Delivery of MDR1 Small Interfering RNA by Self-Complementary Recombinant Adeno-Associated Virus Vector
Xu, Dong, McCarty, Doug, Fernandes, Alda, Fisher, Michael, Samulski, R J, Juliano, R L
Published in Molecular therapy (01.04.2005)
Published in Molecular therapy (01.04.2005)
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Neutralizing antibodies against adeno-associated virus examined prospectively in pediatric patients with hemophilia
Li, C, Narkbunnam, N, Samulski, R J, Asokan, A, Hu, G, Jacobson, L J, Manco-Johnson, M J, Monahan, P E
Published in Gene therapy (01.03.2012)
Published in Gene therapy (01.03.2012)
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Robust spinal motor neuron transduction following intrathecal delivery of AAV9 in pigs
Federici, T, Taub, J S, Baum, G R, Gray, S J, Grieger, J C, Matthews, K A, Handy, C R, Passini, M A, Samulski, R J, Boulis, N M
Published in Gene therapy (01.08.2012)
Published in Gene therapy (01.08.2012)
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Prediction of adeno-associated virus neutralizing antibody activity for clinical application
Wang, M, Crosby, A, Hastie, E, Samulski, J J, McPhee, S, Joshua, G, Samulski, R J, Li, C
Published in Gene therapy (01.12.2015)
Published in Gene therapy (01.12.2015)
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scAAVIL-1ra dosing trial in a large animal model and validation of long-term expression with repeat administration for osteoarthritis therapy
Goodrich, L R, Grieger, J C, Phillips, J N, Khan, N, Gray, S J, McIlwraith, C W, Samulski, R J
Published in Gene therapy (01.07.2015)
Published in Gene therapy (01.07.2015)
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Preclinical safety evaluation of subretinal AAV2.sFlt-1 in non-human primates
Lai, C-M, Estcourt, M J, Himbeck, R P, Lee, S-Y, Yew-San Yeo, I, Luu, C, Loh, B K, Lee, M W, Barathi, A, Villano, J, Ang, C-L, van der Most, R G, Constable, I J, Dismuke, D, Samulski, R J, Degli-Esposti, M A, Rakoczy, E P
Published in Gene therapy (01.10.2012)
Published in Gene therapy (01.10.2012)
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Efficient transduction of vascular smooth muscle cells with a translational AAV2.5 vector: a new perspective for in-stent restenosis gene therapy
Lompré, A-M, Hadri, L, Merlet, E, Keuylian, Z, Mougenot, N, Karakikes, I, Chen, J, Atassi, F, Marchand, A, Blaise, R, Limon, I, McPhee, S W J, Samulski, R J, Hajjar, R J, Lipskaia, L
Published in Gene therapy (01.09.2013)
Published in Gene therapy (01.09.2013)
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Embryonic substantia nigra grafts in the mesencephalon send neurites to the host striatum in non-human primate after overexpression of GDNF
Redmond Jr, D.E., Elsworth, J.D., Roth, R.H., Leranth, C., Collier, T.J., Blanchard, B., Bjugstad, K.B., Samulski, R.J., Aebischer, P., Sladek Jr, J.R.
Published in Journal of comparative neurology (1911) (01.07.2009)
Published in Journal of comparative neurology (1911) (01.07.2009)
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A small regulatory element from chromosome 19 enhances liver-specific gene expression
Li, C, Hirsch, M, Carter, P, Asokan, A, Zhou, X, Wu, Z, Samulski, R J
Published in Gene therapy (01.01.2009)
Published in Gene therapy (01.01.2009)
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