Therapeutic Oligonucleotides: State of the Art
Smith, C.I. Edvard, Zain, Rula
Published in Annual review of pharmacology and toxicology (06.01.2019)
Published in Annual review of pharmacology and toxicology (06.01.2019)
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Cells release subpopulations of exosomes with distinct molecular and biological properties
Willms, Eduard, Johansson, Henrik J, Mäger, Imre, Lee, Yi, Blomberg, K Emelie M, Sadik, Mariam, Alaarg, Amr, Smith, C I Edvard, Lehtiö, Janne, El Andaloussi, Samir, Wood, Matthew J A, Vader, Pieter
Published in Scientific reports (02.03.2016)
Published in Scientific reports (02.03.2016)
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X-linked recessive TLR7 deficiency in ~1% of men under 60 years old with life-threatening COVID-19
Asano, Takaki, Boisson, Bertrand, Onodi, Fanny, Matuozzo, Daniela, Moncada-Velez, Marcela, Maglorius Renkilaraj, Majistor Raj Luxman, Zhang, Peng, Meertens, Laurent, Bolze, Alexandre, Materna, Marie, Korniotis, Sarantis, Gervais, Adrian, Talouarn, Estelle, Bigio, Benedetta, Seeleuthner, Yoann, Bilguvar, Kaya, Zhang, Yu, Neehus, Anna-Lena, Ogishi, Masato, Pelham, Simon J, Le Voyer, Tom, Rosain, Jérémie, Philippot, Quentin, Soler-Palacín, Pere, Colobran, Roger, Martin-Nalda, Andrea, Rivière, Jacques G, Tandjaoui-Lambiotte, Yacine, Chaïbi, Khalil, Shahrooei, Mohammad, Darazam, Ilad Alavi, Olyaei, Nasrin Alipour, Mansouri, Davood, Hatipoğlu, Nevin, Palabiyik, Figen, Ozcelik, Tayfun, Novelli, Giuseppe, Novelli, Antonio, Casari, Giorgio, Bondesan, Simone, Barzaghi, Federica, Rovere-Querini, Patrizia, Franco, Jose Luis, Rojas, Julian, Reyes, Luis Felipe, Bustos, Ingrid G, Arias, Andres Augusto, Morelle, Guillaume, Christèle, Kyheng, Troya, Jesús, Planas-Serra, Laura, Schlüter, Agatha, Gut, Marta, Pujol, Aurora, Allende, Luis M, Rodriguez-Gallego, Carlos, Flores, Carlos, Cabrera-Marante, Oscar, Pleguezuelo, Daniel E, de Diego, Rebeca Pérez, Keles, Sevgi, Aytekin, Gokhan, Akcan, Ozge Metin, Bryceson, Yenan T, Bergman, Peter, Brodin, Petter, Smole, Daniel, Smith, C I Edvard, Norlin, Anna-Carin, Campbell, Tessa M, Covill, Laura E, Hammarström, Lennart, Abolhassani, Hassan, Mane, Shrikant, Marr, Nico, Ata, Manar, Al Ali, Fatima, Khan, Taushif, Spaan, András N, Dalgard, Clifton L, Bonfanti, Paolo, Biondi, Andrea, Tubiana, Sarah, Burdet, Charles, Nussbaum, Robert, Kahn-Kirby, Amanda, Snow, Andrew L, Bustamante, Jacinta, Puel, Anne, Boisson-Dupuis, Stéphanie, Zhang, Shen-Ying, Lifton, Richard P, Bastard, Paul, Notarangelo, Luigi D, Su, Helen C, Jouanguy, Emmanuelle, Soumelis, Vassili, Cobat, Aurélie, Zhang, Qian, Casanova, Jean-Laurent
Published in Science Immunology (19.08.2021)
Published in Science Immunology (19.08.2021)
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Comparative Analysis of BTK Inhibitors and Mechanisms Underlying Adverse Effects
Estupiñán, H Yesid, Berglöf, Anna, Zain, Rula, Smith, C I Edvard
Published in Frontiers in cell and developmental biology (11.03.2021)
Published in Frontiers in cell and developmental biology (11.03.2021)
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Ultrafiltration with size-exclusion liquid chromatography for high yield isolation of extracellular vesicles preserving intact biophysical and functional properties
Nordin, Joel Z., M.D, Lee, Yi, BSc, Vader, Pieter, PhD, Mäger, Imre, PhD, Johansson, Henrik J., PhD, Heusermann, Wolf, PhD, Wiklander, Oscar P.B., M.D, Hällbrink, Mattias, PhD, Seow, Yiqi, DPhil, Bultema, Jarred J., PhD, Gilthorpe, Jonathan, PhD, Davies, Tim, MSc, Fairchild, Paul J., PhD, Gabrielsson, Susanne, PhD, Meisner-Kober, Nicole C., PhD, Lehtiö, Janne, PhD, Smith, C.I. Edvard, M.D., PhD, Wood, Matthew J.A., M.D., DPhil, Andaloussi, Samir EL, PhD
Published in Nanomedicine (01.05.2015)
Published in Nanomedicine (01.05.2015)
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Umbilical cord-derived mesenchymal stromal cells preserve endogenous insulin production in type 1 diabetes: a Phase I/II randomised double-blind placebo-controlled trial
Carlsson, Per-Ola, Espes, Daniel, Sisay, Sofia, Davies, Lindsay C., Smith, C. I. Edvard, Svahn, Mathias G.
Published in Diabetologia (01.08.2023)
Published in Diabetologia (01.08.2023)
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Safety and efficacy of the mRNA BNT162b2 vaccine against SARS-CoV-2 in five groups of immunocompromised patients and healthy controls in a prospective open-label clinical trial
Bergman, Peter, Blennow, Ola, Hansson, Lotta, Mielke, Stephan, Nowak, Piotr, Chen, Puran, Söderdahl, Gunnar, Österborg, Anders, Smith, C. I. Edvard, Wullimann, David, Vesterbacka, Jan, Lindgren, Gustaf, Blixt, Lisa, Friman, Gustav, Wahren-Borgström, Emilie, Nordlander, Anna, Gomez, Angelica Cuapio, Akber, Mira, Valentini, Davide, Norlin, Anna-Carin, Thalme, Anders, Bogdanovic, Gordana, Muschiol, Sandra, Nilsson, Peter, Hober, Sophia, Loré, Karin, Chen, Margaret Sällberg, Buggert, Marcus, Ljunggren, Hans-Gustaf, Ljungman, Per, Aleman, Soo
Published in EBioMedicine (01.12.2021)
Published in EBioMedicine (01.12.2021)
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BTK gatekeeper residue variation combined with cysteine 481 substitution causes super-resistance to irreversible inhibitors acalabrutinib, ibrutinib and zanubrutinib
Estupiñán, H Yesid, Wang, Qing, Berglöf, Anna, Schaafsma, Gerard C P, Shi, Yuye, Zhou, Litao, Mohammad, Dara K, Yu, Liang, Vihinen, Mauno, Zain, Rula, Smith, C I Edvard
Published in Leukemia (01.05.2021)
Published in Leukemia (01.05.2021)
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Immunodeficiency syndromes differentially impact the functional profile of SARS-CoV-2-specific T cells elicited by mRNA vaccination
Gao, Yu, Cai, Curtis, Wullimann, David, Niessl, Julia, Rivera-Ballesteros, Olga, Chen, Puran, Lange, Joshua, Cuapio, Angelica, Blennow, Ola, Hansson, Lotta, Mielke, Stephan, Nowak, Piotr, Vesterbacka, Jan, Akber, Mira, Perez-Potti, Andre, Sekine, Takuya, Müller, Thomas R., Boulouis, Caroline, Kammann, Tobias, Parrot, Tiphaine, Muvva, Jagadeeswara Rao, Sobkowiak, Michal, Healy, Katie, Bogdanovic, Gordana, Muschiol, Sandra, Söderdahl, Gunnar, Österborg, Anders, Hellgren, Fredrika, Grifoni, Alba, Weiskopf, Daniela, Sette, Alessandro, Loré, Karin, Sällberg Chen, Margaret, Ljungman, Per, Sandberg, Johan K., Smith, C.I. Edvard, Bergman, Peter, Ljunggren, Hans-Gustaf, Aleman, Soo, Buggert, Marcus
Published in Immunity (13.09.2022)
Published in Immunity (13.09.2022)
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Large-scale expansions of Friedreich's ataxia GAA•TTC repeats in an experimental human system: role of DNA replication and prevention by LNA-DNA oligonucleotides and PNA oligomers
Rastokina, Anastasia, Cebrián, Jorge, Mozafari, Negin, Mandel, Nicholas H, Smith, C I Edvard, Lopes, Massimo, Zain, Rula, Mirkin, Sergei M
Published in Nucleic acids research (08.09.2023)
Published in Nucleic acids research (08.09.2023)
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Respiratory viral infections in otherwise healthy humans with inherited IRF7 deficiency
Campbell, Tessa Mollie, Liu, Zhiyong, Zhang, Qian, Moncada-Velez, Marcela, Covill, Laura E, Zhang, Peng, Alavi Darazam, Ilad, Bastard, Paul, Bizien, Lucy, Bucciol, Giorgia, Lind Enoksson, Sara, Jouanguy, Emmanuelle, Karabela, Şemsi Nur, Khan, Taushif, Kendir-Demirkol, Yasemin, Arias, Andres Augusto, Mansouri, Davood, Marits, Per, Marr, Nico, Migeotte, Isabelle, Moens, Leen, Ozcelik, Tayfun, Pellier, Isabelle, Sendel, Anton, Şenoğlu, Sevtap, Shahrooei, Mohammad, Smith, C I Edvard, Vandernoot, Isabelle, Willekens, Karen, Kart Yaşar, Kadriye, Bergman, Peter, Abel, Laurent, Cobat, Aurélie, Casanova, Jean-Laurent, Meyts, Isabelle, Bryceson, Yenan T
Published in The Journal of experimental medicine (04.07.2022)
Published in The Journal of experimental medicine (04.07.2022)
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Prevalence, genetics and clinical presentation of chronic granulomatous disease in Sweden
Ahlin, A, De Boer, M, Roos, D, Leusen, J, Smith, C I, Sundin, U, Rabbani, H, Palmblad, J, Elinder, G
Published in Acta pædiatrica (Oslo) (01.12.1995)
Published in Acta pædiatrica (Oslo) (01.12.1995)
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Bruton's tyrosine kinase (Btk): function, regulation, and transformation with special emphasis on the PH domain
Mohamed, Abdalla J, Yu, Liang, Bäckesjö, Carl-Magnus, Vargas, Leonardo, Faryal, Rani, Aints, Alar, Christensson, Birger, Berglöf, Anna, Vihinen, Mauno, Nore, Beston F, Edvard Smith, C.I
Published in Immunological reviews (01.03.2009)
Published in Immunological reviews (01.03.2009)
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Neutralizing SARS-CoV-2 Antibodies in Commercial Immunoglobulin Products Give Patients with X-Linked Agammaglobulinemia Limited Passive Immunity to the Omicron Variant
Lindahl, Hannes, Klingström, Jonas, Da Silva Rodrigues, Rui, Christ, Wanda, Chen, Puran, Ljunggren, Hans-Gustaf, Buggert, Marcus, Aleman, Soo, Smith, C. I. Edvard, Bergman, Peter
Published in Journal of clinical immunology (01.08.2022)
Published in Journal of clinical immunology (01.08.2022)
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