Similar therapeutic efficacy between a single administration of gene therapy and multiple administrations of recombinant enzyme in a mouse model of lysosomal storage disease
Ferla, Rita, Claudiani, Pamela, Cotugno, Gabriella, Saccone, Paola, De Leonibus, Elvira, Auricchio, Alberto
Published in Human gene therapy (01.07.2014)
Published in Human gene therapy (01.07.2014)
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Phosphorylation of the AMPA receptor GluA1 subunit regulates memory load capacity
Olivito, Laura, Saccone, Paola, Perri, Valentina, Bachman, Julia L., Fragapane, Paola, Mele, Andrea, Huganir, Richard L., De Leonibus, Elvira
Published in Brain Structure and Function (01.01.2016)
Published in Brain Structure and Function (01.01.2016)
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A highly secreted sulphamidase engineered to cross the blood‐brain barrier corrects brain lesions of mice with mucopolysaccharidoses type IIIA
Sorrentino, Nicolina Cristina, D'Orsi, Luca, Sambri, Irene, Nusco, Edoardo, Monaco, Ciro, Spampanato, Carmine, Polishchuk, Elena, Saccone, Paola, De Leonibus, Elvira, Ballabio, Andrea, Fraldi, Alessandro
Published in EMBO molecular medicine (01.05.2013)
Published in EMBO molecular medicine (01.05.2013)
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Sensory-motor behavioral characterization of an animal model of Maroteaux-Lamy syndrome (or Mucopolysaccharidosis VI)
Saccone, Paola, Cotugno, Gabriella, Russo, Fabio, Mastrogiacomo, Rosa, Tessitore, Alessandra, Auricchio, Alberto, De Leonibus, Elvira
Published in Scientific reports (10.01.2014)
Published in Scientific reports (10.01.2014)
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