Safety update: risdiplam clinical trial programme for spinal muscular atrophy (SMA)
Laurent, Servais, Giovanni, Baranello, Claudia, Chiriboga, Basil, Darras, Marianne, Gerber, Ksenija, Gorni, Birgit, Jaber, Tammy, McIver, Renata, Scalco, Eugenio, Mercuri
Published in Journal of neurology, neurosurgery and psychiatry (28.11.2023)
Published in Journal of neurology, neurosurgery and psychiatry (28.11.2023)
Get full text
Journal Article
Efficacy and safety of fluticasone propionate/formoterol fumarate in pediatric asthma patients: a randomized controlled trial
Płoszczuk, Anna, Bosheva, Miroslava, Spooner, Kay, McIver, Tammy, Dissanayake, Sanjeeva
Published in Therapeutic advances in respiratory disease (01.05.2018)
Published in Therapeutic advances in respiratory disease (01.05.2018)
Get full text
Journal Article
Racial and ethnic diversity in global neuroscience clinical trials
Rutten-Jacobs, Loes, McIver, Tammy, Reyes, Adriana, Pereira, Marta, Rosenthal, Rachel, Parusel, Christine T, Wagner, Kathryn R, Doody, Rachelle
Published in Contemporary clinical trials communications (01.02.2024)
Published in Contemporary clinical trials communications (01.02.2024)
Get full text
Journal Article
A 12-week open-label, randomized, controlled trial and 24-week extension to assess the efficacy and safety of fluticasone propionate/formoterol in children with asthma
Emeryk, Andrzej, Klink, Rabih, McIver, Tammy, Dalvi, Prashant
Published in Therapeutic advances in respiratory disease (01.08.2016)
Published in Therapeutic advances in respiratory disease (01.08.2016)
Get full text
Journal Article
Two-year efficacy and safety of risdiplam in patients with type 2 or non-ambulant type 3 spinal muscular atrophy (SMA)
Oskoui, Maryam, Day, John W., Deconinck, Nicolas, Mazzone, Elena S., Nascimento, Andres, Saito, Kayoko, Vuillerot, Carole, Baranello, Giovanni, Goemans, Nathalie, Kirschner, Janbernd, Kostera-Pruszczyk, Anna, Servais, Laurent, Papp, Gergely, Gorni, Ksenija, Kletzl, Heidemarie, Martin, Carmen, McIver, Tammy, Scalco, Renata S., Staunton, Hannah, Yeung, Wai Yin, Fontoura, Paulo, Mercuri, Eugenio
Published in Journal of neurology (01.05.2023)
Published in Journal of neurology (01.05.2023)
Get full text
Journal Article
Risdiplam in types 2 and 3 spinal muscular atrophy: A randomised, placebo‐controlled, dose‐finding trial followed by 24 months of treatment
Mercuri, Eugenio, Baranello, Giovanni, Boespflug‐Tanguy, Odile, De Waele, Liesbeth, Goemans, Nathalie, Kirschner, Janbernd, Masson, Riccardo, Mazzone, Elena S., Pechmann, Astrid, Pera, Maria Carmela, Vuillerot, Carole, Bader‐Weder, Silvia, Gerber, Marianne, Gorni, Ksenija, Hoffart, Janine, Kletzl, Heidemarie, Martin, Carmen, McIver, Tammy, Scalco, Renata S., Yeung, Wai Yin, Servais, Laurent
Published in European journal of neurology (01.07.2023)
Published in European journal of neurology (01.07.2023)
Get full text
Journal Article
Web Resource
131 Pooled safety data from the risdiplam clinical trial development programme
Servais, Laurent, Baranello, Giovanni, Chiriboga, Claudia, Darras, Basil, Bader-Weder, Silvia, Gorni, Ksenija, Jaber, Birgit, McIver, Tammy, Scalco, Renata
Published in Journal of neurology, neurosurgery and psychiatry (01.06.2022)
Published in Journal of neurology, neurosurgery and psychiatry (01.06.2022)
Get full text
Journal Article
182 Pooled safety data from the risdiplam clinical development programme
Baranello, Giovanni, Servais, Laurent, Chiriboga, Claudia, Darras, Basil, Bader-Weder, Silvia, Gorni, Ksenija, Jaber, Birgit, McIver, Tammy, Scalco, Renata, Mercuri, Eugenio
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2022)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2022)
Get full text
Journal Article
187 SUNFISH Part 2: 24-month efficacy of risdiplam compared with external control comparators
Servais, Laurent, Day, John W, Mazzone, Elena S, Oskoui, Maryam, Baranello, Giovanni, Gerber, Marianne, Martin, Carmen, McIver, Tammy, Yeung, Wai Yin, Mercuri, Eugenio
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2022)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2022)
Get full text
Journal Article
Risdiplam in types 2 and 3 spinal muscular atrophy: A randomised, placebo‐controlled, dose‐finding trial followed by 24months of treatment
Mercuri, Eugenio, Baranello, Giovanni, Odile Boespflug‐Tanguy, De Waele, Liesbeth, Goemans, Nathalie, Kirschner, Janbernd, Masson, Riccardo, Mazzone, Elena S, Pechmann, Astrid, Pera, Maria Carmela, Vuillerot, Carole, Silvia Bader‐Weder, Gerber, Marianne, Gorni, Ksenija, Hoffart, Janine, Kletzl, Heidemarie, Martin, Carmen, McIver, Tammy, Scalco, Renata S, Wai Yin Yeung, Servais, Laurent
Published in European journal of neurology (01.07.2023)
Published in European journal of neurology (01.07.2023)
Get full text
Journal Article
Correction to: Two‑year efficacy and safety of risdiplam in patients with type 2 or non‑ambulant type 3 spinal muscular atrophy (SMA)
Oskoui, Maryam, Day, John W., Deconinck, Nicolas, Mazzone, Elena S., Nascimento, Andres, Saito, Kayoko, Vuillerot, Carole, Baranello, Giovanni, Goemans, Nathalie, Kirschner, Janbernd, Kostera-Pruszczyk, Anna, Servais, Laurent, Papp, Gergely, Gorni, Ksenija, Kletzl, Heidemarie, Martin, Carmen, McIver, Tammy, Scalco, Renata S., Staunton, Hannah, Yeung, Wai Yin, Fontoura, Paulo, Mercuri, Eugenio
Published in Journal of neurology (01.05.2023)
Published in Journal of neurology (01.05.2023)
Get full text
Journal Article
Durable remissions with obinutuzumab-based chemoimmunotherapy: long-term follow-up of the phase 1b GALTON trial in CLL
Brown, Jennifer R., O'Brien, Susan, Kingsley, C. Daniel, Eradat, Herbert, Pagel, John M., Hirata, Jamie, McIver, Tammy, Morariu-Zamfir, Rodica, Kipps, Thomas J.
Published in Blood (28.02.2019)
Published in Blood (28.02.2019)
Get full text
Journal Article
An evaluation of comparative treatment effects with high and low dose fluticasone propionate/formoterol combination in asthma
Dissanayake, Sanjeeva, Jain, Meena, Grothe, Birgit, McIver, Tammy, Papi, Alberto
Published in Pulmonary pharmacology & therapeutics (01.12.2015)
Published in Pulmonary pharmacology & therapeutics (01.12.2015)
Get full text
Journal Article
Long-Term Fluticasone Propionate/Formoterol Fumarate Combination Therapy Is Associated with a Low Incidence of Severe Asthma Exacerbations
Papi, Alberto, Mansur, Adel H, Pertseva, Tetyana, Kaiser, Kirsten, McIver, Tammy, Grothe, Birgit, Dissanayake, Sanjeeva
Published in Journal of aerosol medicine (01.08.2016)
Published in Journal of aerosol medicine (01.08.2016)
Get full text
Journal Article
Facioscapulohumeral Muscular Dystrophy European Patient Survey: Assessing Patient Reported Disease Burden and Preferences in Clinical Trial Participation
McNiff, Megan M., Hawkins, Sheila, Haase, Bine, Bullivant, Joanne, McIver, Tammy, Mitelman, Olga, Emery, Nicholas, Tasca, Giorgio, Voermans, Nicol, Diaz-Manera, Jordi
Published in Journal of neuromuscular diseases (01.01.2024)
Published in Journal of neuromuscular diseases (01.01.2024)
Get full text
Journal Article
Efficacy and safety profile of fluticasone/formoterol combination therapy compared to its individual components administered concurrently in asthma: a randomised controlled trial
Bodzenta-Lukaszyk, Anna, van Noord, Jan, Schröder-Babo, Winfried, McAulay, Kirsten, McIver, Tammy
Published in Current medical research and opinion (01.05.2013)
Published in Current medical research and opinion (01.05.2013)
Get more information
Journal Article
The EFFECT trial: evaluating exacerbations, biomarkers, and safety outcomes with two dose levels of fluticasone propionate/formoterol in COPD
Papi, Alberto, Jones, Paul W, Dalvi, Prashant S, McAulay, Kirsten, McIver, Tammy, Dissanayake, Sanjeeva
Published in International journal of chronic obstructive pulmonary disease (01.01.2015)
Published in International journal of chronic obstructive pulmonary disease (01.01.2015)
Get full text
Journal Article