Interacting Resident Epicardium-Derived Fibroblasts and Recruited Bone Marrow Cells Form Myocardial Infarction Scar
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Published in Journal of the American College of Cardiology (19.05.2015)
Published in Journal of the American College of Cardiology (19.05.2015)
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Gene editing of PKLR gene in human hematopoietic progenitors through 5' and 3' UTR modified TALEN mRNA
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Published in PloS one (16.10.2019)
Published in PloS one (16.10.2019)
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IKKβ-Mediated Resistance to Skin Cancer Development Is Ink4a/Arf- Dependent
Page, Angustias, Bravo, Ana, Suarez-Cabrera, Cristian, Alameda, Josefa P, Casanova, M Llanos, Lorz, Corina, Segrelles, Carmen, Segovia, José C, Paramio, Jesús M, Navarro, Manuel, Ramirez, Angel
Published in Molecular cancer research (01.09.2017)
Published in Molecular cancer research (01.09.2017)
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Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
Garcia-Gomez, Maria, Calabria, Andrea, Garcia-Bravo, Maria, Benedicenti, Fabrizio, Kosinski, Penelope, López-Manzaneda, Sergio, Hill, Collin, del Mar Mañu-Pereira, María, Martín, Miguel A, Orman, Israel, Vives-Corrons, Joan-LLuis, Kung, Charles, Schambach, Axel, Jin, Shengfang, Bueren, Juan A, Montini, Eugenio, Navarro, Susana, Segovia, Jose C
Published in Molecular therapy (01.07.2016)
Published in Molecular therapy (01.07.2016)
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Targeted gene therapy and cell reprogramming in Fanconi anemia
Rio, Paula, Baños, Rocio, Lombardo, Angelo, Quintana‐Bustamante, Oscar, Alvarez, Lara, Garate, Zita, Genovese, Pietro, Almarza, Elena, Valeri, Antonio, Díez, Begoña, Navarro, Susana, Torres, Yaima, Trujillo, Juan P, Murillas, Rodolfo, Segovia, Jose C, Samper, Enrique, Surralles, Jordi, Gregory, Philip D, Holmes, Michael C, Naldini, Luigi, Bueren, Juan A
Published in EMBO molecular medicine (01.06.2014)
Published in EMBO molecular medicine (01.06.2014)
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Premature aging and cancer development in transgenic mice lacking functional CYLD
Alameda, Josefa P, Ramírez, Ángel, García-Fernández, Rosa A, Navarro, Manuel, Page, Angustias, Segovia, José C, Sanchez, Rebeca, Suárez-Cabrera, Cristian, Paramio, Jesús M, Bravo, Ana, Fernández-Aceñero, M Jesús, Casanova, M Llanos
Published in Aging (Albany, NY.) (10.01.2019)
Published in Aging (Albany, NY.) (10.01.2019)
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Generation of a High Number of Healthy Erythroid Cells from Gene-Edited Pyruvate Kinase Deficiency Patient-Specific Induced Pluripotent Stem Cells
Garate, Zita, Quintana-Bustamante, Oscar, Crane, Ana M., Olivier, Emmanuel, Poirot, Laurent, Galetto, Roman, Kosinski, Penelope, Hill, Collin, Kung, Charles, Agirre, Xabi, Orman, Israel, Cerrato, Laura, Alberquilla, Omaira, Rodriguez-Fornes, Fatima, Fusaki, Noemi, Garcia-Sanchez, Felix, Maia, Tabita M., Ribeiro, Maria L., Sevilla, Julian, Prosper, Felipe, Jin, Shengfang, Mountford, Joanne, Guenechea, Guillermo, Gouble, Agnes, Bueren, Juan A., Davis, Brian R., Segovia, Jose C.
Published in Stem cell reports (08.12.2015)
Published in Stem cell reports (08.12.2015)
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Cell fusion reprogramming leads to a specific hepatic expression pattern during mouse bone marrow derived hepatocyte formation in vivo
Quintana-Bustamante, Oscar, Grueso, Esther, Garcia-Escudero, Ramon, Arza, Elvira, Alvarez-Barrientos, Alberto, Fabregat, Isabel, Garcia-Bravo, Maria, Meza, Nestor W, Segovia, Jose C
Published in PloS one (23.03.2012)
Published in PloS one (23.03.2012)
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Hematopoietic Dysfunction in a Mouse Model for Fanconi Anemia Group D1
Navarro, Susana, Meza, Nestor W, Quintana-Bustamante, Oscar, Casado, José A, Jacome, Ariana, McAllister, Kimberly, Puerto, Silvia, Surrallés, Jordi, Segovia, José C, Bueren, Juan A
Published in Molecular therapy (01.10.2006)
Published in Molecular therapy (01.10.2006)
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Silencing of hepatic fate-conversion factors induce tumorigenesis in reprogrammed hepatic progenitor-like cells
Serrano, Felipe, García-Bravo, Maria, Blazquez, Marina, Torres, Josema, Castell, Jose V, Segovia, Jose C, Bort, Roque
Published in Stem cell research & therapy (27.07.2016)
Published in Stem cell research & therapy (27.07.2016)
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Hydroxytyrosol Administration Enhances Atherosclerotic Lesion Development in Apo E Deficient Mice
Acín, Sergio, Navarro, María A, Arbonés-Mainar, José M, Guillén, Natalia, Sarría, Alfonso J, Carnicer, Ricardo, Surra, Joaquín C, Orman, Israel, Segovia, Jose C, Torre, Rafael de la, Covas, María-Isabel, Fernández-Bolaños, Juan, Ruiz-Gutiérrez, Valentina, Osada, Jesús
Published in Journal of biochemistry (Tokyo) (01.09.2006)
Published in Journal of biochemistry (Tokyo) (01.09.2006)
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Rescue of Pyruvate Kinase Deficiency in Mice by Gene Therapy Using the Human Isoenzyme
Meza, Nestor W, Alonso-Ferrero, Maria E, Navarro, Susana, Quintana-Bustamante, Oscar, Valeri, Antonio, Garcia-Gomez, Maria, Bueren, Juan A, Bautista, Jose M, Segovia, Jose C
Published in Molecular therapy (01.12.2009)
Published in Molecular therapy (01.12.2009)
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Constitutively active Akt induces ectodermal defects and impaired bone morphogenetic protein signaling
Segrelles, Carmen, Moral, Marta, Lorz, Corina, Santos, Mirentxu, Lu, Jerry, Cascallana, José Luis, Lara, M Fernanda, Carbajal, Steve, Martínez-Cruz, Ana Belén, García-Escudero, Ramón, Beltran, Linda, Segovia, José C, Bravo, Ana, DiGiovanni, John, Paramio, Jesús M
Published in Molecular biology of the cell (01.01.2008)
Published in Molecular biology of the cell (01.01.2008)
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Mitapivat versus Placebo for Pyruvate Kinase Deficiency
Shah, Ami J., Schwartz, Jonathan D., Segovia, Jose C., Al-Samkari, Hanny, Beynon, Vanessa, van Beers, Eduard J.
Published in The New England journal of medicine (30.06.2022)
Published in The New England journal of medicine (30.06.2022)
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Characteristics of Lentiviral Vectors Harboring the Proximal Promoter of the vav Proto-oncogene: A Weak and Efficient Promoter for Gene Therapy
Almarza, Elena, Río, Paula, Meza, Nestor W, Aldea, Montserrat, Agirre, Xabier, Guenechea, Guillermo, Segovia, José C, Bueren, Juan A
Published in Molecular therapy (01.08.2007)
Published in Molecular therapy (01.08.2007)
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Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia
Río, Paula, Navarro, Susana, Wang, Wei, Sánchez-Domínguez, Rebeca, Pujol, Roser M, Segovia, José C, Bogliolo, Massimo, Merino, Eva, Wu, Ning, Salgado, Rocío, Lamana, María L, Yañez, Rosa M, Casado, José A, Giménez, Yari, Román-Rodríguez, Francisco J, Álvarez, Lara, Alberquilla, Omaira, Raimbault, Anna, Guenechea, Guillermo, Lozano, M Luz, Cerrato, Laura, Hernando, Miriam, Gálvez, Eva, Hladun, Raquel, Giralt, Irina, Barquinero, Jordi, Galy, Anne, García de Andoín, Nagore, López, Ricardo, Catalá, Albert, Schwartz, Jonathan D, Surrallés, Jordi, Soulier, Jean, Schmidt, Manfred, Díaz de Heredia, Cristina, Sevilla, Julián, Bueren, Juan A
Published in Nature medicine (01.09.2019)
Published in Nature medicine (01.09.2019)
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A human genome editing–based MLL::AF4 ALL model recapitulates key cellular and molecular leukemogenic features
Bueno, Clara, Torres-Ruiz, Raúl, Velasco-Hernández, Talía, Molina, Oscar, Petazzi, Paolo, Martínez, Alba, Rodriguez, Virginia, Vinyoles, Meritxell, Cantilena, Sandra, Willians, Owen, Vega-García, Nerea, Rodriguez-Perales, Sandra, Segovia, Jose C., Quintana-Bustamante, Oscar, Roy, Anindita, Meyer, Claus, Marschalek, Rolf, Smith, Alastair L., Milne, Thomas A., Fraga, Mario F, Tejedor, Juan Ramón, Menéndez, Pablo
Published in Blood (16.11.2023)
Published in Blood (16.11.2023)
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The Current Status of Mesenchymal Stromal Cells: Controversies, Unresolved Issues and Some Promising Solutions to Improve Their Therapeutic Efficacy
García-Bernal, David, García-Arranz, Mariano, Yáñez, Rosa M, Hervás-Salcedo, Rosario, Cortés, Alfonso, Fernández-García, María, Hernando-Rodríguez, Miriam, Quintana-Bustamante, Óscar, Bueren, Juan A, García-Olmo, Damián, Moraleda, Jose M, Segovia, José C, Zapata, Agustín G
Published in Frontiers in cell and developmental biology (16.03.2021)
Published in Frontiers in cell and developmental biology (16.03.2021)
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