Sustained Factor VIII Activity Following Single Dose of Non-Viral Integrating Gene Therapy
Truong, Brian, Nguyen, Giang N., Hajj, Khal, Lucas, Joseph, Schwerk, Johannes, Yen, James, Briseno, Kevin, Burrascano, Michelle, Smith, Daniel, Tamayo, Johnnatan, Lopez-Espinoza, Fernando, Bennett, Michael, Madison, Blair, Sabatino, Denise E., Rychak, Joshua
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
Get full text
Journal Article
Effective Gene Therapy for Hemophilia a: Novel Re-Dosable Non-Viral Formulation That Provides Stable, and Durable FVIII Expression with Improved Tolerability
Truong, Brian, Hajj, Khal, Schwerk, Johannes, Zhang, Dongyang, Tamayo, Johnnatan, Guzelsoy, Gizem, Kubicki, Joseph, Davis, Alicia, Huang, Lijun, Vemuri, Gopi, Johnson, Kevin, Smith, Dan, Bendor, Jordan, Li, Mu, Goolyam, Manjunath, Abernathy, Daniel, Nyshadham, Pranav, Espinoza, Fernando, Burrascano, Michelle, Yen, James, Briseno, Kevin, Tong, Min, Beck, Jen, Lucas, Joseph, Battiprolu, Pavan, Bennett, Michael, Madison, Blair, Warner, Brent, Ostertag, Eric, Rychak, Joshua
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
Get full text
Journal Article