Cas9/sgRNA selective targeting of the P23H Rhodopsin mutant allele for treating retinitis pigmentosa by intravitreal AAV9.PHP.B-based delivery
Giannelli, Serena G, Luoni, Mirko, Castoldi, Valerio, Massimino, Luca, Cabassi, Tommaso, Angeloni, Debora, Demontis, Gian Carlo, Leocani, Letizia, Andreazzoli, Massimiliano, Broccoli, Vania
Published in Human molecular genetics (01.03.2018)
Published in Human molecular genetics (01.03.2018)
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AAV-PHP.B-Mediated Global-Scale Expression in the Mouse Nervous System Enables GBA1 Gene Therapy for Wide Protection from Synucleinopathy
Morabito, Giuseppe, Giannelli, Serena G., Ordazzo, Gabriele, Bido, Simone, Castoldi, Valerio, Indrigo, Marzia, Cabassi, Tommaso, Cattaneo, Stefano, Luoni, Mirko, Cancellieri, Cinzia, Sessa, Alessandro, Bacigaluppi, Marco, Taverna, Stefano, Leocani, Letizia, Lanciego, José L., Broccoli, Vania
Published in Molecular therapy (06.12.2017)
Published in Molecular therapy (06.12.2017)
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Journal Article
Fluid Balance and Recovery of Native Lung Function in Adult Patients Supported by Venovenous Extracorporeal Membrane Oxygenation and Continuous Renal Replacement Therapy
McCanny, Peter, Smith, Myles W, O'Brien, Serena G, Buscher, Hergen, Carton, Edmund G
Published in ASAIO journal (1992) (01.08.2019)
Published in ASAIO journal (1992) (01.08.2019)
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Journal Article
Adult Human Müller Glia Cells Are a Highly Efficient Source of Rod Photoreceptors
Giannelli, Serena G., Demontis, Gian Carlo, Pertile, Grazia, Rama, Paolo, Broccoli, Vania
Published in Stem cells (Dayton, Ohio) (01.02.2011)
Published in Stem cells (Dayton, Ohio) (01.02.2011)
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Rapid Conversion of Fibroblasts into Functional Forebrain GABAergic Interneurons by Direct Genetic Reprogramming
Colasante, Gaia, Lignani, Gabriele, Rubio, Alicia, Medrihan, Lucian, Yekhlef, Latefa, Sessa, Alessandro, Massimino, Luca, Giannelli, Serena G., Sacchetti, Silvio, Caiazzo, Massimiliano, Leo, Damiana, Alexopoulou, Dimitra, Dell’Anno, Maria Teresa, Ciabatti, Ernesto, Orlando, Marta, Studer, Michele, Dahl, Andreas, Gainetdinov, Raul R., Taverna, Stefano, Benfenati, Fabio, Broccoli, Vania
Published in Cell stem cell (03.12.2015)
Published in Cell stem cell (03.12.2015)
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Journal Article
Missing value imputation in high-dimensional phenomic data: imputable or not, and how?
Liao, Serena G, Lin, Yan, Kang, Dongwan D, Chandra, Divay, Bon, Jessica, Kaminski, Naftali, Sciurba, Frank C, Tseng, George C
Published in BMC bioinformatics (05.11.2014)
Published in BMC bioinformatics (05.11.2014)
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Discovery of Novel BRD4 Ligand Scaffolds by Automated Navigation of the Fragment Chemical Space
Piticchio, Serena G, Martínez-Cartró, Míriam, Scaffidi, Salvatore, Rachman, Moira, Rodriguez-Arevalo, Sergio, Sanchez-Arfelis, Ainoa, Escolano, Carmen, Picaud, Sarah, Krojer, Tobias, Filippakopoulos, Panagis, von Delft, Frank, Galdeano, Carles, Barril, Xavier
Published in Journal of medicinal chemistry (23.12.2021)
Published in Journal of medicinal chemistry (23.12.2021)
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Compound heterozygosity for two variants in BMP5 in human skeletal dysostosis with atrioventricular septal defect
Gregersen, Pernille Axél, Hammarsjö, Anna, Graversen, Lise, Brix, Nis, Lindelöf, Hillevi, Jensen, Uffe Birk, Farholt, Stense, Rubak, Sune, Bjerre, Jesper, Piticchio, Serena G., Terkelsen, Thorkild, Nishimura, Gen, Hellfritzsch, Michel Bach, Grigelioniene, Giedre
Published in Clinical genetics (06.09.2024)
Published in Clinical genetics (06.09.2024)
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Crosstalk between microbiome, regulatory T cells and HCA2 orchestrates the inflammatory response in a murine psoriasis model
Schwarz, Agatha, Philippsen, Rebecca, Piticchio, Serena G, Hartmann, Jan N, Häsler, Robert, Rose-John, Stefan, Schwarz, Thomas
Published in Frontiers in immunology (20.02.2023)
Published in Frontiers in immunology (20.02.2023)
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Journal Article
Rapid and efficient CRISPR/Cas9 gene inactivation in human neurons during human pluripotent stem cell differentiation and direct reprogramming
Rubio, Alicia, Luoni, Mirko, Giannelli, Serena G, Radice, Isabella, Iannielli, Angelo, Cancellieri, Cinzia, Di Berardino, Claudia, Regalia, Giulia, Lazzari, Giovanna, Menegon, Andrea, Taverna, Stefano, Broccoli, Vania
Published in Scientific reports (18.11.2016)
Published in Scientific reports (18.11.2016)
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An R package suite for microarray meta-analysis in quality control, differentially expressed gene analysis and pathway enrichment detection
XINGBIN WANG, KANG, Dongwan D, KAMINSKI, Naftali, SIBILLE, Etienne, YAN LIN, JIA LI, TSENG, George C, KUI SHEN, CHI SONG, SHUYA LU, CHANG, Lun-Ching, LIAO, Serena G, ZHIGUANG HUO, SHAOWU TANG, YING DING
Published in Bioinformatics (Oxford, England) (01.10.2012)
Published in Bioinformatics (Oxford, England) (01.10.2012)
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Journal Article
Faculty Perceptions of a Faculty-Led Center for Teaching and Learning
Paynter, Kelly, Stephens, Wendy, Gramling, Serena G.
Published in The journal of faculty development (01.05.2022)
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Published in The journal of faculty development (01.05.2022)
Journal Article
Predictive Models of Genetic Redundancy in Arabidopsis thaliana
Cusack, Siobhan A, Wang, Peipei, Lotreck, Serena G, Moore, Bethany M, Meng, Fanrui, Conner, Jeffrey K, Krysan, Patrick J, Lehti-Shiu, Melissa D, Shiu, Shin-Han
Published in Molecular biology and evolution (01.08.2021)
Published in Molecular biology and evolution (01.08.2021)
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MCT1-dependent energetic failure and neuroinflammation underlie optic nerve degeneration in Wolfram syndrome mice
Rossi, Greta, Ordazzo, Gabriele, Vanni, Niccolò N, Castoldi, Valerio, Iannielli, Angelo, Di Silvestre, Dario, Bellini, Edoardo, Bernardo, Letizia, Giannelli, Serena G, Luoni, Mirko, Muggeo, Sharon, Leocani, Letizia, Mauri, PierLuigi, Broccoli, Vania
Published in eLife (16.01.2023)
Published in eLife (16.01.2023)
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Proinflammatory cytokine interferon‐γ and microbiome‐derived metabolites dictate epigenetic switch between forkhead box protein 3 isoforms in coeliac disease
Serena, G., Yan, S., Camhi, S., Patel, S., Lima, R. S., Sapone, A., Leonard, M. M., Mukherjee, R., Nath, B. J., Lammers, K. M., Fasano, A.
Published in Clinical and experimental immunology (01.03.2017)
Published in Clinical and experimental immunology (01.03.2017)
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