Dominant-negative SERPING1 variants cause intracellular retention of C1 inhibitor in hereditary angioedema
Haslund, Didde, Ryø, Laura Barrett, Seidelin Majidi, Sara, Rose, Iben, Skipper, Kristian Alsbjerg, Fryland, Tue, Bohn, Anja Bille, Koch, Claus, Thomsen, Martin K, Palarasah, Yaseelan, Corydon, Thomas J, Bygum, Anette, Nejsum, Lene N, Mikkelsen, Jacob Giehm
Published in The Journal of clinical investigation (01.01.2019)
Published in The Journal of clinical investigation (01.01.2019)
Get full text
Journal Article
Sustained transgene expression from sleeping beauty DNA transposons containing a core fragment of the HNRPA2B1-CBX3 ubiquitous chromatin opening element (UCOE)
Skipper, Kristian Alsbjerg, Hollensen, Anne Kruse, Antoniou, Michael N, Mikkelsen, Jacob Giehm
Published in BMC biotechnology (09.11.2019)
Published in BMC biotechnology (09.11.2019)
Get full text
Journal Article
DNA transposon-based gene vehicles - scenes from an evolutionary drive
Skipper, Kristian Alsbjerg, Andersen, Peter Refsing, Sharma, Nynne, Mikkelsen, Jacob Giehm
Published in Journal of biomedical science (09.12.2013)
Published in Journal of biomedical science (09.12.2013)
Get full text
Journal Article
CRISPR-Cas9-directed gene tagging using a single integrase-defective lentiviral vector carrying a transposase-based Cas9 off switch
Thomsen, Emil Aagaard, Skipper, Kristian Alsbjerg, Andersen, Sofie, Haslund, Didde, Skov, Thomas Wisbech, Mikkelsen, Jacob Giehm
Published in Molecular therapy. Nucleic acids (13.09.2022)
Published in Molecular therapy. Nucleic acids (13.09.2022)
Get full text
Journal Article
Single-Cell Monitoring of Activated Innate Immune Signaling by a d2eGFP-Based Reporter Mimicking Time-Restricted Activation of IFNB1 Expression
Thomsen, Emil Aagaard, Andersen, Sofie, Marqvorsen, Mikkel Haarslev Schröder, Skipper, Kristian Alsbjerg, Paludan, Søren R, Mikkelsen, Jacob Giehm
Published in Frontiers in cellular and infection microbiology (18.01.2022)
Published in Frontiers in cellular and infection microbiology (18.01.2022)
Get full text
Journal Article
Time-Restricted PiggyBac DNA Transposition by Transposase Protein Delivery Using Lentivirus-Derived Nanoparticles
Skipper, Kristian Alsbjerg, Nielsen, Mathias Gaarde, Andersen, Sofie, Ryø, Laura Barrett, Bak, Rasmus O., Mikkelsen, Jacob Giehm
Published in Molecular therapy. Nucleic acids (01.06.2018)
Published in Molecular therapy. Nucleic acids (01.06.2018)
Get full text
Journal Article
Toward In Vivo Gene Therapy Using CRISPR
Skipper, Kristian Alsbjerg, Mikkelsen, Jacob Giehm
Published in Methods in molecular biology (Clifton, N.J.) (2019)
Published in Methods in molecular biology (Clifton, N.J.) (2019)
Get more information
Journal Article
Optimizing retroviral gene expression for effective therapies
Antoniou, Michael N, Skipper, Kristian Alsbjerg, Anakok, Omer
Published in Human gene therapy (01.04.2013)
Published in Human gene therapy (01.04.2013)
Get more information
Journal Article
Essential role of autophagy in restricting poliovirus infection revealed by identification of an ATG7 defect in a poliomyelitis patient
Brinck Andersen, Nanna-Sophie, Jørgensen, Sofie Eg, Skipper, Kristian Alsbjerg, Larsen, Simon Müller, Heinz, Johanna, Thomsen, Michelle Mølgaard, Farahani, Ensieh, Cai, Yujia, Hait, Alon Schneider, Kay, Lise, Giehm Mikkelsen, Jacob, Høgsbjerg Schleimann, Mariane, Thomsen, Martin Kristian, Paludan, Søren R., Mogensen, Trine H.
Published in Autophagy (02.09.2021)
Published in Autophagy (02.09.2021)
Get full text
Journal Article
Dominant-negative SERPING1 variants cause intracellular retention of C1 inhibitor in hereditary angioedema
Haslund, Didde, Ryø, Laura Barrett, Majidi, Sara Seidelin, Rose, Iben, Skipper, Kristian Alsbjerg, Fryland, Tue, Bohn, Anja Bille, Koch, Claus, Thomsen, Martin K, Palarasah, Yaseelan, Corydon, Thomas J, Bygum, Anette, Nejsum, Lene N, Mikkelsen, Jacob Giehm
Published in The Journal of clinical investigation (01.01.2019)
Published in The Journal of clinical investigation (01.01.2019)
Get full text
Journal Article
Defects in LC3B2 and ATG4A underlie HSV2 meningitis and reveal a critical role for autophagy in antiviral defense in humans
Hait, Alon Schneider, Olagnier, David, Sancho-Shimizu, Vanessa, Skipper, Kristian Alsbjerg, Helleberg, Marie, Larsen, Simon Muller, Bodda, Chiranjeevi, Moldovan, Liviu Ionut, Ren, Fanghui, Brinck Andersen, Nanna-Sophie, Thomsen, Michelle M, Freytag, Mette Ratzer, Darmalinggam, Sathya, Parkes, Isobel, Kadekar, Darshana D, Rahbek, Stine Hess, van der Horst, Demi, Kristensen, Lasse Sommer, Eriksson, Kristina, Kjems, Jørgen, Mostowy, Serge, Christiansen, Mette, Mikkelsen, Jacob Giehm, Brandt, Christian Thomas, Paludan, Søren R, Mogensen, Trine H
Published in Science immunology (11.12.2020)
Published in Science immunology (11.12.2020)
Get more information
Journal Article