Design and validation of cell-based potency assays for frataxin supplementation treatments
Mukherjee, Shibani, Pereboeva, Larisa, Fil, Daniel, Saikia, Achisha, Lee, Jeon, Li, Jixue, Cotticelli, M. Grazia, Soragni, Elisabetta, Wilson, Robert B., Napierala, Marek, Napierala, Jill S.
Published in Molecular therapy. Methods & clinical development (12.12.2024)
Published in Molecular therapy. Methods & clinical development (12.12.2024)
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