Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
Balwani, Manisha, Sardh, Eliane, Ventura, Paolo, Peiró, Paula Aguilera, Rees, David C, Stölzel, Ulrich, Bissell, D. Montgomery, Bonkovsky, Herbert L, Windyga, Jerzy, Anderson, Karl E, Parker, Charles, Silver, Samuel M, Keel, Siobán B, Wang, Jiaan-Der, Stein, Penelope E, Harper, Pauline, Vassiliou, Daphne, Wang, Bruce, Phillips, John, Ivanova, Aneta, Langendonk, Janneke G, Kauppinen, Raili, Minder, Elisabeth, Horie, Yutaka, Penz, Craig, Chen, Jihong, Liu, Shangbin, Ko, John J, Sweetser, Marianne T, Garg, Pushkal, Vaishnaw, Akshay, Kim, Jae B, Simon, Amy R, Gouya, Laurent
Published in The New England journal of medicine (11.06.2020)
Published in The New England journal of medicine (11.06.2020)
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Journal Article
FIRST RESULTS FROM THE HUBBLE OPAL PROGRAM: JUPITER IN 2015
Simon, Amy A., Wong, Michael H., Orton, Glenn S.
Published in The Astrophysical journal (10.10.2015)
Published in The Astrophysical journal (10.10.2015)
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Journal Article
A Highly Durable RNAi Therapeutic Inhibitor of PCSK9
Fitzgerald, Kevin, White, Suellen, Borodovsky, Anna, Bettencourt, Brian R, Strahs, Andrew, Clausen, Valerie, Wijngaard, Peter, Horton, Jay D, Taubel, Jorg, Brooks, Ashley, Fernando, Chamikara, Kauffman, Robert S, Kallend, David, Vaishnaw, Akshay, Simon, Amy
Published in The New England journal of medicine (05.01.2017)
Published in The New England journal of medicine (05.01.2017)
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Journal Article
Pharmacokinetics and Pharmacodynamics of the Small Interfering Ribonucleic Acid, Givosiran, in Patients With Acute Hepatic Porphyria
Agarwal, Sagar, Simon, Amy R, Goel, Varun, Habtemariam, Bahru A, Clausen, Valerie A, Kim, Jae B, Robbie, Gabriel J
Published in Clinical pharmacology and therapeutics (01.07.2020)
Published in Clinical pharmacology and therapeutics (01.07.2020)
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Journal Article
Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria
Sardh, Eliane, Harper, Pauline, Balwani, Manisha, Stein, Penelope, Rees, David, Bissell, D. Montgomery, Desnick, Robert, Parker, Charles, Phillips, John, Bonkovsky, Herbert L, Vassiliou, Daphne, Penz, Craig, Chan-Daniels, Amy, He, Qiuling, Querbes, William, Fitzgerald, Kevin, Kim, Jae B, Garg, Pushkal, Vaishnaw, Akshay, Simon, Amy R, Anderson, Karl E
Published in The New England journal of medicine (07.02.2019)
Published in The New England journal of medicine (07.02.2019)
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Journal Article
Hubble Detects the Start of a New Saturn Ring Spoke Season
Simon, Amy A., Nicholson, Philip D., Tiscareno, Matthew S., Showalter, Mark R., McDonald, Troy
Published in Geophysical research letters (16.02.2023)
Published in Geophysical research letters (16.02.2023)
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Journal Article
Widespread carbon-bearing materials on near-Earth asteroid (101955) Bennu
Simon, Amy A., Kaplan, Hannah H., Hamilton, Victoria E., Lauretta, Dante S., Campins, Humberto, Barucci, M. Antonietta, DellaGiustina, Daniella N., Reuter, Dennis C., Sandford, Scott A., Lim, Lucy F., Rozitis, Benjamin
Published in Science (American Association for the Advancement of Science) (06.11.2020)
Published in Science (American Association for the Advancement of Science) (06.11.2020)
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Journal Article
An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia
Sehgal, Alfica, Barros, Scott, Ivanciu, Lacramioara, Cooley, Brian, Qin, June, Racie, Tim, Hettinger, Julia, Carioto, Mary, Jiang, Yongfeng, Brodsky, Josh, Prabhala, Harsha, Zhang, Xuemei, Attarwala, Husain, Hutabarat, Renta, Foster, Don, Milstein, Stuart, Charisse, Klaus, Kuchimanchi, Satya, Maier, Martin A, Nechev, Lubo, Kandasamy, Pachamuthu, Kel'in, Alexander V, Nair, Jayaprakash K, Rajeev, Kallanthottathil G, Manoharan, Muthiah, Meyers, Rachel, Sorensen, Benny, Simon, Amy R, Dargaud, Yesim, Negrier, Claude, Camire, Rodney M, Akinc, Akin
Published in Nature medicine (01.05.2015)
Published in Nature medicine (01.05.2015)
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Journal Article
ALN-RSV01 for prevention of bronchiolitis obliterans syndrome after respiratory syncytial virus infection in lung transplant recipients
Gottlieb, Jens, MD, Zamora, Martin R., MD, Hodges, Tony, MD, Musk, A.W., MD, Sommerwerk, Urte, MD, Dilling, Daniel, MD, FACP, Arcasoy, Selim, MD, DeVincenzo, John, MD, Karsten, Verena, PhD, Shah, Shaily, Bettencourt, Brian R., PhD, Cehelsky, Jeffrey, MBA, Nochur, Sara, PhD, Gollob, Jared, MD, Vaishnaw, Akshay, MD, Simon, Amy R., MD, Glanville, Allan R., MD, MBBS
Published in The Journal of heart and lung transplantation (01.02.2016)
Published in The Journal of heart and lung transplantation (01.02.2016)
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Journal Article
In-Flight Calibration and Performance of the OSIRIS-REx Visible and IR Spectrometer (OVIRS)
Simon, Amy A., Reuter, Dennis C., Gorius, Nicolas, Lunsford, Allen W., Cosentino, Richard, Wind, Galina, Lauretta, Dante S.
Published in Remote sensing (Basel, Switzerland) (01.09.2018)
Published in Remote sensing (Basel, Switzerland) (01.09.2018)
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Journal Article
Fundamental Science Achieved with a Single Probe in Each Giant Planet Atmosphere
Mandt, Kathleen E., Simon, Amy A., Mousis, Olivier, Atkinson, David H., Hofstadter, Mark
Published in Space science reviews (01.08.2024)
Published in Space science reviews (01.08.2024)
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Journal Article
Effect of an RNA interference drug on the synthesis of proprotein convertase subtilisin/kexin type 9 (PCSK9) and the concentration of serum LDL cholesterol in healthy volunteers: a randomised, single-blind, placebo-controlled, phase 1 trial
Fitzgerald, Kevin, Dr, Frank-Kamenetsky, Maria, PhD, Shulga-Morskaya, Svetlana, MSc, Liebow, Abigail, BS, Bettencourt, Brian R, PhD, Sutherland, Jessica E, PhD, Hutabarat, Renta M, PhD, Clausen, Valerie A, PhD, Karsten, Verena, PhD, Cehelsky, Jeffrey, MBA, Nochur, Saraswathy V, PhD, Kotelianski, Victor, MD, Horton, Jay, MD, Mant, Timothy, MD, Chiesa, Joseph, MD, Ritter, James, MD, Munisamy, Malathy, MD, Vaishnaw, Akshay K, MD, Gollob, Jared A, MD, Simon, Amy, MD
Published in The Lancet (British edition) (04.01.2014)
Published in The Lancet (British edition) (04.01.2014)
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Journal Article
Modelling the seasonal cycle of Uranus’s colour and magnitude, and comparison with Neptune
Irwin, Patrick G J, Dobinson, Jack, James, Arjuna, Teanby, Nicholas A, Simon, Amy A, Fletcher, Leigh N, Roman, Michael T, Orton, Glenn S, Wong, Michael H, Toledo, Daniel, Pérez-Hoyos, Santiago, Beck, Julie
Published in Monthly notices of the Royal Astronomical Society (01.02.2024)
Published in Monthly notices of the Royal Astronomical Society (01.02.2024)
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Journal Article
Cassini spacecraft reveals global energy imbalance of Saturn
Wang, Xinyue, Li, Liming, Jiang, Xun, Fry, Patrick M., West, Robert A., Nixon, Conor A., Guan, Larry, Karandana G, Thishan D., Albright, Ronald, Colwell, Joshua E., Guillot, Tristan, Hofstadter, Mark D., Kenyon, Matthew E., Mallama, Anthony, Perez-Hoyos, Santiago, Sanchez-Lavega, Agustin, Simon, Amy A., Wenkert, Daniel, Zhang, Xi
Published in Nature communications (18.06.2024)
Published in Nature communications (18.06.2024)
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Journal Article
Widely Distributed Exogenic Materials of Varying Compositions and Morphologies on Asteroid (101955) Bennu
Tatsumi, Eri, Popescu, Marcel, Campins, Humberto, León, Julia de, García, Juan Luis Rizos, Licandro, Javier, Simon, Amy A., Kaplan, Hannah H, DellaGiustina, Daniella N, Golish, Dathon R, Lauretta, Dante S
Published in Monthly notices of the Royal Astronomical Society (01.12.2021)
Published in Monthly notices of the Royal Astronomical Society (01.12.2021)
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Journal Article
High-resolution UV/Optical/IR Imaging of Jupiter in 2016-2019
Wong, Michael H., Simon, Amy A., Tollefson, Joshua W., de Pater, Imke, Barnett, Megan N., Hsu, Andrew I., Stephens, Andrew W., Orton, Glenn S., Fleming, Scott W., Goullaud, Charles, Januszewski, William, Roman, Anthony, Bjoraker, Gordon L., Atreya, Sushil K., Adriani, Alberto, Fletcher, Leigh N.
Published in The Astrophysical journal. Supplement series (01.04.2020)
Published in The Astrophysical journal. Supplement series (01.04.2020)
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Journal Article
Constraints on Uranus's haze structure, formation and transport
Toledo, Daniel, Irwin, Patrick G.J., Rannou, Pascal, Teanby, Nicholas A., Simon, Amy A., Wong, Michael H., Orton, Glenn S.
Published in Icarus (New York, N.Y. 1962) (15.11.2019)
Published in Icarus (New York, N.Y. 1962) (15.11.2019)
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