Increased dystrophin production with golodirsen in patients with Duchenne muscular dystrophy
Frank, Diane E, Schnell, Frederick J, Akana, Cody, El-Husayni, Saleh H, Desjardins, Cody A, Morgan, Jennifer, Charleston, Jay S, Sardone, Valentina, Domingos, Joana, Dickson, George, Straub, Volker, Guglieri, Michela, Mercuri, Eugenio, Servais, Laurent, Muntoni, Francesco
Published in Neurology (26.05.2020)
Published in Neurology (26.05.2020)
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Eteplirsen treatment for Duchenne muscular dystrophy: Exon skipping and dystrophin production
Charleston, Jay S, Schnell, Frederick J, Dworzak, Johannes, Donoghue, Cas, Lewis, Sarah, Chen, Lei, Young, G David, Milici, Anthony J, Voss, Jon, DeAlwis, Uditha, Wentworth, Bruce, Rodino-Klapac, Louise R, Sahenk, Zarife, Frank, Diane, Mendell, Jerry R
Published in Neurology (12.06.2018)
Published in Neurology (12.06.2018)
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Functional muscle recovery following dystrophin and myostatin exon splice modulation in aged mdx mice
Lu-Nguyen, Ngoc, Ferry, Arnaud, Schnell, Frederick J, Hanson, Gunnar J, Popplewell, Linda, Dickson, George, Malerba, Alberto
Published in Human molecular genetics (15.09.2019)
Published in Human molecular genetics (15.09.2019)
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Journal Article
Long-term treatment with eteplirsen in nonambulatory patients with Duchenne muscular dystrophy
Alfano, Lindsay N, Charleston, Jay S, Connolly, Anne M, Cripe, Linda, Donoghue, Cas, Dracker, Robert, Dworzak, Johannes, Eliopoulos, Helen, Frank, Diane E, Lewis, Sarah, Lucas, Karin, Lynch, Jessie, Milici, A J, Flynt, Amy, Naughton, Emily, Rodino-Klapac, Louise R, Sahenk, Zarife, Schnell, Frederick J, Young, G David, Mendell, Jerry R, Lowes, Linda P
Published in Medicine (Baltimore) (01.06.2019)
Published in Medicine (Baltimore) (01.06.2019)
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Randomized, Double-Blind, Phase III Trial of Enzastaurin Versus Placebo in Patients Achieving Remission After First-Line Therapy for High-Risk Diffuse Large B-Cell Lymphoma
Crump, Michael, Leppä, Sirpa, Fayad, Luis, Lee, Je Jung, Di Rocco, Alice, Ogura, Michinori, Hagberg, Hans, Schnell, Frederick, Rifkin, Robert, Mackensen, Andreas, Offner, Fritz, Pinter-Brown, Lauren, Smith, Sonali, Tobinai, Kensei, Yeh, Su-Peng, Hsi, Eric D, Nguyen, Tuan, Shi, Peipei, Hahka-Kemppinen, Marjo, Thornton, Don, Lin, Boris, Kahl, Brad, Schmitz, Norbert, Savage, Kerry J, Habermann, Thomas
Published in Journal of clinical oncology (20.07.2016)
Published in Journal of clinical oncology (20.07.2016)
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Utility of PET-CT to evaluate retroperitoneal lymph node metastasis in advanced cervical cancer: Results of ACRIN6671/GOG0233 trial
Atri, Mostafa, Zhang, Zheng, Dehdashti, Farrokh, Lee, Susanna I, Ali, Shamshad, Marques, Helga, Koh, Wui-Jin, Moore, Kathleen, Landrum, Lisa, Kim, Jae Weon, DiSilvestro, Paul, Eisenhauer, Eric, Schnell, Frederick, Gold, Michael
Published in Gynecologic oncology (01.09.2016)
Published in Gynecologic oncology (01.09.2016)
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Gene-Silencing Antisense Oligomers Inhibit Acinetobacter Growth In Vitro and In Vivo
Geller, Bruce L., Marshall-Batty, Kimberly, Schnell, Frederick J., McKnight, Mattie M., Iversen, Patrick L., Greenberg, David E.
Published in The Journal of infectious diseases (15.11.2013)
Published in The Journal of infectious diseases (15.11.2013)
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Splice modulating antisense oligonucleotides restore some acid-alpha-glucosidase activity in cells derived from patients with late-onset Pompe disease
Aung-Htut, May Thandar, Ham, Kristin A, Tchan, Michel, Johnsen, Russell, Schnell, Frederick J, Fletcher, Sue, Wilton, Steve D
Published in Scientific reports (21.04.2020)
Published in Scientific reports (21.04.2020)
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Systemic PPMO-mediated dystrophin expression in the Dup2 mouse model of Duchenne muscular dystrophy
Gushchina, Liubov V., Vetter, Tatyana A., Frair, Emma C., Bradley, Adrienne J., Grounds, Kelly M., Lay, Jacob W., Huang, Nianyuan, Suhaiba, Aisha, Schnell, Frederick J., Hanson, Gunnar, Simmons, Tabatha R., Wein, Nicolas, Flanigan, Kevin M.
Published in Molecular therapy. Nucleic acids (13.12.2022)
Published in Molecular therapy. Nucleic acids (13.12.2022)
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Lymphocytic choriomeningitis virus infection in FVB mouse produces hemorrhagic disease
Schnell, Frederick J, Sundholm, Sarah, Crumley, Stacy, Iversen, Patrick L, Mourich, Dan V
Published in PLoS pathogens (01.12.2012)
Published in PLoS pathogens (01.12.2012)
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Palifermin Reduces the Incidence of Oral Mucositis in Patients With Metastatic Colorectal Cancer Treated With Fluorouracil-Based Chemotherapy
ROSEN, Lee S, ABDI, Ehtesham, DAVIS, Ian D, GUTHEIL, John, SCHNELL, Frederick M, ZALCBERG, John, CESANO, Alessandra, GAYKO, Urte, CHEN, Mon-Gy, CLARKE, Stephen
Published in Journal of clinical oncology (20.11.2006)
Published in Journal of clinical oncology (20.11.2006)
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Journal Article
Junction Adhesion Molecule Is a Receptor for Reovirus
Barton, Erik S, Forrest, J.Craig, Connolly, Jodi L, Chappell, James D, Liu, Yuan, Schnell, Frederick J, Nusrat, Asma, Parkos, Charles A, Dermody, Terence S
Published in Cell (09.02.2001)
Published in Cell (09.02.2001)
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An IL-7-Dependent Rebound in Thymic T Cell Output Contributes to the Bone Loss Induced by Estrogen Deficiency
Michaela Robbie Ryan, Rebecca Shepherd, Jennifer K. Leavey, Gao, Yuhao, Francesco Grassi, Frederick J. Schnell, Qian, Wei-Ping, Gilbert J. Kersh, Weitzmann, M. Neale, Pacifici, Roberto
Published in Proceedings of the National Academy of Sciences - PNAS (15.11.2005)
Published in Proceedings of the National Academy of Sciences - PNAS (15.11.2005)
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Signal Regulatory Protein (SIRPα), a Cellular Ligand for CD47, Regulates Neutrophil Transmigration
Liu, Yuan, Bühring, Hans-Jörg, Zen, Ke, Burst, Stephanie L., Schnell, Frederick J., Williams, Ifor R., Parkos, Charles A.
Published in The Journal of biological chemistry (22.03.2002)
Published in The Journal of biological chemistry (22.03.2002)
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"Of Mice and Measures": A Project to Improve How We Advance Duchenne Muscular Dystrophy Therapies to the Clinic
Gordish-Dressman, Heather, Willmann, Raffaella, Dalle Pazze, Laura, Kreibich, Arati, van Putten, Maaike, Heydemann, Ahlke, Bogdanik, Laurent, Lutz, Cathleen, Davies, Kay, Demonbreun, Alexis R, Duan, Dongsheng, Elsey, David, Fukada, So-Ichiro, Girgenrath, Mahasweta, Patrick Gonzalez, J, Grounds, Miranda D, Nichols, Andy, Partridge, Terry, Passini, Marco, Sanarica, Francesca, Schnell, Frederick J, Wells, Dominic J, Yokota, Toshifumi, Young, Courtney S, Zhong, Zhong, Spurney, Christopher, Spencer, Melissa, De Luca, Annamaria, Nagaraju, Kanneboyina, Aartsma-Rus, Annemieke
Published in Journal of neuromuscular diseases (2018)
Published in Journal of neuromuscular diseases (2018)
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Alternative Splice Forms of CTLA-4 Induced by Antisense Mediated Splice-Switching Influences Autoimmune Diabetes Susceptibility in NOD Mice
Mourich, Dan V., Oda, Shannon K., Schnell, Frederick J., Crumley, Stacy L., Hauck, Laura L., Moentenich, Carla A., Marshall, Nikki B., Hinrichs, Dave J., Iversen, Patrick L.
Published in Nucleic acid therapeutics (01.04.2014)
Published in Nucleic acid therapeutics (01.04.2014)
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