Safe, Long-term Hepatic Expression of Anti-HCV shRNA in a Nonhuman Primate Model
Suhy, David A, Kao, Shih-Chu, Mao, Tin, Whiteley, Laurence, Denise, Hubert, Souberbielle, Bernard, Burdick, Andrew D, Hayes, Kyle, Wright, J Fraser, Lavender, Helen, Roelvink, Peter, Kolykhalov, Alexander, Brady, Kevin, Moschos, Sterghios A, Hauck, Bernd, Zelenaia, Olga, Zhou, Shangzhen, Scribner, Curt, High, Katherine A, Renison, Sara H, Corbau, Romu
Published in Molecular therapy (01.09.2012)
Published in Molecular therapy (01.09.2012)
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Journal Article
BB-301: a silence and replace AAV-based vector for the treatment of oculopharyngeal muscular dystrophy
Strings-Ufombah, Vanessa, Malerba, Alberto, Kao, Shih-Chu, Harbaran, Sonal, Roth, Fanny, Cappellari, Ornella, Lu-Nguyen, Ngoc, Takahashi, Keiko, Mukadam, Sophie, Kilfoil, Georgina, Kloth, Claudia, Roelvink, Petrus, Dickson, George, Trollet, Capucine, Suhy, David
Published in Molecular therapy. Nucleic acids (04.06.2021)
Published in Molecular therapy. Nucleic acids (04.06.2021)
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Journal Article
In Vitro Characterization of the Activity of PF-05095808, a Novel Biological Agent for Hepatitis C Virus Therapy
Lavender, Helen, Brady, Kevin, Burden, Frances, Delpuech-Adams, Oona, Denise, Hubert, Palmer, Amy, Perkins, Hannah, Savic, Boris, Scott, Sarah, Smith-Burchnell, Caroline, Troke, Phil, Wright, J. Fraser, Suhy, David, Corbau, Romu
Published in Antimicrobial Agents and Chemotherapy (01.03.2012)
Published in Antimicrobial Agents and Chemotherapy (01.03.2012)
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Journal Article
Deep Sequencing Insights in Therapeutic shRNA Processing and siRNA Target Cleavage Precision
Denise, Hubert, Moschos, Sterghios A., Sidders, Benjamin, Burden, Frances, Perkins, Hannah, Carter, Nikki, Stroud, Tim, Kennedy, Michael, Fancy, Sally-Ann, Lapthorn, Cris, Lavender, Helen, Kinloch, Ross, Suhy, David, Corbau, Romu
Published in Molecular therapy. Nucleic acids (01.02.2014)
Published in Molecular therapy. Nucleic acids (01.02.2014)
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Journal Article
Abstract 2548: Preclinical development of EARLI-001, a genetic platform producing cancer-activated synthetic biomarkers for the early detection of malignancies
Ananthanarayanan, Badriprasad, Nieu, Regina, Bishop, Evan, Rudina, Shireen, Harwig, Alex, George, Bijee, Suhy, David
Published in Cancer research (Chicago, Ill.) (01.07.2021)
Published in Cancer research (Chicago, Ill.) (01.07.2021)
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Journal Article
1099. RNAi-Based Therapy for the Treatment of HCV
Couto, Linda B., Parker, Amy E., Haniff, Gabriel, Suhy, David A., Kolykhalov, Alexander A., Roelvink, Peter W., Maria Garcia, Luz, Schroeder, Rosanna, Kay, Mark A., Cunningham, Sara M.
Published in Molecular therapy (01.05.2006)
Published in Molecular therapy (01.05.2006)
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Journal Article
1034. Expression of Short Hairpin RNAs by Liver and Non Liver Specific RNA Pol II Expression Cassettes: What Governs Activity?
Suhy, David A., Kolykhalov, Alexander A., Couto, Linda B., Garcia, Luz-Maria, Schroeder, Annette R., Parker, Amy E., Haniff, Gabriel, Kay, Mark A., Roelvink, PeterW
Published in Molecular therapy (01.05.2006)
Published in Molecular therapy (01.05.2006)
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Journal Article
Established PABPN1 intranuclear inclusions in OPMD muscle can be efficiently reversed by AAV-mediated knockdown and replacement of mutant expanded PABPN1
Malerba, Alberto, Klein, Pierre, Lu-Nguyen, Ngoc, Cappellari, Ornella, Strings-Ufombah, Vanessa, Harbaran, Sonal, Roelvink, Peter, Suhy, David, Trollet, Capucine, Dickson, George
Published in Human molecular genetics (01.10.2019)
Published in Human molecular genetics (01.10.2019)
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Journal Article
Abstract 4311: Using multiomics analysis to identify dysregulated transcription factors in non-small cell lung cancer (NSCLC) to drive the expression of a cancer-activated synthetic biomarker
Zhang, Yue Wendy, Rudina, Shireen, Wodziak, Dariusz, Xia, Chloe, Louie, Maggie, Park, Albert, Suhy, David
Published in Cancer research (Chicago, Ill.) (04.04.2023)
Published in Cancer research (Chicago, Ill.) (04.04.2023)
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Journal Article
합성 바이오마커를 위한 개선된 방법 및 조성물
LIN JUSTIN, HARWIG ALEX, SUHY DAVID, HARTWELL LELAND HARRISON, ESCARPE PAUL, ROEDING CYRIAC, RUDINA SHIREEN
Year of Publication 15.01.2024
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Year of Publication 15.01.2024
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