Development of a gene-editing approach to restore vision loss in Leber congenital amaurosis type 10
Maeder, Morgan L, Stefanidakis, Michael, Wilson, Christopher J, Baral, Reshica, Barrera, Luis Alberto, Bounoutas, George S, Bumcrot, David, Chao, Hoson, Ciulla, Dawn M, DaSilva, Jennifer A, Dass, Abhishek, Dhanapal, Vidya, Fennell, Tim J, Friedland, Ari E, Giannoukos, Georgia, Gloskowski, Sebastian W, Glucksmann, Alexandra, Gotta, Gregory M, Jayaram, Hariharan, Haskett, Scott J, Hopkins, Bei, Horng, Joy E, Joshi, Shivangi, Marco, Eugenio, Mepani, Rina, Reyon, Deepak, Ta, Terence, Tabbaa, Diana G, Samuelsson, Steven J, Shen, Shen, Skor, Maxwell N, Stetkiewicz, Pam, Wang, Tongyao, Yudkoff, Clifford, Myer, Vic E, Albright, Charles F, Jiang, Haiyan
Published in Nature medicine (01.02.2019)
Published in Nature medicine (01.02.2019)
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