Partial Rescue of F508del-CFTR Stability and Trafficking Defects by Double Corrector Treatment
Capurro, Valeria, Tomati, Valeria, Sondo, Elvira, Renda, Mario, Borrelli, Anna, Pastorino, Cristina, Guidone, Daniela, Venturini, Arianna, Giraudo, Alessandro, Mandrup Bertozzi, Sine, Musante, Ilaria, Bertozzi, Fabio, Bandiera, Tiziano, Zara, Federico, Galietta, Luis J. V., Pedemonte, Nicoletta
Published in International journal of molecular sciences (17.05.2021)
Published in International journal of molecular sciences (17.05.2021)
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Journal Article
Pharmacological Inhibition of the Ubiquitin Ligase RNF5 Rescues F508del-CFTR in Cystic Fibrosis Airway Epithelia
Sondo, Elvira, Falchi, Federico, Caci, Emanuela, Ferrera, Loretta, Giacomini, Elisa, Pesce, Emanuela, Tomati, Valeria, Mandrup Bertozzi, Sine, Goldoni, Luca, Armirotti, Andrea, Ravazzolo, Roberto, Cavalli, Andrea, Pedemonte, Nicoletta
Published in Cell chemical biology (19.07.2018)
Published in Cell chemical biology (19.07.2018)
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Journal Article
RNF5, DAB2 and Friends: Novel Drug Targets for Cystic Fibrosis
Sondo, Elvira, Pesce, Emanuela, Tomati, Valeria, Marini, Monica, Pedemonte, Nicoletta
Published in Current pharmaceutical design (01.01.2017)
Published in Current pharmaceutical design (01.01.2017)
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Journal Article
Influence of cell background on pharmacological rescue of mutant CFTR
Pedemonte, Nicoletta, Tomati, Valeria, Sondo, Elvira, Galietta, Luis J V
Published in American Journal of Physiology: Cell Physiology (01.04.2010)
Published in American Journal of Physiology: Cell Physiology (01.04.2010)
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Journal Article
The L467F-F508del Complex Allele Hampers Pharmacological Rescue of Mutant CFTR by Elexacaftor/Tezacaftor/Ivacaftor in Cystic Fibrosis Patients: The Value of the Ex Vivo Nasal Epithelial Model to Address Non-Responders to CFTR-Modulating Drugs
Sondo, Elvira, Cresta, Federico, Pastorino, Cristina, Tomati, Valeria, Capurro, Valeria, Pesce, Emanuela, Lena, Mariateresa, Iacomino, Michele, Baffico, Ave Maria, Coviello, Domenico, Bandiera, Tiziano, Zara, Federico, Galietta, Luis J V, Bocciardi, Renata, Castellani, Carlo, Pedemonte, Nicoletta
Published in International journal of molecular sciences (15.03.2022)
Published in International journal of molecular sciences (15.03.2022)
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Journal Article
Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis
Haque, A K M Ashiqul, Dewerth, Alexander, Antony, Justin S, Riethmüller, Joachim, Schweizer, Georg R, Weinmann, Petra, Latifi, Ngadhnjim, Yasar, Hanzey, Pedemonte, Nicoletta, Sondo, Elvira, Weidensee, Brian, Ralhan, Anjali, Laval, Julie, Schlegel, Patrick, Seitz, Christian, Loretz, Brigitta, Lehr, Claus-Michael, Handgretinger, Rupert, Kormann, Michael S D
Published in Scientific reports (13.11.2018)
Published in Scientific reports (13.11.2018)
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Journal Article
Genetic Inhibition Of The Ubiquitin Ligase Rnf5 Attenuates Phenotypes Associated To F508del Cystic Fibrosis Mutation
Tomati, Valeria, Sondo, Elvira, Armirotti, Andrea, Caci, Emanuela, Pesce, Emanuela, Marini, Monica, Gianotti, Ambra, Jeon, Young Ju, Cilli, Michele, Pistorio, Angela, Mastracci, Luca, Ravazzolo, Roberto, Scholte, Bob, Ronai, Ze'ev, Galietta, Luis J V, Pedemonte, Nicoletta
Published in Scientific reports (17.07.2015)
Published in Scientific reports (17.07.2015)
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Journal Article
Targeting of Ubiquitin E3 Ligase RNF5 as a Novel Therapeutic Strategy in Neuroectodermal Tumors
Principi, Elisa, Sondo, Elvira, Bianchi, Giovanna, Ravera, Silvia, Morini, Martina, Tomati, Valeria, Pastorino, Cristina, Zara, Federico, Bruno, Claudio, Eva, Alessandra, Pedemonte, Nicoletta, Raffaghello, Lizzia
Published in Cancers (01.04.2022)
Published in Cancers (01.04.2022)
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Journal Article
Upregulation of TMEM16A Protein in Bronchial Epithelial Cells by Bacterial Pyocyanin
Caci, Emanuela, Scudieri, Paolo, Di Carlo, Emma, Morelli, Patrizia, Bruno, Silvia, De Fino, Ida, Bragonzi, Alessandra, Gianotti, Ambra, Sondo, Elvira, Ferrera, Loretta, Palleschi, Alessandro, Santambrogio, Luigi, Ravazzolo, Roberto, Galietta, Luis J V
Published in PloS one (29.06.2015)
Published in PloS one (29.06.2015)
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Journal Article
Dual Activity of Aminoarylthiazoles on the Trafficking and Gating Defects of the Cystic Fibrosis Transmembrane Conductance Regulator Chloride Channel Caused by Cystic Fibrosis Mutations
Pedemonte, Nicoletta, Tomati, Valeria, Sondo, Elvira, Caci, Emanuela, Millo, Enrico, Armirotti, Andrea, Damonte, Gianluca, Zegarra-Moran, Olga, Galietta, Luis J.V.
Published in The Journal of biological chemistry (29.04.2011)
Published in The Journal of biological chemistry (29.04.2011)
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Journal Article
The anoctamin family: TMEM16A and TMEM16B as calcium‐activated chloride channels
Scudieri, Paolo, Sondo, Elvira, Ferrera, Loretta, Galietta, Luis J. V.
Published in Experimental physiology (01.02.2012)
Published in Experimental physiology (01.02.2012)
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Journal Article
Thiocyanate Transport in Resting and IL-4-Stimulated Human Bronchial Epithelial Cells: Role of Pendrin and Anion Channels
Pedemonte, Nicoletta, Caci, Emanuela, Sondo, Elvira, Caputo, Antonella, Rhoden, Kerry, Pfeffer, Ulrich, Di Candia, Michele, Bandettini, Roberto, Ravazzolo, Roberto, Zegarra-Moran, Olga, Galietta, Luis J. V
Published in Journal of Immunology (15.04.2007)
Published in Journal of Immunology (15.04.2007)
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Journal Article
The Autophagy Inhibitor Spautin-1 Antagonizes Rescue of Mutant CFTR Through an Autophagy-Independent and USP13-Mediated Mechanism
Pesce, Emanuela, Sondo, Elvira, Ferrera, Loretta, Tomati, Valeria, Caci, Emanuela, Scudieri, Paolo, Musante, Ilaria, Renda, Mario, Baatallah, Nesrine, Servel, Nathalie, Hinzpeter, Alexandre, di Bernardo, Diego, Pedemonte, Nicoletta, Galietta, Luis J V
Published in Frontiers in pharmacology (13.12.2018)
Published in Frontiers in pharmacology (13.12.2018)
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Journal Article
Alternative splicing at a NAGNAG acceptor site as a novel phenotype modifier
Hinzpeter, Alexandre, Aissat, Abdel, Sondo, Elvira, Costa, Catherine, Arous, Nicole, Gameiro, Christine, Martin, Natacha, Tarze, Agathe, Weiss, Laurence, de Becdelièvre, Alix, Costes, Bruno, Goossens, Michel, Galietta, Luis J, Girodon, Emmanuelle, Fanen, Pascale
Published in PLoS genetics (07.10.2010)
Published in PLoS genetics (07.10.2010)
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Journal Article
Targeting the E1 ubiquitin-activating enzyme (UBA1) improves elexacaftor/tezacaftor/ivacaftor efficacy towards F508del and rare misfolded CFTR mutants
Borgo, Christian, D’Amore, Claudio, Capurro, Valeria, Tomati, Valeria, Sondo, Elvira, Cresta, Federico, Castellani, Carlo, Pedemonte, Nicoletta, Salvi, Mauro
Published in Cellular and molecular life sciences : CMLS (01.04.2022)
Published in Cellular and molecular life sciences : CMLS (01.04.2022)
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Journal Article
TMEM16A, A Membrane Protein Associated with Calcium-Dependent Chloride Channel Activity
Caputo, Antonella, Caci, Emanuela, Ferrera, Loretta, Pedemonte, Nicoletta, Barsanti, Cristina, Sondo, Elvira, Pfeffer, Ulrich, Ravazzolo, Roberto, Zegarra-Moran, Olga, Galietta, Luis J.V
Published in Science (American Association for the Advancement of Science) (24.10.2008)
Published in Science (American Association for the Advancement of Science) (24.10.2008)
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Journal Article
Ion channel and lipid scramblase activity associated with expression of TMEM16F/ANO6 isoforms
Scudieri, Paolo, Caci, Emanuela, Venturini, Arianna, Sondo, Elvira, Pianigiani, Giulia, Marchetti, Carla, Ravazzolo, Roberto, Pagani, Franco, Galietta, Luis J. V.
Published in The Journal of physiology (01.09.2015)
Published in The Journal of physiology (01.09.2015)
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