Establishment of two quantitative nested qPCR assays targeting the human EPO transgene
Neuberger, E W I, Perez, I, Le Guiner, C, Moser, D, Ehlert, T, Allais, M, Moullier, P, Simon, P, Snyder, R O
Published in Gene therapy (01.04.2016)
Published in Gene therapy (01.04.2016)
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Journal Article
Midbrain Injection of Recombinant Adeno-Associated Virus Encoding Rat Glial Cell Line-Derived Neurotrophic Factor Protects Nigral Neurons in a Progressive 6-hydroxydopamine-Induced Degeneration Model of Parkinson's Disease in Rats
Mandel, R. J., Spratt, S. K., Snyder, R. O., Leff, S. E.
Published in Proceedings of the National Academy of Sciences - PNAS (09.12.1997)
Published in Proceedings of the National Academy of Sciences - PNAS (09.12.1997)
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Journal Article
Characterization of Intrastriatal Recombinant Adeno-Associated Virus-Mediated Gene Transfer of Human Tyrosine Hydroxylase and Human GTP-Cyclohydrolase I in a Rat Model of Parkinson's Disease
Mandel, R. J, Rendahl, K. G, Spratt, S. K, Snyder, R. O, Cohen, L. K, Leff, S. E
Published in The Journal of neuroscience (01.06.1998)
Published in The Journal of neuroscience (01.06.1998)
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Journal Article
Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors
Snyder, Richard O, Miao, Carol H, Patijn, Gijsbert A, Spratt, S. Kaye, Danos, Olivier, Nagy, Dea, Gown, Allen M, Winther, Brian, Meuse, Leonard, Cohen, Lawrence K, Thompson, Arthur R, Kay, Mark A
Published in Nature genetics (01.07.1997)
Published in Nature genetics (01.07.1997)
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Journal Article
Nerve growth factor expressed in the medial septum following in vivo gene delivery using a recombinant adeno-associated viral vector protects cholinergic neurons from fimbria-fornix lesion-induced degeneration
MANDEL, R. J, GAGE, F. H, CLEVENGER, D. G, SPRATT, S. K, SNYDER, R. O, LEFF, S. E
Published in Experimental neurology (1999)
Published in Experimental neurology (1999)
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Journal Article
Features of the adeno-associated virus origin involved in substrate recognition by the viral Rep protein
Snyder, R O, Im, D S, Ni, T, Xiao, X, Samulski, R J, Muzyczka, N
Published in Journal of Virology (01.10.1993)
Published in Journal of Virology (01.10.1993)
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Journal Article
Regulation of gene expression in vivo following transduction by two separate rAAV vectors
Rendahl, Katherine G, Leff, Stuart E, Otten, Gillis R, Spratt, S. Kaye, Bohl, Delphine, Van Roey, Melinda, Donahue, Brian A, Cohen, Lawrence K, Mandel, Ronald J, Danos, Olivier, Snyder, Richard O
Published in Nature biotechnology (01.08.1998)
Published in Nature biotechnology (01.08.1998)
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Journal Article
Progress in direct striatal delivery of L-dopa via gene therapy for treatment of Parkinson's disease using recombinant adeno-associated viral vectors
MANDEL, R. J, RENDAHL, K. G, SNYDER, R. O, LEFF, S. E
Published in Experimental neurology (01.09.1999)
Published in Experimental neurology (01.09.1999)
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Conference Proceeding
Journal Article
Practical aspects of the development of ex vivo and in vivo gene therapy for Parkinson's disease
BANKIEWICZ, K. S, LEFF, S. E, NAGY, D, JUNGLES, S, ROKOVICH, J, SPRATT, K, COHEN, L, LIBONATI, M, SNYDER, R. O, MANDEL, R. J
Published in Experimental neurology (01.03.1997)
Published in Experimental neurology (01.03.1997)
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Conference Proceeding
Journal Article
Epitope Mapping of Human Anti-Adeno-Associated Virus Type 2 Neutralizing Antibodies: Implications for Gene Therapy and Virus Structure
Moskalenko, M, Chen, L, van Roey, M, Donahue, B A, Snyder, R O, McArthur, J G, Patel, S D
Published in Journal of Virology (01.02.2000)
Published in Journal of Virology (01.02.2000)
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Journal Article
Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors
Kay, Mark A, Snyder, Richard O, Miao, Carol, Meuse, Leonard, Tubb, Julie, Donahue, Brian A, Lin, Hui-Feng, Stafford, Darrel W, Patel, Salil, Thompson, Arthur R, Nichols, Timothy, Read, Marjorie S, Bellinger, Dwight A, Brinkhous, Kenneth M
Published in Nature medicine (01.01.1999)
Published in Nature medicine (01.01.1999)
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Journal Article
Nonrandom Transduction of Recombinant Adeno-Associated Virus Vectors in Mouse Hepatocytes In Vivo: Cell Cycling Does Not Influence Hepatocyte Transduction
Miao, C H, Nakai, H, Thompson, A R, Storm, T A, Chiu, W, Snyder, R O, Kay, M A
Published in Journal of Virology (01.04.2000)
Published in Journal of Virology (01.04.2000)
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Journal Article
Efficient and stable adeno-associated virus-mediated transduction in the skeletal muscle of adult immunocompetent mice
Snyder, R O, Spratt, S K, Lagarde, C, Bohl, D, Kaspar, B, Sloan, B, Cohen, L K, Danos, O
Published in Human gene therapy (01.11.1997)
Published in Human gene therapy (01.11.1997)
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Journal Article
The kinetics of rAAV integration in the liver
Miao, Carol H, Snyder, Richard O, Schowalter, David B, Patijn, Gijsbert A, Donahue, Brian, Winther, Brian, Kay, Mark A
Published in Nature genetics (01.05.1998)
Published in Nature genetics (01.05.1998)
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Journal Article
Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease
Kim, Jinkuk, Hu, Chunguang, Moufawad El Achkar, Christelle, Black, Lauren E, Douville, Julie, Larson, Austin, Pendergast, Mary K, Goldkind, Sara F, Lee, Eunjung A, Kuniholm, Ashley, Soucy, Aubrie, Vaze, Jai, Belur, Nandkishore R, Fredriksen, Kristina, Stojkovska, Iva, Tsytsykova, Alla, Armant, Myriam, DiDonato, Renata L, Choi, Jaejoon, Cornelissen, Laura, Pereira, Luis M, Augustine, Erika F, Genetti, Casie A, Dies, Kira, Barton, Brenda, Williams, Lucinda, Goodlett, Benjamin D, Riley, Bobbie L, Pasternak, Amy, Berry, Emily R, Pflock, Kelly A, Chu, Stephen, Reed, Chantal, Tyndall, Kimberly, Agrawal, Pankaj B, Beggs, Alan H, Grant, P. Ellen, Urion, David K, Snyder, Richard O, Waisbren, Susan E, Poduri, Annapurna, Park, Peter J, Patterson, Al, Biffi, Alessandra, Mazzulli, Joseph R, Bodamer, Olaf, Berde, Charles B, Yu, Timothy W
Published in The New England journal of medicine (24.10.2019)
Published in The New England journal of medicine (24.10.2019)
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Journal Article