CXCR4/IgG-expressing plasma cells are associated with human gastrointestinal tissue inflammation
Buckner, Clarisa M., PhD, Moir, Susan, PhD, Kardava, Lela, PhD, Ho, Jason, PhD, Santich, Brian H., BA, Kim, Leo Jin Young, BA, Funk, Emily K., BA, Nelson, Amy K., BSN, Winckler, Britanny, BA, Chairez, Cheryl L., BSN, Theobald-Whiting, Narda L., BS, Anaya-O’Brien, Sandra, MSN, Alimchandani, Meghna, MD, Quezado, Martha M., MD, Yao, Michael D., MD, Kovacs, Joseph A., MD, Chun, Tae-Wook, PhD, Fauci, Anthony S., MD, Malech, Harry L., MD, De Ravin, Suk See, MD, PhD
Published in Journal of allergy and clinical immunology (01.06.2014)
Published in Journal of allergy and clinical immunology (01.06.2014)
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Hypomorphic Rag mutations can cause destructive midline granulomatous disease
De Ravin, Suk See, Cowen, Edward W., Zarember, Kol A., Whiting-Theobald, Narda L., Kuhns, Douglas B., Sandler, Netanya G., Douek, Daniel C., Pittaluga, Stefania, Poliani, Pietro L., Lee, Yu Nee, Notarangelo, Luigi D., Wang, Lei, Alt, Frederick W., Kang, Elizabeth M., Milner, Joshua D., Niemela, Julie E., Fontana-Penn, Mary, Sinal, Sara H., Malech, Harry L.
Published in Blood (26.08.2010)
Published in Blood (26.08.2010)
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The Late Dividing Population of γ‐Retroviral Vector Transduced Human Mobilized Peripheral Blood Progenitor Cells Contributes Most to Gene‐Marked Cell Engraftment in Nonobese Diabetic/Severe Combined Immunodeficient Mice
Brenner, Sebastian, Ryser, Martin F., Whiting‐Theobald, Narda L., Gentsch, Marcus, Linton, Gilda F., Malech, Harry L.
Published in Stem cells (Dayton, Ohio) (01.07.2007)
Published in Stem cells (Dayton, Ohio) (01.07.2007)
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Lentivector cryptic splicing mediates increase in CD34+ clones expressing truncated HMGA2 in human X-linked severe combined immunodeficiency
De Ravin, Suk See, Liu, Siyuan, Sweeney, Colin L., Brault, Julie, Whiting-Theobald, Narda, Ma, Michelle, Liu, Taylor, Choi, Uimook, Lee, Janet, O’Brien, Sandra Anaya, Quackenbush, Priscilla, Estwick, Tyra, Karra, Anita, Docking, Ethan, Kwatemaa, Nana, Guo, Shuang, Su, Ling, Sun, Zhonghe, Zhou, Sheng, Puck, Jennifer, Cowan, Morton J., Notarangelo, Luigi D., Kang, Elizabeth, Malech, Harry L., Wu, Xiaolin
Published in Nature communications (28.06.2022)
Published in Nature communications (28.06.2022)
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Correction of canine X-linked severe combined immunodeficiency by in vivo retroviral gene therapy
Ravin, Suk See Ting–De, Kennedy, Douglas R., Naumann, Nora, Kennedy, Jeffrey S., Choi, Uimook, Hartnett, Brian J., Linton, Gilda F., Whiting-Theobald, Narda L., Moore, Peter F., Vernau, William, Malech, Harry L., Felsburg, Peter J.
Published in Blood (15.04.2006)
Published in Blood (15.04.2006)
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WHIM syndrome myelokathexis reproduced in the NOD/SCID mouse xenotransplant model engrafted with healthy human stem cells transduced with C-terminus–truncated CXCR4
Kawai, Toshinao, Choi, Uimook, Cardwell, Lanise, DeRavin, Suk See, Naumann, Nora, Whiting-Theobald, Narda L., Linton, Gilda F., Moon, Jaehyun, Murphy, Philip M., Malech, Harry L.
Published in Blood (01.01.2007)
Published in Blood (01.01.2007)
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Gene therapy improves immune function in preadolescents with X-linked severe combined immunodeficiency
Chinen, Javier, Davis, Joie, De Ravin, Suk See, Hay, Beverly N., Hsu, Amy P., Linton, Gilda F., Naumann, Nora, Nomicos, Effie Y.H., Silvin, Christopher, Ulrick, Jean, Whiting-Theobald, Narda L., Malech, Harry L., Puck, Jennifer M.
Published in Blood (01.07.2007)
Published in Blood (01.07.2007)
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CXCR4‐Transgene Expression Significantly Improves Marrow Engraftment of Cultured Hematopoietic Stem Cells
Brenner, Sebastian, Whiting‐Theobald, Narda, Kawai, Toshinao, Linton, Gilda F., Rudikoff, Andrew G., Choi, Uimook, Ryser, Martin F., Murphy, Philip M., Sechler, Joan M.G., Malech, Harry L.
Published in Stem cells (Dayton, Ohio) (01.01.2004)
Published in Stem cells (Dayton, Ohio) (01.01.2004)
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Enhanced function with decreased internalization of carboxy-terminus truncated CXCR4 responsible for WHIM syndrome
Kawai, Toshinao, Choi, Uimook, Whiting-Theobald, Narda L., Linton, Gilda F., Brenner, Sebastian, Sechler, Joan M.G., Murphy, Philip M., Malech, Harry L.
Published in Experimental hematology (01.04.2005)
Published in Experimental hematology (01.04.2005)
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Diprotin A infusion into nonobese diabetic/severe combined immunodeficiency mice markedly enhances engraftment of human mobilized CD34+ peripheral blood cells
Kawai, Toshinao, Choi, Uimook, Liu, Po-Ching, Whiting-Theobald, Narda L, Linton, Gilda F, Malech, Harry L
Published in Stem cells and development (01.06.2007)
Published in Stem cells and development (01.06.2007)
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Prolonged Production of NADPH Oxidase-Corrected Granulocytes after Gene Therapy of Chronic Granulomatous Disease
Malech, H L, Maples, P B, Whiting-Theobald, N, Linton, G F, Sekhsaria, S, Vowells, S J, Li, F, Miller, J A, DeCarlo, E, Holland, S M, Leitman, S F, Carter, C S, Butz, R E, Read, E J, Fleisher, T A, Schneiderman, R D, Van Epps, D E, Spratt, S K, Maack, C A, Rokovich, J A, Cohen, L K, Gallin, J I
Published in Proceedings of the National Academy of Sciences - PNAS (28.10.1997)
Published in Proceedings of the National Academy of Sciences - PNAS (28.10.1997)
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664. WHIM Syndrome Type Myelokathexis In Vivo in the NOD/SCID Mouse Model Following Transplant of Healthy Human Stem Cells Transduced with C-Terminus Truncated CXCR4
Kawai, Toshinao, Choi, Uimook, Cardwell, Lanise, Deravin, Suk See, Naumann, Nora, Whiting-Theobald, Narda L., Linton, Gilda F., Brenner, Sebastian, Murphy, Philip M., Malech, Harry L.
Published in Molecular therapy (01.05.2006)
Published in Molecular therapy (01.05.2006)
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CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease
De Ravin, Suk See, Li, Linhong, Wu, Xiaolin, Choi, Uimook, Allen, Cornell, Koontz, Sherry, Lee, Janet, Theobald-Whiting, Narda, Chu, Jessica, Garofalo, Mary, Sweeney, Colin, Kardava, Lela, Moir, Susan, Viley, Angelia, Natarajan, Pachai, Su, Ling, Kuhns, Douglas, Zarember, Kol A, Peshwa, Madhusudan V, Malech, Harry L
Published in Science translational medicine (11.01.2017)
Published in Science translational medicine (11.01.2017)
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Concentrated RD114-pseudotyped MFGS-gp91phox vector achieves high levels of functional correction of the chronic granulomatous disease oxidase defect in NOD/SCID/β2-microglobulin–/– repopulating mobilized human peripheral blood CD34+ cells
Brenner, Sebastian, Whiting-Theobald, Narda L., Linton, Gilda F., Holmes, Kevin L., Anderson-Cohen, Mindy, Kelly, Patrick F., Vanin, Elio F., Pilon, André M., Bodine, David M., Horwitz, Mitchell E., Malech, Harry L.
Published in Blood (15.10.2003)
Published in Blood (15.10.2003)
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Journal Article
CXCR4‐Transgene Expression Significantly Improves Marrow Engraftment of Cultured Hematopoietic Stem Cells
Brenner, Sebastian, Whiting‐Theobald, Narda, Kawai, Toshinao, Linton, Gilda F., Rudikoff, Andrew G., Choi, Uimook, Ryser, Martin F., Murphy, Philip M., Sechler, Joan M.G., Malech, Harry L.
Published in Stem cells (Dayton, Ohio) (01.12.2004)
Published in Stem cells (Dayton, Ohio) (01.12.2004)
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Journal Article
CXCR4/lgG-expressing plasma cells are associated with human gastrointestinal tissue inflammation
BUCKNER, Clarisa M, MOIR, Susan, THEOBALD-WHITING, Narda L, ANAYA-O'BRIEN, Sandra, ALIMCHANDANI, Meghna, QUEZADO, Martha M, YAO, Michael D, KOVACS, Joseph A, CHUN, Tae-Wook, FAUCI, Anthony S, MALECH, Harry L, DE RAVIN, Suk See, KARDAVA, Lela, HO, Jason, SANTICH, Brian H, LEO JIN YOUNG KIM, FUNK, Emily K, NELSON, Amy K, WINCKLER, Britanny, CHAIREZ, Cheryl L
Published in Journal of allergy and clinical immunology (2014)
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Published in Journal of allergy and clinical immunology (2014)
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Third-generation, self-inactivating gp91(phox) lentivector corrects the oxidase defect in NOD/SCID mouse-repopulating peripheral blood-mobilized CD34+ cells from patients with X-linked chronic granulomatous disease
Roesler, Joachim, Brenner, Sebastian, Bukovsky, Anatoly A, Whiting-Theobald, Narda, Dull, Thomas, Kelly, Michael, Civin, Curt I, Malech, Harry L
Published in Blood (15.12.2002)
Published in Blood (15.12.2002)
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Simian immundeficiency virus lentivector corrects human X-linked chronic granulomatous disease in the NOD/SCID mouse xenograft
Naumann, Nora, De Ravin, Suk See, Choi, Uimook, Moayeri, Morvarid, Whiting-Theobald, Narda, Linton, Gilda F., Ikeda, Yasuhiro, Malech, Harry L.
Published in Gene therapy (30.08.2007)
Published in Gene therapy (30.08.2007)
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Journal Article
WHIM syndrome myelokathexis reproduced in the NOD/SCID mouse xenotransplant model engrafted with healthy human stem cells transduced with C-terminus-truncated CXCR4. Commentary
DALE, David C, KAWAI, Toshinao, MALECH, Harry L, CHOI, Uimook, CARDWELL, Lanise, SUK SEE DERAVIN, NAUMANN, Nora, WHITING-THEOBALD, Narda L, LINTON, Gilda F, MOON, Jaehyun, MURPHY, Philip M
Published in Blood (2007)
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Published in Blood (2007)
Journal Article
Polyclonal Long-Term MFGS-gp91phox Marking in Rhesus Macaques after Nonmyeloablative Transplantation with Transduced Autologous Peripheral Blood Progenitor Cells
Brenner, Sebastian, Ryser, Martin F, Choi, Uimook, Whiting-Theobald, Narda, Kuhlisch, Eberhard, Linton, Gilda, Kang, Elizabeth, Lehmann, Romy, Rosen-Wolff, Angela, Rudikoff, Andrew G, Farese, Ann M, Macvittie, Thomas J, Roesler, Joachim, Horwitz, Mitchell E, Malech, Harry L
Published in Molecular therapy (01.08.2006)
Published in Molecular therapy (01.08.2006)
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