First-in-human in vivo genome editing via AAV-zinc-finger nucleases for mucopolysaccharidosis I/II and hemophilia B
Harmatz, Paul, Prada, Carlos E., Burton, Barbara K., Lau, Heather, Kessler, Craig M., Cao, Liching, Falaleeva, Marina, Villegas, Andres G., Zeitler, Jennifer, Meyer, Kathleen, Miller, Weston, Wong Po Foo, Cheryl, Vaidya, Sagar, Swenson, Wendy, Shiue, Lisa H., Rouy, Didier, Muenzer, Joseph
Published in Molecular therapy (07.12.2022)
Published in Molecular therapy (07.12.2022)
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Journal Article
Bond fixation in annulenes. 11. Synthesis and absolute configuration of the enantiomeric 1,3-di-tert-butylcyclooctatetraenes. Quantitative kinetic assessment of the effect of nonvicinal tert-butyl groups on [8]annulene ring-inversion and bond-shifting barriers
Paquette, Leo A, Hanzawa, Yuji, McCullough, Kevin J, Tagle, Bruce, Swenson, Wendy, Clardy, Jon
Published in Journal of the American Chemical Society (01.05.1981)
Published in Journal of the American Chemical Society (01.05.1981)
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Journal Article