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Published in Mathematics (Basel) (01.07.2022)
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Chakraborty, C., Sarkar, B., Hsu, C. H., Wen, Z. H., Lin, C. S., Shieh, P. C.
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Chang, H-J, Chou, C-T, Chang, H-T, Liang, W-Z, Hung, T-Y, Li, Y-D, Fang, Y-C, Kuo, C-C, Kuo, D-H, Shieh, P, Jan, C-R
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Pharmacokinetics of 21-desacetyldeflazacort and the safety of deflazacort after oral administration to children and adolescents with Duchenne muscular dystrophy
Wanaski, S, Shieh, P, Kuntz, N, Ciafaloni, E, Butterfield, R, Brantley, S, Grasfeder, L, Dubow, J, Beers, B, Kernbauer, E, Wells, C, Cunniff, T, Griggs, R
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Cheng, H-H, Chou, C-T, Sun, T-K, Liang, W-Z, Cheng, J-S, Chang, H-T, Tseng, H-W, Kuo, C-C, Chen, F-A, Kuo, D-H, Shieh, P, Jan, C-R
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Published in Human & experimental toxicology (01.11.2015)
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Lau, H, Argov, Z, Caraco, Y, Pestronk, A, Shieh, P, Skrinar, A.M, Mayhew, J, Martinisi, J, Kakkis, E
Published in Neuromuscular disorders : NMD (01.10.2014)
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S12 Onasemnogene abeparvovec gene therapy for spinal muscular atrophy type 1: phase 3 study (STR1VE-US)
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Published in Thorax (01.02.2021)
Published in Thorax (01.02.2021)
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S61 Onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): preliminary pulmonary and ventilatory findings from the phase 3 study (STR1VE)
Shell, R, Day, JW, Chiriboga, CA, Crawford, TO, Darras, BT, Finkel, RS, Connolly, AM, Iannaccone, ST, Kuntz, NL, Peña, LDM, Shieh, PB, Smith, EC, Kausar, I, Schultz, M, Feltner, DE, Ogrinc, FG, Macek, TA, Kernbauer, E, L’Italien, J, Sproule, DM, Kaspar, BK, Mendell, JR
Published in Thorax (01.12.2019)
Published in Thorax (01.12.2019)
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P.4.9 Variable clinical and histological features in severe congenital RYR1 associated myopathy
Santi, M, Medne, L, Bharucha-Goebel, D, Bonnemann, C, Dastgir, J, Zukosky, K, Shieh, P, Winder, T, Tennekoon, G, Finkel, R, Dowling, J, Monnier, N
Published in Neuromuscular disorders : NMD (01.10.2013)
Published in Neuromuscular disorders : NMD (01.10.2013)
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Effects of time-varying political connections on loan contracts
Fang, Hao, Wang, Chieh-Hsuan, Joseph CP Shieh, Chien-Ping, Chung
Published in International journal of managerial finance (10.07.2024)
Published in International journal of managerial finance (10.07.2024)
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P.3.1 GNE myopathy functional activity scale (GNEM-FAS): Development of a disease-specific instrument for measuring function and independence
Skrinar, A.M, Argov, Z, Caraco, Y, Kolodny, E, Lau, H, Pestronk, A, Shieh, P, Bronstein, F, Esposito, A, Feinsod-Meiri, Y, Florence, J, Fowler, E, Greenberg, M, Malkus, E, Rebibo, O, Siener, C, Mayhew, J.E
Published in Neuromuscular disorders : NMD (01.10.2013)
Published in Neuromuscular disorders : NMD (01.10.2013)
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P.3.2 Characterization of strength and function in adults with inclusion body myopathy (HIBM)/GNE myopathy
Mayhew, J.E, Skrinar, A.M, Bronstein, F, Esposito, A, Feinsod-Meiri, Y, Florence, J, Fowler, E, Greenberg, M, Malkus, E, Rebibo, O, Siener, C, Caraco, Y, Kolodny, E, Lau, H, Pestronk, A, Shieh, P, Argov, Z
Published in Neuromuscular disorders : NMD (01.10.2013)
Published in Neuromuscular disorders : NMD (01.10.2013)
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