Selection of Fluorescent, Bioluminescent, and Radioactive Tracers to Accurately Reflect Extracellular Vesicle Biodistribution in Vivo
Lázaro-Ibáñez, Elisa, Faruqu, Farid N, Saleh, Amer F, Silva, Andreia M, Tzu-Wen Wang, Julie, Rak, Janusz, Al-Jamal, Khuloud T, Dekker, Niek
Published in ACS nano (23.02.2021)
Published in ACS nano (23.02.2021)
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Journal Article
Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy
Hammond, Suzan M., Hazell, Gareth, Shabanpoor, Fazel, Saleh, Amer F., Bowerman, Melissa, Sleigh, James N., Meijboom, Katharina E., Zhou, Haiyan, Muntoni, Francesco, Talbot, Kevin, Gait, Michael J., Wood, Matthew J. A.
Published in Proceedings of the National Academy of Sciences - PNAS (27.09.2016)
Published in Proceedings of the National Academy of Sciences - PNAS (27.09.2016)
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Journal Article
Extracellular vesicles induce minimal hepatotoxicity and immunogenicity
Saleh, Amer F, Lázaro-Ibáñez, Elisa, Forsgard, Malin A-M, Shatnyeva, Olga, Osteikoetxea, Xabier, Karlsson, Fredrik, Heath, Nikki, Ingelsten, Madeleine, Rose, Jonathan, Harris, Jayne, Mairesse, Maelle, Bates, Stephanie M, Clausen, Maryam, Etal, Damla, Leonard, Emilyanne, Fellows, Mick D, Dekker, Niek, Edmunds, Nicholas
Published in Nanoscale (04.04.2019)
Published in Nanoscale (04.04.2019)
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Journal Article
Pip5 Transduction Peptides Direct High Efficiency Oligonucleotide-mediated Dystrophin Exon Skipping in Heart and Phenotypic Correction in mdx Mice
Yin, HaiFang, Saleh, Amer F, Betts, Corinne, Camelliti, Patrizia, Seow, Yiqi, Ashraf, Shirin, Arzumanov, Andrey, Hammond, Suzan, Merritt, Thomas, Gait, Michael J, Wood, Matthew JA
Published in Molecular therapy (01.07.2011)
Published in Molecular therapy (01.07.2011)
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Journal Article
Pip6-PMO, A New Generation of Peptide-oligonucleotide Conjugates With Improved Cardiac Exon Skipping Activity for DMD Treatment
Betts, Corinne, Saleh, Amer F, Arzumanov, Andrey A, Hammond, Suzan M, Godfrey, Caroline, Coursindel, Thibault, Gait, Michael J, Wood, Matthew JA
Published in Molecular therapy. Nucleic acids (01.08.2012)
Published in Molecular therapy. Nucleic acids (01.08.2012)
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Journal Article
Self-Assembly into Nanoparticles Is Essential for Receptor Mediated Uptake of Therapeutic Antisense Oligonucleotides
Ezzat, Kariem, Aoki, Yoshitsugu, Koo, Taeyoung, McClorey, Graham, Benner, Leif, Coenen-Stass, Anna, O’Donovan, Liz, Lehto, Taavi, Garcia-Guerra, Antonio, Nordin, Joel, Saleh, Amer F, Behlke, Mark, Morris, John, Goyenvalle, Aurelie, Dugovic, Branislav, Leumann, Christian, Gordon, Siamon, Gait, Michael J, El−Andaloussi, Samir, Wood, Matthew JA
Published in Nano letters (08.07.2015)
Published in Nano letters (08.07.2015)
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Journal Article
Identification of novel, therapy-responsive protein biomarkers in a mouse model of Duchenne muscular dystrophy by aptamer-based serum proteomics
Coenen-Stass, Anna M. L., McClorey, Graham, Manzano, Raquel, Betts, Corinne A., Blain, Alison, Saleh, Amer F., Gait, Michael J., Lochmüller, Hanns, Wood, Matthew J. A., Roberts, Thomas C.
Published in Scientific reports (23.11.2015)
Published in Scientific reports (23.11.2015)
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Journal Article
Improved Tat-mediated plasmid DNA transfer by fusion to LK15 peptide
Saleh, Amer F., Aojula, Harmesh, Arthanari, Yamini, Offerman, Shaun, Alkotaji, Myasar, Pluen, Alain
Published in Journal of controlled release (19.04.2010)
Published in Journal of controlled release (19.04.2010)
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Journal Article
Prevention of exercised induced cardiomyopathy following Pip-PMO treatment in dystrophic mdx mice
Betts, Corinne A., Saleh, Amer F., Carr, Carolyn A., Hammond, Suzan M., Coenen-Stass, Anna M. L., Godfrey, Caroline, McClorey, Graham, Varela, Miguel A., Roberts, Thomas C., Clarke, Kieran, Gait, Michael J., Wood, Matthew J. A.
Published in Scientific reports (11.03.2015)
Published in Scientific reports (11.03.2015)
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Journal Article
Bi-specific splice-switching PMO oligonucleotides conjugated via a single peptide active in a mouse model of Duchenne muscular dystrophy
Shabanpoor, Fazel, McClorey, Graham, Saleh, Amer F, Järver, Peter, Wood, Matthew J A, Gait, Michael J
Published in Nucleic Acids Research (01.01.2015)
Published in Nucleic Acids Research (01.01.2015)
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Combination Antisense Treatment for Destructive Exon Skipping of Myostatin and Open Reading Frame Rescue of Dystrophin in Neonatal mdx Mice
Lu-Nguyen, Ngoc B, Jarmin, Susan A, Saleh, Amer F, Popplewell, Linda, Gait, Michael J, Dickson, George
Published in Molecular therapy (01.08.2015)
Published in Molecular therapy (01.08.2015)
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Journal Article
Synthesis and Splice-Redirecting Activity of Branched, Arginine-Rich Peptide Dendrimer Conjugates of Peptide Nucleic Acid Oligonucleotides
Saleh, Amer F, Arzumanov, Andrey, Abes, Rachida, Owen, David, Lebleu, Bernard, Gait, Michael J
Published in Bioconjugate chemistry (20.10.2010)
Published in Bioconjugate chemistry (20.10.2010)
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Journal Article
2′-O-(2-Methoxyethyl) Nucleosides Are Not Phosphorylated or Incorporated Into the Genome of Human Lymphoblastoid TK6 Cells
Saleh, Amer F, Bachman, Martin, Priestley, Catherine C, Gooderham, Nigel J, Andersson, Patrik, Henry, Scott P, Edmunds, Nicholas J, Fellows, Mick D
Published in Toxicological sciences (01.05.2018)
Published in Toxicological sciences (01.05.2018)
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Journal Article
Optimization of Peptide Nucleic Acid Antisense Oligonucleotides for Local and Systemic Dystrophin Splice Correction in the mdx Mouse
Yin, HaiFang, Betts, Corinne, Saleh, Amer F, Ivanova, Gabriela D, Lee, Hyunil, Seow, Yiqi, Kim, Dalsoo, Gait, Michael J, Wood, Matthew JA
Published in Molecular therapy (01.04.2010)
Published in Molecular therapy (01.04.2010)
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Journal Article
Aflibercept or ranibizumab for diabetic macular edema
Ali Ali, Mahmoud Abdelhalim, Hegazy, Hanan Saied, Abdelkhalek Elsayed, Mohammed Othman, Tharwat, Ehab, Mansour, Mona Nabeh, Hassanein, Mohamed, Ezzeldin, Ezzeldin Ramadan, GadElkareem, Ashraf Mohammed, Abd Ellateef, Essam Mahmoud, Elsayed, Ahmed A, Elabd, Ibrahim Hassan, Abd Rbu, Mahmoud H, Amer, Ramy Saleh, Gabbar, Abdel Ghany Ali El, Mahmoud, Hatem, Abdelhameed, Hazem Mohamed, Abdelkader, Amr Mohammed Elsayed
Published in Medical hypothesis, discovery and innovation in ophthalmology (01.07.2024)
Published in Medical hypothesis, discovery and innovation in ophthalmology (01.07.2024)
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Journal Article
Diaphragm rescue alone prevents heart dysfunction in dystrophic mice
CRISP, Alastair, HAIFANG YIN, STUCKEY, Daniel J, CLARKE, Kieran, DAVIES, Kay E, WOOD, Matthew J. A, GOYENVALLE, Aurelie, BETTS, Corinne, MOULTON, Hong M, SEOW, Yiqi, BABBS, Arran, MERRITT, Thomas, SALEH, Amer F, GAIT, Michael J
Published in Human molecular genetics (01.02.2011)
Published in Human molecular genetics (01.02.2011)
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