EPS7.2 Pharmacokinetics of oral MAC antibiotics in cystic fibrosis
Martiniano, S.L, Wagner, B.D, Brennan, L, Wempe, M.F, Anderson, P.L, Nick, J.A, Sagel, S.D
Published in Journal of cystic fibrosis (01.06.2017)
Published in Journal of cystic fibrosis (01.06.2017)
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Improvement in ion transport biomarkers and spirometry with the investigational CFTR potentiator VX-770 in subjects with cystic fibrosis and the G551D-CFTR mutation
Rowe, S.M, Accurso, F.J, Clancy, J.P, Boyle, M.P, Dunitz, J.M, Durie, P.R, Sagel, S.D, Hornick, D.B, Konstan, M.W, Donaldson, S.H, Moss, R.B, Pilewski, J.M, Rubenstein, R, Uluer, D.B, Aitken, M.L, Dong, Q, Ordonez, C.L, Campbell, P.W, Ashlock, M.A, Ramsey, B.W
Published in Paediatric respiratory reviews (2010)
Published in Paediatric respiratory reviews (2010)
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Final results of a 14- and 28-day study of VX-770 in subjects with CF
Accurso, F.J, Rowe, S.M, Durie, P.R, Konstan, M.W, Dunitz, J, Hornick, D.B, Sagel, S.D, Boyle, M.P, Uluer, A.Z, Moss, R.B, Ramsey, B.W, Freedman, S.D, Dong, Q, Zha, J, Stone, A.J, Olson, E.R, Ordonez, C.L, Clancy, J.P, Campbell, P.W, Ashlock, M.A
Published in Journal of cystic fibrosis (2009)
Published in Journal of cystic fibrosis (2009)
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Long term clinical effectiveness of ivacaftor in people with the G551D CFTR mutation
Guimbellot, J.S., Baines, A., Paynter, A., Heltshe, S.L., VanDalfsen, J., Jain, M., Rowe, S.M., Sagel, S.D.
Published in Journal of cystic fibrosis (01.03.2021)
Published in Journal of cystic fibrosis (01.03.2021)
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P185 Prospective randomized observational study validating biomarkers for association with future pulmonary exacerbations in people with cystic fibrosis
Liou, T.G., Argel, N., Asfour, F., Brown, P.S., Chatfield, B.A., Cox, D.R., Daines, C.L., Francis, J.A., Glover, B., Helms, M., Heynekamp, T., Hoidal, J.R., Jensen, J.L., Kartsonaki, C., Keogh, R., Kopecky, C., Lechtzin, N., Li, Y., Lysinger, J., Molina, O., Nakamura, C., Packer, K.A., Paine, R., Poch, K.R., Quittner, A.L., Radford, P., Redway, A., Sagel, S.D., Szczesniak, R.D., Sprandel, S., Taylor-Cousar, J.L., Vroom, J.B., Yoshikawa, R., Clancy, J.P., Elborn, S.J., Olivier, K.N., Adler, F.R.
Published in Journal of cystic fibrosis (01.06.2023)
Published in Journal of cystic fibrosis (01.06.2023)
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