Tominersen in Adults with Manifest Huntington's Disease
McColgan, Peter, Thobhani, Alpa, Boak, Lauren, Schobel, Scott A, Nicotra, Alessia, Palermo, Giuseppe, Trundell, Dylan, Zhou, Julian, Schlegel, Valerie, Sanwald Ducray, Patricia, Hawellek, David J, Dorn, Jonas, Simillion, Cedric, Lindemann, Michael, Wheelock, Vicki, Durr, Alexandra, Anderson, Karen E, Long, Jeffrey D, Wild, Edward J, Landwehrmeyer, G Bernhard, Leavitt, Blair R, Tabrizi, Sarah J, Doody, Rachelle
Published in The New England journal of medicine (07.12.2023)
Published in The New England journal of medicine (07.12.2023)
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Journal Article
Development of a population pharmacokinetic model to characterize the pharmacokinetics of intrathecally administered tominersen in cerebrospinal fluid and plasma
Yamamoto, Yumi, Sanwald Ducray, Patricia, Björnsson, Marcus, Smart, Kevin, Grimsey, Paul, Vatakuti, Suresh, Portron, Agnes, Massonnet, Benoit, Norris, Daniel A, Silber Baumann, Hanna E
Published in CPT: pharmacometrics and systems pharmacology (01.09.2023)
Published in CPT: pharmacometrics and systems pharmacology (01.09.2023)
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Journal Article
Mathematical Disease Progression Modeling in Type 2/3 Spinal Muscular Atrophy
Jacqmin, Philippe, Gieschke, Ronald, Delor, Isabelle, Snoeck, Eric, Vianna, Eduardo, Vuillerot, Carole, Sanwald Ducray, Patricia
Published in Muscle & nerve (01.10.2018)
Published in Muscle & nerve (01.10.2018)
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Journal Article
J02 Quantitative analyses of pooled tominersen clinical data to support dose selection (rationale) for the new phase II study
Yamamoto, Yumi, Zhou, Julian, Grimsey, Paul, McColgan, Peter, Ducray, Patricia Sanwald
Published in Journal of neurology, neurosurgery and psychiatry (12.09.2022)
Published in Journal of neurology, neurosurgery and psychiatry (12.09.2022)
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Journal Article
NfL concentration in CSF is a quantitative marker of the rate of neurodegeneration in aging and Huntington's disease: a semi-mechanistic model-based analysis
Machacek, Matthias, Garcia-Montoya, Elena, McColgan, Peter, Sanwald-Ducray, Patricia, Mazer, Norman Alan
Published in Frontiers in neuroscience (03.07.2024)
Published in Frontiers in neuroscience (03.07.2024)
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Journal Article
Equivalent Pharmacokinetics of Mycophenolate Mofetil in African‐American and Caucasian Male and Female Stable Renal Allograft Recipients
Pescovitz, Mark D., Guasch, Antonio, Gaston, Robert, Rajagopalan, P., Tomlanovich, Stephen, Weinstein, Samuel, Bumgardner, Ginny L., Melton, Larry, Ducray, Patricia Sanwald, Banken, Ludger, Hall, Joanna, Boutouyrie, Bruno X.
Published in American journal of transplantation (01.12.2003)
Published in American journal of transplantation (01.12.2003)
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Journal Article
Inhibition of gastrointestinal lipolysis by Orlistat during digestion of test meals in healthy volunteers
Carrière, F, Renou, C, Ransac, S, Lopez, V, De Caro, J, Ferrato, F, De Caro, A, Fleury, A, Sanwald-Ducray, P, Lengsfeld, H, Beglinger, C, Hadvary, P, Verger, R, Laugier, R
Published in American journal of physiology: Gastrointestinal and liver physiology (01.07.2001)
Published in American journal of physiology: Gastrointestinal and liver physiology (01.07.2001)
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Journal Article
Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial
Bertini, Enrico, Prof, Dessaud, Eric, PhD, Mercuri, Eugenio, Prof, Muntoni, Francesco, Prof, Kirschner, Janbernd, Prof, Reid, Carol, PhD, Lusakowska, Anna, MD, Comi, Giacomo P, Prof, Cuisset, Jean-Marie, MD, Abitbol, Jean-Louis, MD, Scherrer, Bruno, PhD, Ducray, Patricia Sanwald, PhD, Buchbjerg, Jeppe, MSc, Vianna, Eduardo, PhD, van der Pol, W Ludo, MD, Vuillerot, Carole, MD, Blaettler, Thomas, MD, Fontoura, Paulo, MD
Published in Lancet neurology (01.07.2017)
Published in Lancet neurology (01.07.2017)
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Journal Article
J02 A global development program testing RG6042, an anti-sense oligonucleotide, for the treatment of early manifest huntington’s disease (hd)
Schobel, Scott, Palermo, Giuseppe, Trundell, Dylan, Kremer, Thomas, Sanwald-Ducray, Patricia, Smith, Anne, Boak, Lauren, Doody, Rachelle
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2018)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2018)
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Journal Article
Simulating the Impact of Elevated Levels of Interleukin-6 on the Pharmacokinetics of Various CYP450 Substrates in Patients with Neuromyelitis Optica or Neuromyelitis Optica Spectrum Disorders in Different Ethnic Populations
Machavaram, Krishna K., Endo-Tsukude, Chihiro, Terao, Kimio, Gill, Katherine L., Hatley, Oliver J., Gardner, Iain, Parrott, Neil, Ducray, Patricia Sanwald
Published in The AAPS journal (01.05.2019)
Published in The AAPS journal (01.05.2019)
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Journal Article
NEW TREATMENT OF SMA
MCCARTHY, Kathleen Dorothy, SANWALD DUCRAY, Patricia, SCHAEDELI STARK, Franziska, BLAETTLER, Thomas
Year of Publication 10.04.2019
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Year of Publication 10.04.2019
Patent
Inhibition of gastrointestinal lipolysis by Orlistat during digestion of test meals in healthy volunteers
CARRIERE, Frederic, RENOU, Christophe, BEGLINGER, Christoph, HADVARY, Paul, VERGER, Robert, LAUGIER, René, RANSAC, Stéphane, LOPEZ, Veronique, DE CARO, Josiane, FERRATO, Francine, DE CARO, Alain, FLEURY, André, SANWALD-DUCRAY, Patricia, LENGSFELD, Hans
Published in American journal of physiology: Gastrointestinal and liver physiology (01.07.2001)
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Published in American journal of physiology: Gastrointestinal and liver physiology (01.07.2001)
Journal Article
NEW TREATMENT OF SMA
MCCARTHY, Kathleen Dorothy, SANWALD DUCRAY, Patricia, SCHAEDELI STARK, Franziska, BLAETTLER, Thomas
Year of Publication 07.12.2017
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Year of Publication 07.12.2017
Patent
NEW TREATMENT OF SMA
BLAETTLER THOMAS, SANWALD DUCRAY PATRICIA, SCHAEDELI STARK FRANZISKA, MCCARTHY KATHLEEN DOROTHY
Year of Publication 04.01.2019
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Year of Publication 04.01.2019
Patent
MÉTODO PARA EL TRATAMIENTO DE LA AME Y COMPOSICIÓN FARMACÉUTICA
SCHAEDELI STARK, FRANZISKA, SANWALD DUCRAY, PATRICIA, BLAETTLER, THOMAS, MCARTHY, KATHLEEN DOROTHY
Year of Publication 12.12.2018
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Year of Publication 12.12.2018
Patent