Treatment of canine leukocyte adhesion deficiency by foamy virus vectors expressing CD18 from a PGK promoter
BAUER, T. R, OLSON, E. M, HUO, Y, TUSCHONG, L. M, ALLEN, J. M, LI, Y, BURKHOLDER, T. H, RUSSELL, D. W
Published in Gene therapy (01.06.2011)
Published in Gene therapy (01.06.2011)
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Potential genotoxicity from integration sites in CLAD dogs treated successfully with gammaretroviral vector-mediated gene therapy
HAI, M, ADLER, R. L, BAUER, T. R, TUSCHONG, L. M, GU, Y.-C, WU, X, HICKSTEIN, D. D
Published in Gene therapy (01.07.2008)
Published in Gene therapy (01.07.2008)
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Conversion of the severe to the moderate disease phenotype with donor leukocyte microchimerism in canine leukocyte adhesion deficiency
GU, Y.-C, BAUER, T. R, SOKOLIC, R. A, HAI, M, TUSCHONG, L. M, BURKHOLDER, T, BACHER, J, STAROST, M. F, HICKSTEIN, D. D
Published in Bone marrow transplantation (Basingstoke) (01.03.2006)
Published in Bone marrow transplantation (Basingstoke) (01.03.2006)
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Canine leukocyte adhesion deficiency colony for investigation of novel hematopoietic therapies
Creevy, Kate E, Bauer, Thomas R, Tuschong, Laura M, Embree, Lisa J, Colenda, Lyn, Cogan, Kevin, Starost, Matthew F, Haskins, Mark E, Hickstein, Dennis D
Published in Veterinary immunology and immunopathology (15.07.2003)
Published in Veterinary immunology and immunopathology (15.07.2003)
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Flow cytometry analysis of adenosine deaminase (ADA) expression: a simple and reliable tool for the assessment of ADA-deficient patients before and after gene therapy
Otsu, Makoto, Hershfield, Michael S, Tuschong, Laura M, Muul, Linda M, Onodera, Masafumi, Ariga, Tadashi, Sakiyama, Yukio, Candotti, Fabio
Published in Human gene therapy (10.02.2002)
Published in Human gene therapy (10.02.2002)
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Gene therapy for canine leukocyte adhesion deficiency with lentiviral vectors using the murine stem cell virus and human phosphoglycerate kinase promoters
Hunter, Michael J, Zhao, Huifen, Tuschong, Laura M, Bauer, Jr, Thomas R, Burkholder, Tanya H, Persons, Derek A, Hickstein, Dennis D
Published in Human gene therapy (01.06.2011)
Published in Human gene therapy (01.06.2011)
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Persistence and expression of the adenosine deaminase gene for 12 years and immune reaction to gene transfer components: long-term results of the first clinical gene therapy trial
Muul, Linda Mesler, Tuschong, Laura M., Soenen, Sherry Lau, Jagadeesh, G. Jayashree, Ramsey, W. Jay, Long, Zhifeng, Carter, Charles S., Garabedian, Elizabeth K., Alleyne, Melinna, Brown, Margaret, Bernstein, Wendy, Schurman, Shepherd H., Fleisher, Thomas A., Leitman, Susan F., Dunbar, Cynthia E., Blaese, R. Michael, Candotti, Fabio
Published in Blood (01.04.2003)
Published in Blood (01.04.2003)
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Nonmyeloablative hematopoietic stem cell transplantation corrects the disease phenotype in the canine model of leukocyte adhesion deficiency
Bauer, Thomas R., Gu, Yu-chen, Tuschong, Laura M., Burkholder, Tanya, Bacher, John D., Starost, Matthew F., Donahue, Robert E., Sokolic, Robert A., Hickstein, Dennis D.
Published in Experimental hematology (01.06.2005)
Published in Experimental hematology (01.06.2005)
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Journal Article
Very low levels of donor CD18+ neutrophils following allogeneic hematopoietic stem cell transplantation reverse the disease phenotype in canine leukocyte adhesion deficiency
Bauer, Thomas R., Creevy, Kate E., Gu, Yu-chen, Tuschong, Laura M., Donahue, Robert E., Metzger, Mark E., Embree, Lisa J., Burkholder, Tanya, Bacher, John D., Romines, Chris, Thomas, Marvin L., Colenda, Lyn, Hickstein, Dennis D.
Published in Blood (01.05.2004)
Published in Blood (01.05.2004)
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Journal Article
Leukocyte adhesion deficiency in children and irish setter dogs
BAUER, Thomas R, GU, Yu-Chen, CREEVY, Kate E, TUSCHONG, Laura M, EMBREE, Lisa, HOLLAND, Steven M, SOKOLIC, Robert A, HICKSTEIN, Dennis D
Published in Pediatric research (01.03.2004)
Published in Pediatric research (01.03.2004)
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Nonmyeloablative Conditioning with Busulfan before Matched Littermate Bone Marrow Transplantation Results in Reversal of the Disease Phenotype in Canine Leukocyte Adhesion Deficiency
Sokolic, Robert A., Bauer, Thomas R., Gu, Yu-Chen, Hai, Mehreen, Tuschong, Laura M., Burkholder, Tanya, Colenda, Lyn, Bacher, John, Starost, Matthew F., Hickstein, Dennis D.
Published in Biology of blood and marrow transplantation (01.10.2005)
Published in Biology of blood and marrow transplantation (01.10.2005)
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