Functional Therapeutic Target Validation Using Pediatric Zebrafish Xenograft Models
Gatzweiler, Charlotte, Ridinger, Johannes, Herter, Sonja, Gerloff, Xenia F, ElHarouni, Dina, Berker, Yannick, Imle, Roland, Schmitt, Lukas, Kreth, Sina, Stainczyk, Sabine, Ayhan, Simay, Najafi, Sara, Krunic, Damir, Frese, Karen, Meder, Benjamin, Reuss, David, Fiesel, Petra, Schramm, Kathrin, Blattner-Johnson, Mirjam, Jones, David T W, Banito, Ana, Westermann, Frank, Oppermann, Sina, Milde, Till, Peterziel, Heike, Witt, Olaf, Oehme, Ina
Published in Cancers (08.02.2022)
Published in Cancers (08.02.2022)
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Author Correction: A MYCN-driven de-differentiation profile identifies a subgroup of aggressive retinoblastoma
Ryl, Tatsiana, Afanasyeva, Elena, Hartmann, Till, Schwermer, Melanie, Schneider, Markus, Schröder, Christopher, Wagemanns, Maren, Bister, Arthur, Kanber, Deniz, Steenpass, Laura, Schramm, Kathrin, Jones, Barbara, Jones, David T. W., Biewald, Eva, Astrahantseff, Kathy, Hanenberg, Helmut, Rahmann, Sven, Lohmann, Dietmar R., Schramm, Alexander, Ketteler, Petra
Published in Communications biology (11.09.2024)
Published in Communications biology (11.09.2024)
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A MYCN-driven de-differentiation profile identifies a subgroup of aggressive retinoblastoma
Ryl, Tatsiana, Afanasyeva, Elena, Hartmann, Till, Schwermer, Melanie, Schneider, Markus, Schröder, Christopher, Wagemanns, Maren, Bister, Arthur, Kanber, Deniz, Steenpass, Laura, Schramm, Kathrin, Jones, Barbara, Jones, David T. W., Biewald, Eva, Astrahantseff, Kathy, Hanenberg, Helmut, Rahmann, Sven, Lohmann, Dietmar R., Schramm, Alexander, Ketteler, Petra
Published in Communications biology (30.07.2024)
Published in Communications biology (30.07.2024)
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Cerebrospinal Fluid Penetration and Combination Therapy of Entrectinib for Disseminated ROS1/NTRK -Fusion Positive Pediatric High-Grade Glioma
Mayr, Lisa, Guntner, Armin S, Madlener, Sibylle, Schmook, Maria T, Peyrl, Andreas, Azizi, Amedeo A, Dieckmann, Karin, Reisinger, Dominik, Stepien, Natalia M, Schramm, Kathrin, Laemmerer, Anna, Jones, David T W, Ecker, Jonas, Sahm, Felix, Milde, Till, Pajtler, Kristian W, Blattner-Johnson, Mirjam, Strbac, Miroslav, Dorfer, Christian, Czech, Thomas, Kirchhofer, Dominik, Gabler, Lisa, Berger, Walter, Haberler, Christine, Müllauer, Leonhard, Buchberger, Wolfgang, Slavc, Irene, Lötsch-Gojo, Daniela, Gojo, Johannes
Published in Journal of personalized medicine (18.12.2020)
Published in Journal of personalized medicine (18.12.2020)
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Somatic CRISPR/Cas9-mediated tumour suppressor disruption enables versatile brain tumour modelling
Zuckermann, Marc, Hovestadt, Volker, Knobbe-Thomsen, Christiane B, Zapatka, Marc, Northcott, Paul A, Schramm, Kathrin, Belic, Jelena, Jones, David T W, Tschida, Barbara, Moriarity, Branden, Largaespada, David, Roussel, Martine F, Korshunov, Andrey, Reifenberger, Guido, Pfister, Stefan M, Lichter, Peter, Kawauchi, Daisuke, Gronych, Jan
Published in Nature communications (11.06.2015)
Published in Nature communications (11.06.2015)
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Multiomics analysis of pediatric solid tumors within the INFORM precision oncology study: From functional drug profiling to biomarker identification
ElHarouni, Dina, Peterziel, Heike, Schramm, Kathrin, Milde, Till, Oppermann, Sina, Oehme, Ina, Witt, Olaf, Schlesner, Matthias, Jäger, Natalie
Published in Journal of clinical oncology (01.06.2022)
Published in Journal of clinical oncology (01.06.2022)
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The Pediatric Precision Oncology INFORM Registry: Clinical Outcome and Benefit for Patients with Very High-Evidence Targets
van Tilburg, Cornelis M, Pfaff, Elke, Pajtler, Kristian W, Langenberg, Karin P S, Fiesel, Petra, Jones, Barbara C, Balasubramanian, Gnana Prakash, Stark, Sebastian, Johann, Pascal D, Blattner-Johnson, Mirjam, Schramm, Kathrin, Dikow, Nicola, Hirsch, Steffen, Sutter, Christian, Grund, Kerstin, von Stackelberg, Arend, Kulozik, Andreas E, Lissat, Andrej, Borkhardt, Arndt, Meisel, Roland, Reinhardt, Dirk, Klusmann, Jan-Henning, Fleischhack, Gudrun, Tippelt, Stephan, von Schweinitz, Dietrich, Schmid, Irene, Kramm, Christof M, von Bueren, André O, Calaminus, Gabriele, Vorwerk, Peter, Graf, Norbert, Westermann, Frank, Fischer, Matthias, Eggert, Angelika, Burkhardt, Birgit, Wößmann, Wilhelm, Nathrath, Michaela, Hecker-Nolting, Stefanie, Frühwald, Michael C, Schneider, Dominik T, Brecht, Ines B, Ketteler, Petra, Fulda, Simone, Koscielniak, Ewa, Meister, Michael T, Scheer, Monika, Hettmer, Simone, Schwab, Matthias, Tremmel, Roman, Øra, Ingrid, Hutter, Caroline, Gerber, Nicolas U, Lohi, Olli, Kazanowska, Bernarda, Kattamis, Antonis, Filippidou, Maria, Goemans, Bianca, Zwaan, C Michel, Milde, Till, Jäger, Natalie, Wolf, Stephan, Reuss, David, Sahm, Felix, von Deimling, Andreas, Dirksen, Uta, Freitag, Angelika, Witt, Ruth, Lichter, Peter, Kopp-Schneider, Annette, Jones, David T W, Molenaar, Jan J, Capper, David, Pfister, Stefan M, Witt, Olaf
Published in Cancer discovery (01.11.2021)
Published in Cancer discovery (01.11.2021)
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Feasibility and antitumour activity of the FGFR inhibitor erdafitnib in three paediatric CNS tumour patients
Stepien, Natalia, Mayr, Lisa, Schmook, Maria T., Raimann, Adalbert, Dorfer, Christian, Peyrl, Andreas, Azizi, Amedeo A., Schramm, Kathrin, Haberler, Christine, Gojo, Johannes
Published in Pediatric blood & cancer (01.03.2024)
Published in Pediatric blood & cancer (01.03.2024)
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Recurrent MET fusion genes represent a drug target in pediatric glioblastoma
Bender, Sebastian, Gronych, Jan, Warnatz, Hans-Jorg, Hutter, Barbara, Grobner, Susanne, Ryzhova, Marina, Pfaff, Elke, Hovestadt, Volker, Weinberg, Florian, Halbach, Sebastian, Kool, Marcel, Northcott, Paul A, Sturm, Dominik, Bjerke, Lynn, Zichner, Thomas, Stuetz, Adrian M, Schramm, Kathrin, Huang, Bingding, Buchhalter, Ivo, Heinold, Michael, Risch, Thomas, Worst, Barbara C, van Tilburg, Cornelis M, Weber, Ursula D, Zapatka, Marc, Raeder, Benjamin, Milford, David, Heiland, Sabine, von Kalle, Christof, Previti, Christopher, Lawerenz, Chris, Kulozik, Andreas E, Unterberg, Andreas, Witt, Olaf, von Deimling, Andreas, Capper, David, Truffaux, Nathalene, Grill, Jacques, Jabado, Nada, Sehested, Astrid M, Sumerauer, David, Brahim, Dorra Hmida-Ben, Trabelsi, Saoussen, Ng, Ho-Keung, Zagzag, David, Allen, Jeffrey C, Karajannis, Matthias A, Gottardo, Nicholas G, Jones, Chris, Korbel, Jan O, et. al
Published in Nature medicine (01.11.2016)
Published in Nature medicine (01.11.2016)
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Genomic ALK alterations in primary and relapsed neuroblastoma
Rosswog, Carolina, Fassunke, Jana, Ernst, Angela, Schömig-Markiefka, Birgid, Merkelbach-Bruse, Sabine, Bartenhagen, Christoph, Cartolano, Maria, Ackermann, Sandra, Theissen, Jessica, Blattner-Johnson, Mirjam, Jones, Barbara, Schramm, Kathrin, Altmüller, Janine, Nürnberg, Peter, Ortmann, Monika, Berthold, Frank, Peifer, Martin, Büttner, Reinhard, Westermann, Frank, Schulte, Johannes H, Simon, Thorsten, Hero, Barbara, Fischer, Matthias
Published in British journal of cancer (12.04.2023)
Published in British journal of cancer (12.04.2023)
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Nuclear Calcium Buffering Capacity Shapes Neuronal Architecture
Mauceri, Daniela, Hagenston, Anna M., Schramm, Kathrin, Weiss, Ursula, Bading, Hilmar
Published in The Journal of biological chemistry (18.09.2015)
Published in The Journal of biological chemistry (18.09.2015)
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DECIPHER pooled shRNA library screen identifies PP2A and FGFR signaling as potential therapeutic targets for diffuse intrinsic pontine gliomas
Schramm, Kathrin, Iskar, Murat, Statz, Britta, Jäger, Natalie, Haag, Daniel, Słabicki, Mikołaj, Pfister, Stefan M, Zapatka, Marc, Gronych, Jan, Jones, David T W, Lichter, Peter
Published in Neuro-oncology (Charlottesville, Va.) (11.07.2019)
Published in Neuro-oncology (Charlottesville, Va.) (11.07.2019)
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HGG-21. DISTRIBUTION AND MUTATIONAL PATTERNS OF TP53 ALTERATIONS ACROSS SUBTYPES OF PEDIATRIC HIGH-GRADE GLIOMAS
Blattner-Johnson, Mirjam, Sturm, Dominik, Hirsch, Steffen, Jones, Barbara, Schramm, Kathrin, Balasubramanian, Gnana Prakash, Sill, Martin, Autry, Robert, Previti, Christopher, van Tilburg, Cornelis M, Milde, Till, Pajtler, Kristian W, Sahm, Felix, Kramm, Christof M, Witt, Olaf, Pfister, Stefan M, Jones, David T W
Published in Neuro-oncology (Charlottesville, Va.) (18.06.2024)
Published in Neuro-oncology (Charlottesville, Va.) (18.06.2024)
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MDB-26. GENE REGULATORY NETWORK LANDSCAPE OF GROUP 3/4 MEDULLOBLASTOMA
Joshi, Piyush, Stelzer, Tamina, Okonechnikov, Konstantin, Sarropoulos, Ioannis, Sepp, Mari, Pour-Jamnani, Mischan V, Rademacher, Anne, Yamada-Saito, Tetsuya, Schneider, Céline, Schmidt, Julia, Schäfer, Philipp, Leiss, Kevin, Bortolomeazzi, Michele, Mallm, Jan-Philipp, da Silva, Patricia B G, Statz, Britta, Wittmann, Andrea, Schramm, Kathrin, Blattner-Johnson, Mirjam, Fiesel, Petra, Jones, Barbara, Milde, Till, Pajtler, Kristian, van Tilburg, Cornelis M, Witt, Olaf, Rippe, Karsten, Korshunov, Andrey, Jones, David T W, Hovestadt, Volker, Northcott, Paul A, Thongjuea, Supat, Jäger, Natalie, Kaessmann, Henrik, Pfister, Stefan M, Kutscher, Lena M
Published in Neuro-oncology (Charlottesville, Va.) (18.06.2024)
Published in Neuro-oncology (Charlottesville, Va.) (18.06.2024)
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HGG-61.Landscape of cancer predisposition in pediatric high-grade glioma
Blattner-Johnson, Mirjam, Sturm, Dominik, Sievers, Philipp, Jones, Barbara, Schramm, Kathrin, Balasubramanian, Gnana Prakash, Sill, Martin, Jäger, Natalie, van Tilburg, Cornelis M, Milde, Till, Pajtler, Kristian W, Dikow, Nicola, Hirsch, Steffen, Sutter, Christian, Sahm, Felix, Witt, Olaf, Pfister, Stefan M, Jones, David T W
Published in Neuro-oncology (Charlottesville, Va.) (03.06.2022)
Published in Neuro-oncology (Charlottesville, Va.) (03.06.2022)
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Amplification of the PLAG-family genes—PLAGL1 and PLAGL2—is a key feature of the novel tumor type CNS embryonal tumor with PLAGL amplification
Keck, Michaela-Kristina, Sill, Martin, Wittmann, Andrea, Joshi, Piyush, Stichel, Damian, Beck, Pengbo, Okonechnikow, Konstantin, Sievers, Philipp, Wefers, Annika K., Roncaroli, Federico, Avula, Shivaram, McCabe, Martin G., Hayden, James T., Wesseling, Pieter, Øra, Ingrid, Nistér, Monica, Kranendonk, Mariëtte E. G., Tops, Bastiaan B. J., Zapotocky, Michal, Zamecnik, Josef, Vasiljevic, Alexandre, Fenouil, Tanguy, Meyronet, David, von Hoff, Katja, Schüller, Ulrich, Loiseau, Hugues, Figarella-Branger, Dominique, Kramm, Christof M., Sturm, Dominik, Scheie, David, Rauramaa, Tuomas, Pesola, Jouni, Gojo, Johannes, Haberler, Christine, Brandner, Sebastian, Jacques, Tom, Sexton Oates, Alexandra, Saffery, Richard, Koscielniak, Ewa, Baker, Suzanne J., Yip, Stephen, Snuderl, Matija, Ud Din, Nasir, Samuel, David, Schramm, Kathrin, Blattner-Johnson, Mirjam, Selt, Florian, Ecker, Jonas, Milde, Till, von Deimling, Andreas, Korshunov, Andrey, Perry, Arie, Pfister, Stefan M., Sahm, Felix, Solomon, David A., Jones, David T. W.
Published in Acta neuropathologica (01.01.2023)
Published in Acta neuropathologica (01.01.2023)
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MODL-11. COMPARISON OF HUMAN & MURINE PA/PXA CHARACTERISTICS
Sommerkamp, Alexander C, Sun, Pengbo, Wefers, Annika K, Ismer, Britta, Schramm, Kathrin, Wittmann, Andrea, Gronych, Jan, Korshunov, Andrey, von Deimling, Andreas, Jäger, Natalie, Pfister, Stefan M, Jones, David T W
Published in Neuro-oncology (Charlottesville, Va.) (04.12.2020)
Published in Neuro-oncology (Charlottesville, Va.) (04.12.2020)
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OTHR-04. DEVELOPMENT OF A FUNCTIONAL PLATFORM FOR REAL-TIME PERSONALIZED DRUG SENSITIVITY PROFILING OF PATIENT-DERIVED 3D FRESH TUMOR TISSUE CULTURES IN THE PEDIATRIC PRECISION ONCOLOGY PROGRAM INFORM
Peterziel, Heike, Jamaladdin, Nora, ElHarouni, Dina, Gerloff, Xenia F, Herter, Sonja, Fiesel, Petra, Berker, Yannick, Blattner-Johnson, Mirjam, Schramm, Kathrin, Jones, Barbara C, Reuss, David, Turunen, Laura, Friedenauer, Aileen, Holland-Letz, Tim, Sill, Martin, Weiser, Lena, Previti, Christopher, Balasubramanian, Gnanaprakash, Gerber, Nicolas U, Gojo, Johannes, Hutter, Caroline, Øra, Ingrid, Lohi, Olli, Kattamis, Antonis, de Wilde, Bram, Westermann, Frank, Tippelt, Stephan, Graf, Norbert, Nathrath, Michaela, Sparber-Sauer, Monika, Sehested, Astrid, Kramm, Christof M, Dirksen, Uta, Kallioniemi, Olli, Pfister, Stefan M, van Tilburg, Cornelis M, Jones, David T W, Saarela, Jani, Pietiäinen, Vilja, Jäger, Natalie, Schlesner, Matthias, Kopp-Schneider, Annette, Oppermann, Sina, Milde, Till, Witt, Olaf, Oehme, Ina
Published in Neuro-oncology (Charlottesville, Va.) (12.06.2023)
Published in Neuro-oncology (Charlottesville, Va.) (12.06.2023)
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The pediatric precision oncology study INFORM: Clinical outcome and benefit for molecular subgroups
van Tilburg, Cornelis Martinus, Pfaff, Elke, Pajtler, Kristian W., Langenberg, Karin P.S., Fiesel, Petra, Jones, Barbara C., Balasubramanian, Gnana Prakash, Stark, Sebastian, Johann, Pascal D., Blattner-Johnson, Mirjam, Schramm, Kathrin, Jäger, Natalie, von Deimling, Andreas, Dirksen, Uta, Freitag, Angelika, Witt, Ruth, Lichter, Peter, Jones, David T.W., Pfister, Stefan M., Witt, Olaf
Published in Journal of clinical oncology (20.06.2020)
Published in Journal of clinical oncology (20.06.2020)
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