Search Results - "TATSUYOSHI YAMAMOTO" :: K.UTB vyhledávací portál | TBU Library Retrieval Portal

Enzyme Replacement Therapy with Pabinafusp Alfa for Neuronopathic Mucopolysaccharidosis II: An Integrated Analysis of Preclinical and Clinical Data

Enzyme Replacement Therapy with Pabinafusp Alfa for Neuronopathic Mucopolysaccharidosis II: An Integrated Analysis of Preclinical and Clinical Data

by Giugliani, Roberto, Martins, Ana Maria, Okuyama, Torayuki, Eto, Yoshikatsu, Sakai, Norio, Nakamura, Kimitoshi, Morimoto, Hideto, Minami, Kohtaro, Yamamoto, Tatsuyoshi, Yamaoka, Mariko, Ikeda, Toshiaki, So, Sairei, Tanizawa, Kazunori, Sonoda, Hiroyuki, Schmidt, Mathias, Sato, Yuji
Published in International journal of molecular sciences (10.10.2021)

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Journal Article

Analysis of caregiver perspectives on patients with mucopolysaccharidosis II treated with pabinafusp alfa: results of qualitative interviews in Japan

Analysis of caregiver perspectives on patients with mucopolysaccharidosis II treated with pabinafusp alfa: results of qualitative interviews in Japan

by Nakamura, Kimitoshi, Sakai, Norio, Hossain, Mohammad Arif, Eisengart, Julie B, Yamamoto, Tatsuyoshi, Tanizawa, Kazunori, So, Sairei, Schmidt, Mathias, Sato, Yuji
Published in Orphanet journal of rare diseases (07.03.2024)

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Treatment of Neuronopathic Mucopolysaccharidoses with Blood–Brain Barrier-Crossing Enzymes: Clinical Application of Receptor-Mediated Transcytosis

Treatment of Neuronopathic Mucopolysaccharidoses with Blood–Brain Barrier-Crossing Enzymes: Clinical Application of Receptor-Mediated Transcytosis

by Sonoda, Hiroyuki, Takahashi, Kenichi, Minami, Kohtaro, Hirato, Toru, Yamamoto, Tatsuyoshi, So, Sairei, Tanizawa, Kazunori, Schmidt, Mathias, Sato, Yuji
Published in Pharmaceutics (11.06.2022)

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Efficacy and safety of GH treatment in Japanese children with short stature due to SHOX deficiency: a randomized phase 3 study

Efficacy and safety of GH treatment in Japanese children with short stature due to SHOX deficiency: a randomized phase 3 study

by Ogata, Tsutomu, Fukami, Maki, Tanizawa, Kazunori, Yamamoto, Tatsuyoshi, Sato, Yuji, Hirai, Hideaki, Takasao, Naoko, Ibaraki, Ryo, Noda, Marin
Published in Clinical Pediatric Endocrinology (2024)

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Divergent developmental trajectories in two siblings with neuropathic mucopolysaccharidosis type II (Hunter syndrome) receiving conventional and novel enzyme replacement therapies: A case report

Divergent developmental trajectories in two siblings with neuropathic mucopolysaccharidosis type II (Hunter syndrome) receiving conventional and novel enzyme replacement therapies: A case report

by Tomita, Kazuyoshi, Okamoto, Shungo, Seto, Toshiyuki, Hamazaki, Takashi, So, Sairei, Yamamoto, Tatsuyoshi, Tanizawa, Kazunori, Sonoda, Hiroyuki, Sato, Yuji
Published in JIMD reports (01.11.2021)

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Journal Article

Efficacy and safety of GH treatment in Japanese children with short stature due to SHOX deficiency : a randomized phase 3 study

Efficacy and safety of GH treatment in Japanese children with short stature due to SHOX deficiency : a randomized phase 3 study

by Tsutomu Ogata, Maki Fukami, Kazunori Tanizawa, Tatsuyoshi Yamamoto, Yuji Sato, Hideaki Hirai, Naoko Takasao, Ryo Ibaraki, Marin Noda
Published in Clinical Pediatric Endocrinology (01.04.2024)

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Journal Article

A comprehensive expression analysis of mucins in appendiceal carcinoma in a multicenter study: MUC3 is a novel prognostic factor

A comprehensive expression analysis of mucins in appendiceal carcinoma in a multicenter study: MUC3 is a novel prognostic factor

by Shibahara, Hiroaki, Higashi, Michiyo, Yokoyama, Seiya, Rousseau, Karine, Kitazono, Iwao, Osako, Masahiko, Shirahama, Hiroshi, Tashiro, Yukie, Kurumiya, Yasuhiro, Narita, Michihiko, Kuze, Shingo, Hasagawa, Hiroshi, Kato, Takehito, Kubota, Hitoshi, Suzuki, Hideaki, Arai, Toshiyuki, Sakai, Yu, Yuasa, Norihiro, Fujino, Masahiko, Kondo, Shinji, Okamoto, Yoshichika, Yamamoto, Tatsuyoshi, Hiromatsu, Takashi, Sasaki, Eiji, Shirai, Kazuhisa, Kawai, Satoru, Hattori, Koutarou, Tsuji, Hideki, Okochi, Osamu, Sakamoto, Masaki, Kondo, Akinobu, Konishi, Naomi, Batra, Surinder K, Yonezawa, Suguru
Published in PloS one (31.12.2014)

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Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial

Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial

by Okuyama, Torayuki, Eto, Yoshikatsu, Sakai, Norio, Minami, Kohtaro, Yamamoto, Tatsuyoshi, Sonoda, Hiroyuki, Yamaoka, Mariko, Tachibana, Katsuhiko, Hirato, Tohru, Sato, Yuji
Published in Molecular therapy (06.02.2019)

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Journal Article

A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-II

A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-II

by Okuyama, Torayuki, Eto, Yoshikatsu, Sakai, Norio, Nakamura, Kimitoshi, Yamamoto, Tatsuyoshi, Yamaoka, Mariko, Ikeda, Toshiaki, So, Sairei, Tanizawa, Kazunori, Sonoda, Hiroyuki, Sato, Yuji
Published in Molecular therapy (03.02.2021)

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A global phase III study of pabinafusp alfa (JR-141) for neuronopathic mucopolysaccharidosis type II: Updated study design

A global phase III study of pabinafusp alfa (JR-141) for neuronopathic mucopolysaccharidosis type II: Updated study design

by Ikeda, Toshiaki, Harmatz, Paul, So, Sairei, Yamamoto, Tatsuyoshi, Schmidt, Mathias, Tanizawa, Kazunori, Sato, Yuji
Published in Molecular genetics and metabolism (01.02.2024)

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Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II: A phase 2 trial in Brazil

Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II: A phase 2 trial in Brazil

by Giugliani, Roberto, Martins, Ana Maria, So, Sairei, Yamamoto, Tatsuyoshi, Yamaoka, Mariko, Ikeda, Toshiaki, Tanizawa, Kazunori, Sonoda, Hiroyuki, Schmidt, Mathias, Sato, Yuji
Published in Molecular therapy (07.07.2021)

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Journal Article

Real-world data of enzyme replacement therapy with pabinafusp alfa for neuronopathic MPS-II: Updated clinical data from Japan

Real-world data of enzyme replacement therapy with pabinafusp alfa for neuronopathic MPS-II: Updated clinical data from Japan

by Eto, Yoshikatsu, Nakamura, Kimitoshi, Sakai, Norio, Tanizawa, Kazunori, So, Sairei, Yamamoto, Tatsuyoshi, Ikeda, Toshiaki, Moriuchi, Hiroaki, Sonoda, Hiroyuki, Sato, Yuji
Published in Molecular genetics and metabolism (01.02.2023)

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Journal Article

Integrated long-term efficacy and safety data on enzyme replacement therapy with pabinafusp alfa for neuronopathic mucopolysaccharidosis type II (MPS II): Updated clinical data from Japan and Brazil

Integrated long-term efficacy and safety data on enzyme replacement therapy with pabinafusp alfa for neuronopathic mucopolysaccharidosis type II (MPS II): Updated clinical data from Japan and Brazil

by Eto, Yoshikatsu, Giugliani, Roberto, Nakamura, Kimitoshi, Sakai, Norio, Martins, Ana Maria, Tanizawa, Kazunori, So, Sairei, Yamamoto, Tatsuyoshi, Cunegundes, Ricardo, Ikeda, Toshiaki, Moriuchi, Hiroaki, Schmidt, Mathias, Sato, Yuji
Published in Molecular genetics and metabolism (01.02.2024)

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Pharmacokinetics and pharmacodynamics of JR-051, a biosimilar of agalsidase beta, in healthy adults and patients with Fabry disease: Phase I and II/III clinical studies

Pharmacokinetics and pharmacodynamics of JR-051, a biosimilar of agalsidase beta, in healthy adults and patients with Fabry disease: Phase I and II/III clinical studies

by Nakamura, Kimitoshi, Kawashima, Satoshi, Tozawa, Hirotaka, Yamaoka, Mariko, Yamamoto, Tatsuyoshi, Tanaka, Noboru, Yamamoto, Ryuji, Okuyama, Torayuki, Eto, Yoshikatsu
Published in Molecular genetics and metabolism (01.07.2020)

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Journal Article

Novel blood-brain barrier delivery system to treat CNS in MPS II: First clinical trial of anti-transferrin receptor antibody fused enzyme therapy

Novel blood-brain barrier delivery system to treat CNS in MPS II: First clinical trial of anti-transferrin receptor antibody fused enzyme therapy

by Okuyama, Torayuki, Sakai, Norio, Yamamoto, Tatsuyoshi, Yamaoka, Mariko, Tomio, Teiji
Published in Molecular genetics and metabolism (01.02.2018)

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Journal Article

Efficacy and safety of JR-051, a biosimilar of agalsidase beta, in patients with Fabry disease; results of a multicenter, open-label phase 3 study in Japan

Efficacy and safety of JR-051, a biosimilar of agalsidase beta, in patients with Fabry disease; results of a multicenter, open-label phase 3 study in Japan

by Kobayashi, Minako, Yamamoto, Tatsuyoshi, Yamaoka, Mariko, Tomio, Teiji
Published in Molecular genetics and metabolism (01.02.2018)

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Journal Article

Novel Development Rescuing Factors (DRFs) Secreted by the Developing Dictyostelium Cells, That are Involved in the Restoration of a Mutant Lacking MAP-kinase ERK2

Novel Development Rescuing Factors (DRFs) Secreted by the Developing Dictyostelium Cells, That are Involved in the Restoration of a Mutant Lacking MAP-kinase ERK2

by Masatsune Tsujioka;Tatsuyoshi Yamamoto;Christopher R. Thompson;Robert R. Kay;Mineko Maeda
Published in Zoological Science (01.08.2004)

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Journal Article

Long-term neurodevelopmental changes in subjects with MPS II following long-term treatment with pabinafusp alfa: An integrated analysis from pre- and post-approval clinical trials in Brazil and Japan

Long-term neurodevelopmental changes in subjects with MPS II following long-term treatment with pabinafusp alfa: An integrated analysis from pre- and post-approval clinical trials in Brazil and Japan

by Giugliani, Roberto, Eto, Yoshikatsu, Nakamura, Kimitoshi, Sakai, Norio, Martins, Ana Maria, Cunegundes, Ricardo, So, Sairei, Tanizawa, Kazunori, Yamamoto, Tatsuyoshi, Ikeda, Toshiaki, Moriuchi, Hiroaki, Sonoda, Hiroyuki, Schmidt, Mathias, Sato, Yuji
Published in Molecular genetics and metabolism (01.02.2023)

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Journal Article

Pharmacokinetics and pharmacodynamics of once-weekly administration of JR-142, a long-acting albumin-fused human growth hormone: A rondemized, placebo-controlled phase 1 study

Pharmacokinetics and pharmacodynamics of once-weekly administration of JR-142, a long-acting albumin-fused human growth hormone: A rondemized, placebo-controlled phase 1 study

by Owada, Yasuko, Okazaki, Mika, Ikeda, Toshiaki, Yamamoto, Ryuji, Minami, Kohtaro, Takahashi, Kenichi, Hirato, Tohru, Mita, Yoko, Yamamoto, Tatsuyoshi, Tanizawa, Kazunori, Sonoda, Hiroyuki, Sato, Yuji
Published in Growth hormone & IGF research (01.12.2022)

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Journal Article

Therapy for mucopolysaccharidosis type II with an intravenous blood-brain barrier-crossing enzyme (JR-141): 26-week results from a phase 3 study in Japan suggesting significant efficacy against central nervous system and systemic symptoms

Therapy for mucopolysaccharidosis type II with an intravenous blood-brain barrier-crossing enzyme (JR-141): 26-week results from a phase 3 study in Japan suggesting significant efficacy against central nervous system and systemic symptoms

by Okuyama, Torayuki, Eto, Yoshikatsu, Nakamura, Kimitoshi, Sakai, Norio, Sato, Yuji, Tanizawa, Kazunori, Yamamoto, Tatsuyoshi, So, Sairei, Yamaoka, Mariko, Kobayashi, Minako
Published in Molecular genetics and metabolism (01.02.2020)

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