Combination of enzyme replacement and hematopoietic stem cell transplantation as therapy for Hurler syndrome
TOLAR, J, GREWAL, S. S, BJORAKER, K. J, WHITLEY, C. B, SHAPIRO, E. G, CHARNAS, L, ORCHARD, P. J
Published in Bone marrow transplantation (Basingstoke) (01.03.2008)
Published in Bone marrow transplantation (Basingstoke) (01.03.2008)
Get full text
Journal Article
Long-term metabolic, endocrine, and neuropsychological outcome of hematopoietic cell transplantation for Wolman disease
TOLAR, J, PETRYK, A, KHAN, K, BJORAKER, K. J, JESSURUN, J, DOLAN, M, KIVISTO, T, CHARNAS, L, SHAPIRO, E. G, ORCHARD, P. J
Published in Bone marrow transplantation (Basingstoke) (01.01.2009)
Published in Bone marrow transplantation (Basingstoke) (01.01.2009)
Get full text
Journal Article
N-acetyl-L-cysteine improves outcome of advanced cerebral adrenoleukodystrophy
TOLAR, J, ORCHARD, P. J, BJORAKER, K. J, ZIEGLER, R. S, SHAPIRO, E. G, CHARNAS, L
Published in Bone marrow transplantation (Basingstoke) (01.02.2007)
Published in Bone marrow transplantation (Basingstoke) (01.02.2007)
Get full text
Journal Article
Hematopoietic Stem-Cell Transplantation in Globoid-Cell Leukodystrophy
Krivit, William, Shapiro, Elsa G, Peters, Charles, Wagner, John E, Cornu, Guy, Kurtzberg, Joanne, Wenger, David A, Kolodny, Edwin H, Vanier, Marie T, Loes, Daniel J, Dusenbery, Kathryn, Lockman, Lawrence A
Published in The New England journal of medicine (16.04.1998)
Published in The New England journal of medicine (16.04.1998)
Get full text
Journal Article
The future for treatment by bone marrow transplantation for adrenoleukodystrophy, metachromatic leukodystrophy, globoid cell leukodystrophy and Hurler syndrome
Krivit, W, Lockman, L A, Watkins, P A, Hirsch, J, Shapiro, E G
Published in Journal of inherited metabolic disease (01.07.1995)
Published in Journal of inherited metabolic disease (01.07.1995)
Get more information
Journal Article
Outcome of Unrelated Donor Bone Marrow Transplantation in 40 Children With Hurler Syndrome
Peters, Charles, Balthazor, Michael, Shapiro, Elsa G., King, Roberta J., Kollman, Craig, Hegland, Janet D., Henslee-Downey, Jean, Trigg, Michael E., Cowan, Morton J., Sanders, Jean, Bunin, Nancy, Weinstein, Howard, Lenarsky, Carl, Falk, Peter, Harris, Richard, Bowen, Tom, Williams, Thomas E., Grayson, Guy H., Warkentin, Phyllis, Sender, Leonard, Cool, Valerie A., Crittenden, Mary, Packman, Seymour, Kaplan, Paige, Lockman, Lawrence A., Anderson, James, Krivit, William, Dusenbery, Kathryn, Wagner, John
Published in Blood (01.06.1996)
Published in Blood (01.06.1996)
Get full text
Journal Article
The nature and impact of neurobehavioral symptoms in neuronopathic Hunter syndrome
Eisengart, J.B., King, K.E., Shapiro, E.G., Whitley, C.B., Muenzer, J.
Published in Molecular genetics and metabolism reports (01.03.2020)
Published in Molecular genetics and metabolism reports (01.03.2020)
Get full text
Journal Article
Outcome of second hematopoietic cell transplantation in Hurler syndrome
GREWAL, S. S, KRIVIT, W, DEFOR, T. E, SHAPIRO, E. G, ORCHARD, P. J, ABEL, S. L, LOCKMAN, L. A, ZIEGLER, R. S, DUSENBERY, K. E, PETERS, C
Published in Bone marrow transplantation (Basingstoke) (01.03.2002)
Published in Bone marrow transplantation (Basingstoke) (01.03.2002)
Get full text
Journal Article