantelle, Knop, David R, Shearman, Mark S
Published in Human gene therapy (01.01.2020)
Published in Human gene therapy (01.01.2020)
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Journal Article
Restoration of cone vision in a mouse model of achromatopsia
Hauswirth, William W, Alexander, John J, Umino, Yumiko, Everhart, Drew, Chang, Bo, Min, Seok H, Li, Qiuhong, Timmers, Adrian M, Hawes, Norman L, Pang, Ji-jing, Barlow, Robert B
Published in Nature medicine (01.06.2007)
Published in Nature medicine (01.06.2007)
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Journal Article
A Muscleblind Knockout Model for Myotonic Dystrophy
Kanadia, Rahul N., Johnstone, Karen A., Mankodi, Ami, Lungu, Codrin, Thornton, Charles A., Esson, Douglas, Timmers, Adrian M., Hauswirth, William W., Swanson, Maurice S.
Published in Science (American Association for the Advancement of Science) (12.12.2003)
Published in Science (American Association for the Advancement of Science) (12.12.2003)
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Journal Article
Dose Range Finding Studies with Two RPGR Transgenes in a Canine Model of X-Linked Retinitis Pigmentosa Treated with Subretinal Gene Therapy
Song, Chunjuan, Dufour, Valérie L, Cideciyan, Artur V, Ye, Guo-Jie, Swider, Malgorzata, Newmark, Judith A, Timmers, Adrian M, Robinson, Paulette M, Knop, David R, Chulay, Jeffrey D, Jacobson, Samuel G, Aguirre, Gustavo D, Beltran, William A, Shearman, Mark S
Published in Human gene therapy (01.07.2020)
Published in Human gene therapy (01.07.2020)
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Journal Article
Prolonged recovery of retinal structure/function after gene therapy in an Rs1h-deficient mouse model of x-linked juvenile retinoschisis
Min, Seok H, Molday, Laurie L, Seeliger, Mathias W, Dinculescu, Astra, Timmers, Adrian M, Janssen, Andreas, Tonagel, Felix, Tanimoto, Naoyuki, Weber, Bernhard H F, Molday, Robert S, Hauswirth, William W
Published in Molecular therapy (01.10.2005)
Published in Molecular therapy (01.10.2005)
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Journal Article
Cone-specific expression using a human red opsin promoter in recombinant AAV
Li, Qiuhong, Timmers, Adrian M., Guy, John, Pang, Jijing, Hauswirth, William W.
Published in Vision research (Oxford) (01.02.2008)
Published in Vision research (Oxford) (01.02.2008)
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Journal Article
Human Blue-Opsin Promoter Preferentially Targets Reporter Gene Expression to Rat S-Cone Photoreceptors
Glushakova, Lyudmyla G, Timmers, Adrian M, Pang, Jijing, Teusner, Jacqueline T, Hauswirth, William W
Published in Investigative ophthalmology & visual science (01.08.2006)
Published in Investigative ophthalmology & visual science (01.08.2006)
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Journal Article
Preventing Stem Cell Incorporation into Choroidal Neovascularization by Targeting Homing and Attachment Factors
Sengupta, Nilanjana, Caballero, Sergio, Mames, Robert N, Timmers, Adrian M, Saban, Daniel, Grant, Maria B
Published in Investigative ophthalmology & visual science (01.01.2005)
Published in Investigative ophthalmology & visual science (01.01.2005)
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Journal Article
AAV-Mediated Intravitreal Gene Therapy Reduces Lysosomal Storage in the Retinal Pigmented Epithelium and Improves Retinal Function in Adult MPS VII Mice
Hennig, Anne K, Ogilvie, Judith Mosinger, Ohlemiller, Kevin K, Timmers, Adrian M, Hauswirth, William W, Sands, Mark S
Published in Molecular therapy (01.07.2004)
Published in Molecular therapy (01.07.2004)
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Journal Article
Structural and Functional Protection of Photoreceptors from MNU-Induced Retinal Degeneration by the X-Linked Inhibitor of Apoptosis
Petrin, Dino, Baker, Adam, Coupland, Stuart G, Liston, Peter, Narang, Monica, Damji, Karim, Leonard, Brian, Chiodo, Vince A, Timmers, Adrian, Hauswirth, William, Korneluk, Robert G, Tsilfidis, Catherine
Published in Investigative ophthalmology & visual science (01.06.2003)
Published in Investigative ophthalmology & visual science (01.06.2003)
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Journal Article
Does recombinant adeno-associated virus-vectored proximal region of mouse rhodopsin promoter support only rod-type specific expression in vivo?
Glushakova, Lyudmyla G, Timmers, Adrian M, Issa, Tawfik M, Cortez, Nenita G, Pang, Jijing, Teusner, Jacqueline T, Hauswirth, William W
Published in Molecular vision (07.04.2006)
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Published in Molecular vision (07.04.2006)
Journal Article
AAV Gene Augmentation of Truncated Complement Factor H Differentially Rescues Ocular Complement Dysregulation in a Mouse Model
Grigsby, Daniel, Klingeborn, Mikael, Kelly, Una, Chew, Lindsey A, Asokan, Aravind, Devlin, Garth, Smith, Sharon, Keyes, Lisa, Timmers, Adrian, Scaria, Abraham, Bowes Rickman, Catherine
Published in Investigative ophthalmology & visual science (20.07.2023)
Published in Investigative ophthalmology & visual science (20.07.2023)
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Journal Article
Toxicity and Efficacy Evaluation of an Adeno-Associated Virus Vector Expressing Codon-Optimized RPGR Delivered by Subretinal Injection in a Canine Model of X-linked Retinitis Pigmentosa
Dufour, Valérie L, Cideciyan, Artur V, Ye, Guo-Jie, Song, Chunjuan, Timmers, Adrian, Habecker, Perry L, Pan, Wei, Weinstein, Nicole M, Swider, Malgorzata, Durham, Amy C, Ying, Gui-Shuang, Robinson, Paulette M, Jacobson, Samuel G, Knop, David R, Chulay, Jeffrey D, Shearman, Mark S, Aguirre, Gustavo D, Beltran, William A
Published in Human gene therapy (01.02.2020)
Published in Human gene therapy (01.02.2020)
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Journal Article
프로그래뉼린 연관 신경변성 질환 또는 장애의 치료를 위한 아데노-연관 바이러스 (AAV) 시스템
TIMMERS ADRIAN, LI JUAN, MANDAPADI SAVITRI, PENNOCK STEVEN, SHEARMAN MARK, FARIVAR TANAZ, NEWMARK JUDITH
Year of Publication 08.02.2023
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Year of Publication 08.02.2023
Patent
연령-관련 황반 변성 및 다른 안구 질환 및 장애의 치료를 위한 아데노-연관 바이러스 (AAV) 벡터
TIMMERS ADRIAN, MURELI RAKSHAA, SHEARMAN MARK, PENNOCK STEVEN, KEYES LISA, NEWMARK JUDITH, SONG CHUNJUAN
Year of Publication 07.02.2023
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Year of Publication 07.02.2023
Patent