Ruxolitinib for Glucocorticoid-Refractory Acute Graft-versus-Host Disease
Zeiser, Robert, von Bubnoff, Nikolas, Butler, Jason, Mohty, Mohamad, Niederwieser, Dietger, Or, Reuven, Szer, Jeff, Wagner, Eva M, Zuckerman, Tsila, Mahuzier, Bruyère, Xu, Judith, Wilke, Celine, Gandhi, Kunal K, Socié, Gérard
Published in The New England journal of medicine (07.05.2020)
Published in The New England journal of medicine (07.05.2020)
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Journal Article
Pegcetacoplan versus Eculizumab in Paroxysmal Nocturnal Hemoglobinuria
Hillmen, Peter, Szer, Jeff, Weitz, Ilene, Röth, Alexander, Höchsmann, Britta, Panse, Jens, Usuki, Kensuke, Griffin, Morag, Kiladjian, Jean-Jacques, de Castro, Carlos, Nishimori, Hisakazu, Tan, Lisa, Hamdani, Mohamed, Deschatelets, Pascal, Francois, Cedric, Grossi, Federico, Ajayi, Temitayo, Risitano, Antonio, de la Tour, Régis Peffault
Published in The New England journal of medicine (18.03.2021)
Published in The New England journal of medicine (18.03.2021)
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Journal Article
How we manage Gaucher Disease in the era of choices
Revel‐Vilk, Shoshana, Szer, Jeff, Mehta, Atul, Zimran, Ari
Published in British journal of haematology (01.08.2018)
Published in British journal of haematology (01.08.2018)
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Journal Article
One and a half million hematopoietic stem cell transplants: continuous and differential improvement in worldwide access with the use of non-identical family donors
Niederwieser, Dietger, Baldomero, Helen, Bazuaye, Nosa, Bupp, Caitrin, Chaudhri, Naeem, Corbacioglu, Selim, Elhaddad, Alaa, Frutos, Cristóbal, Galeano, Sebastian, Hamad, Nada, Hamidieh, Amir Ali, Hashmi, Shahrukh, Ho, Aloysius, Horowitz, Mary M, Iida, Minako, Jaimovich, Gregorio, Karduss, Amado, Kodera, Yoshihisa, Kröger, Nicolaus, Péffault de Latour, Regis, Lee, Jong Wook, Martínez-Rolón, Juliana, Pasquini, Marcelo C, Passweg, Jakob, Paulson, Kristjan, Seber, Adriana, Snowden, John A, Srivastava, Alok, Szer, Jeff, Weisdorf, Daniel, Worel, Nina, Koh, Mickey B C, Aljurf, Mahmoud, Greinix, Hildegard, Atsuta, Yoshiko, Saber, Wael
Published in Haematologica (Roma) (01.05.2022)
Published in Haematologica (Roma) (01.05.2022)
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Journal Article
Eculizumab in Pregnant Patients with Paroxysmal Nocturnal Hemoglobinuria
Kelly, Richard J, Höchsmann, Britta, Szer, Jeff, Kulasekararaj, Austin, de Guibert, Sophie, Röth, Alexander, Weitz, Ilene C, Armstrong, Elina, Risitano, Antonio M, Patriquin, Christopher J, Terriou, Louis, Muus, Petra, Hill, Anita, Turner, Michelle P, Schrezenmeier, Hubert, Peffault de Latour, Regis
Published in The New England journal of medicine (10.09.2015)
Published in The New England journal of medicine (10.09.2015)
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Journal Article
Worldwide Network for Blood & Marrow Transplantation (WBMT) special article, challenges facing emerging alternate donor registries
Aljurf, Mahmoud, Weisdorf, Daniel, Alfraih, Feras, Szer, Jeff, Müller, Carlheinz, Confer, Dennis, Hashmi, Shahrukh, Kröger, Nicolaus, Shaw, Bronwen E., Greinix, Hildegard, Kharfan-Dabaja, Mohamed A., Foeken, Lydia, Seber, Adriana, Ahmed, Syed, El-Jawahri, Areej, Al-Awwami, Moheeb, Atsuta, Yoshiko, Pasquini, Marcelo, Hanbali, Amr, Alzahrani, Hazzaa, Okamoto, Shinichiro, Gluckman, Eliane, Mohty, Mohamad, Kodera, Yoshihisa, Horowitz, Mary, Niederwieser, Dietger, El Fakih, Riad
Published in Bone marrow transplantation (Basingstoke) (01.08.2019)
Published in Bone marrow transplantation (Basingstoke) (01.08.2019)
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Journal Article
High-Dose Ambroxol Therapy in Type 1 Gaucher Disease Focusing on Patients with Poor Response to Enzyme Replacement Therapy or Substrate Reduction Therapy
Istaiti, Majdolen, Frydman, Dafna, Dinur, Tama, Szer, Jeff, Revel-Vilk, Shoshana, Zimran, Ari
Published in International journal of molecular sciences (01.04.2023)
Published in International journal of molecular sciences (01.04.2023)
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Journal Article
One million haemopoietic stem-cell transplants: a retrospective observational study
Gratwohl, Alois, Pasquini, Marcelo C, Aljurf, Mahmoud, Atsuta, Yoshiko, Baldomero, Helen, Foeken, Lydia, Gratwohl, Michael, Bouzas, Luis Fernando, Confer, Dennis, Frauendorfer, Karl, Gluckman, Eliane, Greinix, Hildegard, Horowitz, Mary, Iida, Minako, Lipton, Jeff, Madrigal, Alejandro, Mohty, Mohamad, Noel, Luc, Novitzky, Nicolas, Nunez, José, Oudshoorn, Machteld, Passweg, Jakob, van Rood, Jon, Szer, Jeff, Blume, Karl, Appelbaum, Frederic R, Kodera, Yoshihisa, Niederwieser, Dietger
Published in The Lancet. Haematology (01.03.2015)
Published in The Lancet. Haematology (01.03.2015)
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Journal Article
All-trans-retinoic acid, idarubicin, and IV arsenic trioxide as initial therapy in acute promyelocytic leukemia (APML4)
Iland, Harry J., Bradstock, Ken, Supple, Shane G., Catalano, Alberto, Collins, Marnie, Hertzberg, Mark, Browett, Peter, Grigg, Andrew, Firkin, Frank, Hugman, Amanda, Reynolds, John, Di Iulio, Juliana, Tiley, Campbell, Taylor, Kerry, Filshie, Robin, Seldon, Michael, Taper, John, Szer, Jeff, Moore, John, Bashford, John, Seymour, John F.
Published in Blood (23.08.2012)
Published in Blood (23.08.2012)
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Journal Article
Treatable lysosomal storage diseases in the advent of disease‐specific therapy
Peters, Heidi, Ellaway, Carolyn, Nicholls, Kathleen, Reardon, Katrina, Szer, Jeff
Published in Internal medicine journal (01.11.2020)
Published in Internal medicine journal (01.11.2020)
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Journal Article
The definition of neuronopathic Gaucher disease
Schiffmann, Raphael, Sevigny, Jeff, Rolfs, Arndt, Davies, Elin Haf, Goker‐Alpan, Ozlem, Abdelwahab, Magy, Vellodi, Ashok, Mengel, Eugen, Lukina, Elena, Yoo, Han‐Wook, Collin‐Histed, Tanya, Narita, Aya, Dinur, Tama, Revel‐Vilk, Shoshana, Arkadir, David, Szer, Jeff, Wajnrajch, Michael, Ramaswami, Uma, Sidransky, Ellen, Donald, Aimee, Zimran, Ari
Published in Journal of inherited metabolic disease (01.09.2020)
Published in Journal of inherited metabolic disease (01.09.2020)
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Journal Article
Neurocognitive dysfunction in hematopoietic cell transplant recipients: expert review from the late effects and Quality of Life Working Committee of the CIBMTR and complications and Quality of Life Working Party of the EBMT
Buchbinder, David, Kelly, Debra Lynch, Duarte, Rafael F., Auletta, Jeffery J., Bhatt, Neel, Byrne, Michael, DeFilipp, Zachariah, Gabriel, Melissa, Mahindra, Anuj, Norkin, Maxim, Schoemans, Helene, Shah, Ami J., Ahmed, Ibrahim, Atsuta, Yoshiko, Basak, Grzegorz W., Beattie, Sara, Bhella, Sita, Bredeson, Christopher, Bunin, Nancy, Dalal, Jignesh, Daly, Andrew, Gajewski, James, Gale, Robert Peter, Galvin, John, Hamadani, Mehdi, Hayashi, Robert J., Adekola, Kehinde, Law, Jason, Lee, Catherine J., Liesveld, Jane, Malone, Adriana K., Nagler, Arnon, Naik, Seema, Nishihori, Taiga, Parsons, Susan K., Scherwath, Angela, Schofield, Hannah-Lise, Soiffer, Robert, Szer, Jeff, Twist, Ida, Warwick, Anne B., Wirk, Baldeep M., Yi, Jean, Battiwalla, Minoo, Flowers, Mary D. E., Savani, Bipin, Shaw, Bronwen E.
Published in Bone marrow transplantation (Basingstoke) (01.05.2018)
Published in Bone marrow transplantation (Basingstoke) (01.05.2018)
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Journal Article
Moving toward Individual Treatment Goals with Pegcetacoplan in Patients with PNH and Impaired Bone Marrow Function
Szer, Jeff, Panse, Jens, Kulasekararaj, Austin, Oliver, Monika, Fattizzo, Bruno, Nishimura, Jun-Ichi, Horneff, Regina, Szamosi, Johan, Peffault de Latour, Régis
Published in International journal of molecular sciences (06.08.2024)
Published in International journal of molecular sciences (06.08.2024)
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Journal Article
Pegcetacoplan versus Eculizumab in Paroxysmal Nocturnal Hemoglobinuria
Hillmen, Peter, Szer, Jeff, Weitz, Ilene, Röth, Alexander, Höchsmann, Britta, Panse, Jens, Usuki, Kensuke, Griffin, Morag, Kiladjian, Jean-Jacques, de Castro, Carlos, Nishimori, Hisakazu, Tan, Lisa, Hamdani, Mohamed, Deschatelets, Pascal, Francois, Cedric, Grossi, Federico, Ajayi, Temitayo, Risitano, Antonio, Peffault de Latour, Régis
Published in The New England journal of medicine (18.03.2021)
Published in The New England journal of medicine (18.03.2021)
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Journal Article
Erratum to: Utility of clinical comprehensive genomic characterization for diagnostic categorization in patients presenting with hypocellular bone marrow failure syndromes
Blombery, Piers, Fox, Lucy, Ryland, Georgina L, Thompson, Ella R, Lickiss, Jennifer, McBean, Michelle, Yerneni, Satwica, Trainer, Alison, Hughes, David, Greenway, Anthea, Mechinaud, Francoise, Wood, Erica M, Lieschke, Graham J, Szer, Jeff, Barbaro, Pasquale, Roy, John, Wight, Joel, Lynch, Elly, Martyn, Melissa, Gaff, Clara, Ritchie, David
Published in Haematologica (Roma) (01.04.2024)
Published in Haematologica (Roma) (01.04.2024)
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