Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function
Hoffman, Eric P, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Smith, Edward C, Castro, Diana, Mah, Jean K, McDonald, Craig M, Kuntz, Nancy L, Finkel, Richard S, Guglieri, Michela, Bushby, Katharine, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Smith, Andrea L, Morgenroth, Lauren P, Arrieta, Adrienne, Shimony, Maya, Siener, Catherine, Jaros, Mark, Shale, Phil, McCall, John M, Nagaraju, Kanneboyina, van den Anker, John, Conklin, Laurie S, Cnaan, Avital, Gordish-Dressman, Heather, Damsker, Jesse M, Clemens, Paula R
Published in Neurology (24.09.2019)
Published in Neurology (24.09.2019)
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Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial
Guglieri, Michela, Clemens, Paula R, Perlman, Seth J, Smith, Edward C, Horrocks, Iain, Finkel, Richard S, Mah, Jean K, Deconinck, Nicolas, Goemans, Nathalie, Haberlova, Jana, Straub, Volker, Mengle-Gaw, Laurel J, Schwartz, Benjamin D, Harper, Amy D, Shieh, Perry B, De Waele, Liesbeth, Castro, Diana, Yang, Michelle L, Ryan, Monique M, McDonald, Craig M, Tulinius, Mar, Webster, Richard, McMillan, Hugh J, Kuntz, Nancy L, Rao, Vashmi K, Baranello, Giovanni, Spinty, Stefan, Childs, Anne-Marie, Sbrocchi, Annie M, Selby, Kathryn A, Monduy, Migvis, Nevo, Yoram, Vilchez-Padilla, Juan J, Nascimento-Osorio, Andres, Niks, Erik H, de Groot, Imelda JM, Katsalouli, Marina, James, Meredith K, van den Anker, Johannes, Damsker, Jesse M, Ahmet, Alexandra, Ward, Leanne M, Jaros, Mark, Shale, Phil, Dang, Utkarsh J, Hoffman, Eric P
Published in Archives of neurology (Chicago) (01.10.2022)
Published in Archives of neurology (Chicago) (01.10.2022)
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Journal Article
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study
Smith, Edward C., Conklin, Laurie S., Hoffman, Eric P., Clemens, Paula R., Mah, Jean K., Finkel, Richard S., Guglieri, Michela, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M., Webster, Richard, Castro, Diana, Kuntz, Nancy L., Kerchner, Laurie, Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, Gordish-Dressman, Heather, Hagerty, Laura, Dang, Utkarsh J., Damsker, Jesse M., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., McDonald, Craig M.
Published in PLoS medicine (01.09.2020)
Published in PLoS medicine (01.09.2020)
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Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug
Conklin, Laurie S., Damsker, Jesse M., Hoffman, Eric P., Jusko, William J., Mavroudis, Panteleimon D., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., Smith, Edward C., Mah, Jean K., Guglieri, Michela, Nevo, Yoram, Kuntz, Nancy, McDonald, Craig M., Tulinius, Mar, Ryan, Monique M., Webster, Richard, Castro, Diana, Finkel, Richard S., Smith, Andrea L., Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, McCall, John M., Hathout, Yetrib, Nagaraju, Kanneboyina, van den Anker, John, Ward, Leanne M., Ahmet, Alexandra, Cornish, Michaelyn R., Clemens, Paula R.
Published in Pharmacological research (01.10.2018)
Published in Pharmacological research (01.10.2018)
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Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy: A Randomized Controlled Trial
Dang, Utkarsh J, Damsker, Jesse M, Guglieri, Michela, Clemens, Paula R, Perlman, Seth J, Smith, Edward C, Horrocks, Iain, Finkel, Richard S, Mah, Jean K, Deconinck, Nicolas, Goemans, Nathalie M, Haberlová, Jana, Straub, Volker, Mengle-Gaw, Laurel, Schwartz, Benjamin D, Harper, Amy, Shieh, Perry B, De Waele, Liesbeth, Castro, Diana, Yang, Michele L, Ryan, Monique M, McDonald, Craig M, Tulinius, Mar, Webster, Richard I, Mcmillan, Hugh J, Kuntz, Nancy, Rao, Vamshi K, Baranello, Giovanni, Spinty, Stefan, Childs, Anne-Marie, Sbrocchi, Annie M, Selby, Kathryn A, Monduy, Migvis, Nevo, Yoram, Vilchez, Juan J, Nascimento-Osorio, Andres, Niks, Erik H, De Groot, Imelda J M, Katsalouli, Marina, Van Den Anker, John N, Ward, Leanne M, Leinonen, Mika, D'Alessandro, Andrea L, Hoffman, Eric P
Published in Neurology (12.03.2024)
Published in Neurology (12.03.2024)
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Journal Article
Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial
Mah, Jean K, Clemens, Paula R, Guglieri, Michela, Smith, Edward C, Finkel, Richard S, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Castro, Diana, Kuntz, Nancy L, McDonald, Craig M, Damsker, Jesse M, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Jackowski, Stefan, Stimpson, Georgia, Ridout, Deborah A, Ayyar-Gupta, Vandana, Baranello, Giovanni, Manzur, Adnan Y, Muntoni, Francesco, Gordish-Dressman, Heather, Leinonen, Mika, Ward, Leanne M, Hoffman, Eric P, Dang, Utkarsh J
Published in JAMA network open (04.01.2022)
Published in JAMA network open (04.01.2022)
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Preliminary study of the safety and efficacy of SC-58635, a novel cyclooxygenase 2 inhibitor: efficacy and safety in two placebo-controlled trials in osteoarthritis and rheumatoid arthritis, and studies of gastrointestinal and platelet effects
Simon, L S, Lanza, F L, Lipsky, P E, Hubbard, R C, Talwalker, S, Schwartz, B D, Isakson, P C, Geis, G S
Published in Arthritis and rheumatism (01.09.1998)
Published in Arthritis and rheumatism (01.09.1998)
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A Peptidomimetic that Specifically Inhibits Human Leukocyte Antigen DRB10401-restricted T Cell Proliferation
Woulfe, S L, Bono, C P, Zacheis, M L, Welply, J K, Kirschmann, D A, Baudino, T A, Wang, Y, Stone, D A, Hanson, G J, Vuletich, J L, Bedell, L J, Schwartz, B D, Howard, S C
Published in The Journal of pharmacology and experimental therapeutics (01.05.1997)
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Published in The Journal of pharmacology and experimental therapeutics (01.05.1997)
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Efficacy and safety of tacrolimus in patients with rheumatoid arthritis: A double‐blind trial
Yocum, David E., Furst, Daniel E., Kaine, Jeffrey L., Baldassare, Andrew R., Stevenson, Jon T., Borton, Mary Ann, Mengle‐Gaw, Laurel J., Schwartz, Benjamin D., Wisemandle, Wayne, Mekki, Qais A.
Published in Arthritis and rheumatism (01.12.2003)
Published in Arthritis and rheumatism (01.12.2003)
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Tacrolimus in rheumatoid arthritis patients receiving concomitant methotrexate: A six-month, open-label study
KREMER, Joel M, HABROS, Joseph S, KOLBA, Karen S, KAINE, Jeffrey L, BORTON, Mary Ann, MENGLE-GAW, Laurel J, SCHWARTZ, Benjamin D, WISEMANDLE, Wayne, MEKKI, Qais A
Published in Arthritis and rheumatism (01.10.2003)
Published in Arthritis and rheumatism (01.10.2003)
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Journal Article
Isolation of H-2 Alloantigens Solubilized by the Detergent NP-40
Schwartz, Benjamin D, Nathenson, Stanley G
Published in The Journal of immunology (1950) (01.11.1971)
Published in The Journal of immunology (1950) (01.11.1971)
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Collagen-induced arthritis in the BB rat. Prevention of disease by treatment with CTLA-4-Ig
Knoerzer, D B, Karr, R W, Schwartz, B D, Mengle-Gaw, L J
Published in The Journal of clinical investigation (01.08.1995)
Published in The Journal of clinical investigation (01.08.1995)
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Journal Article
Isoelectric Focusing of Guinea Pig Ia Antigens
Schwartz, Benjamin D, Gordon, Diane, Thomas, David W
Published in The Journal of immunology (1950) (01.10.1978)
Published in The Journal of immunology (1950) (01.10.1978)
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Journal Article
Macrophage Ia Antigens
Cowing, Carol, Schwartz, Benjamin D., Dickler, Howard B.
Published in The Journal of immunology (1950) (01.02.1978)
Published in The Journal of immunology (1950) (01.02.1978)
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Journal Article
Structural Differences Between the Ia Antigens Determined by the I-A and I-C Subregions
Cullen, Susan E, Littman, Dan R, Schwartz, Benjamin D
Published in The Journal of immunology (1950) (01.10.1978)
Published in The Journal of immunology (1950) (01.10.1978)
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Journal Article
Labeling Characteristics and Separation of Ia Antigen Subunits
Schwartz, Benjamin D, Vitetta, Ellen S, Cullen, Susan E
Published in The Journal of immunology (1950) (01.02.1978)
Published in The Journal of immunology (1950) (01.02.1978)
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