Pharmacologic inhibition of L-tyrosine degradation ameliorates cerebral dopamine deficiency in murine phenylketonuria (PKU)
Harding, Cary O., Winn, Shelley R., Gibson, K. Michael, Arning, Erland, Bottiglieri, Teodoro, Grompe, Markus
Published in Journal of inherited metabolic disease (01.09.2014)
Published in Journal of inherited metabolic disease (01.09.2014)
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Development of a porcine model of phenylketonuria with a humanized R408W mutation for gene editing
Kaiser, Robert A, Carlson, Daniel F, Allen, Kari L, Webster, Dennis A, VanLith, Caitlin J, Nicolas, Clara T, Hillin, Lori G, Yu, Yue, Kaiser, Catherine W, Wahoff, William R, Hickey, Raymond D, Watson, Adrienne L, Winn, Shelley R, Thöny, Beat, Kern, Douglas R, Harding, Cary O, Lillegard, Joseph B
Published in PloS one (25.01.2021)
Published in PloS one (25.01.2021)
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Hepatocytes from wild-type or heterozygous donors are equally effective in achieving successful therapeutic liver repopulation in murine phenylketonuria (PKU)
Hamman, Kelly J., Winn, Shelley R., Harding, Cary O.
Published in Molecular genetics and metabolism (01.11.2011)
Published in Molecular genetics and metabolism (01.11.2011)
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Journal Article
Bone morphogenetic proteins: An update on basic biology and clinical relevance
Schmitt, John M., Hwang, Kun, Winn, Shelley R., Hollinger, Jeffrey O.
Published in Journal of orthopaedic research (01.03.1999)
Published in Journal of orthopaedic research (01.03.1999)
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Journal Article
VEGF Gene Therapy Augments Localized Angiogenesis and Promotes Anastomotic Wound Healing: A Pilot Study in a Clinically Relevant Animal Model
Enestvedt, C. Kristian, Hosack, Luke, Winn, Shelley R., Diggs, Brian S., Uchida, Barry, O’Rourke, Robert W., Jobe, Blair A.
Published in Journal of gastrointestinal surgery (01.10.2008)
Published in Journal of gastrointestinal surgery (01.10.2008)
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Therapeutic liver repopulation by transient acetaminophen selection of gene-modified hepatocytes
Vonada, Anne, Tiyaboonchai, Amita, Nygaard, Sean, Posey, Jeffrey, Peters, Alexander Mack, Winn, Shelley R, Cantore, Alessio, Naldini, Luigi, Harding, Cary O, Grompe, Markus
Published in Science translational medicine (09.06.2021)
Published in Science translational medicine (09.06.2021)
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Modeling the cognitive effects of diet discontinuation in adults with phenylketonuria (PKU) using pegvaliase therapy in PAH-deficient mice
Winn, Shelley R., Dudley, Sandra, Scherer, Tanja, Rimann, Nicole, Thöny, Beat, Boutros, Sydney, Krenik, Destine, Raber, Jacob, Harding, Cary O.
Published in Molecular genetics and metabolism (01.05.2022)
Published in Molecular genetics and metabolism (01.05.2022)
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Journal Article
Protective effect of encapsulated cells producing neurotrophic factor CNTF in a monkey model of Huntington's disease
Emerich, Dwaine F, Winn, Shelley R, Hantraye, Philippe M, Peschanski, Marc, Chen, Er-Yun, Chu, Yaping, McDermott, Patricia, Baetge, E. Edward, Kordower, Jeffrey H
Published in Nature (London) (27.03.1997)
Published in Nature (London) (27.03.1997)
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Journal Article
Blood phenylalanine reduction corrects CNS dopamine and serotonin deficiencies and partially improves behavioral performance in adult phenylketonuric mice
Winn, Shelley R., Scherer, Tanja, Thöny, Beat, Ying, Ming, Martinez, Aurora, Weber, Sydney, Raber, Jacob, Harding, Cary O.
Published in Molecular genetics and metabolism (01.01.2018)
Published in Molecular genetics and metabolism (01.01.2018)
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Journal Article
Biochemical and behavioural profile of NTBC treated Tyrosinemie type 1 mice
van Ginkel, Willem G., Winn, Shelley R., Dudley, Sandra, Krenik, Destine, Perez, Ruby, Rimann, Nicole, Thöny, Beat, Raber, Jacob, Harding, Cary O.
Published in Molecular genetics and metabolism (01.09.2022)
Published in Molecular genetics and metabolism (01.09.2022)
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Tetrahydrobiopterin treatment reduces brain L-Phe but only partially improves serotonin in hyperphenylalaninemic ENU1/2 mice
Scherer, Tanja, Allegri, Gabriella, Sarkissian, Christineh N., Ying, Ming, Grisch-Chan, Hiu Man, Rassi, Anahita, Winn, Shelley R., Harding, Cary O., Martinez, Aurora, Thöny, Beat
Published in Journal of inherited metabolic disease (01.07.2018)
Published in Journal of inherited metabolic disease (01.07.2018)
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Porous polymer scaffolds surface-modified with arginine-glycine-aspartic acid enhance bone cell attachment and differentiation in vitro
Hu, Yunhua, Winn, Shelley R., Krajbich, Ian, Hollinger, Jeffrey O.
Published in Journal of biomedical materials research. Part A (01.03.2003)
Published in Journal of biomedical materials research. Part A (01.03.2003)
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Injection of Chemotherapeutic Microspheres and Glioma IV: Eradicating Tumors in Rats
Emerich, Dwaine F., Winn, Shelley R., Bartus, Raymond T.
Published in Cell transplantation (01.01.2002)
Published in Cell transplantation (01.01.2002)
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Journal Article
Injection of Chemotherapeutic Microspheres and Glioma III: Parameters to Optimize Efficacy
Emerich, Dwaine F., Winn, Shelley R., Bartus, Raymond T.
Published in Cell transplantation (01.01.2002)
Published in Cell transplantation (01.01.2002)
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