CAR T cell manufacturing from naive/stem memory T lymphocytes enhances antitumor responses while curtailing cytokine release syndrome
Arcangeli, Silvia, Bove, Camilla, Mezzanotte, Claudia, Camisa, Barbara, Falcone, Laura, Manfredi, Francesco, Bezzecchi, Eugenia, El Khoury, Rita, Norata, Rossana, Sanvito, Francesca, Ponzoni, Maurilio, Greco, Beatrice, Moresco, Marta Angiola, Carrabba, Matteo G, Ciceri, Fabio, Bonini, Chiara, Bondanza, Attilio, Casucci, Monica
Published in The Journal of clinical investigation (15.06.2022)
Published in The Journal of clinical investigation (15.06.2022)
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Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1
Schiroli, Giulia, Ferrari, Samuele, Conway, Anthony, Jacob, Aurelien, Capo, Valentina, Albano, Luisa, Plati, Tiziana, Castiello, Maria C, Sanvito, Francesca, Gennery, Andrew R, Bovolenta, Chiara, Palchaudhuri, Rahul, Scadden, David T, Holmes, Michael C, Villa, Anna, Sitia, Giovanni, Lombardo, Angelo, Genovese, Pietro, Naldini, Luigi
Published in Science translational medicine (11.10.2017)
Published in Science translational medicine (11.10.2017)
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The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy
Montini, Eugenio, Cesana, Daniela, Schmidt, Manfred, Sanvito, Francesca, Bartholomae, Cynthia C, Ranzani, Marco, Benedicenti, Fabrizio, Sergi, Lucia Sergi, Ambrosi, Alessandro, Ponzoni, Maurilio, Doglioni, Claudio, Di Serio, Clelia, von Kalle, Christof, Naldini, Luigi
Published in The Journal of clinical investigation (01.04.2009)
Published in The Journal of clinical investigation (01.04.2009)
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Uncovering and Dissecting the Genotoxicity of Self-inactivating Lentiviral Vectors In Vivo
Cesana, Daniela, Ranzani, Marco, Volpin, Monica, Bartholomae, Cynthia, Duros, Caroline, Artus, Alexandre, Merella, Stefania, Benedicenti, Fabrizio, Sergi Sergi, Lucia, Sanvito, Francesca, Brombin, Chiara, Nonis, Alessandro, Serio, Clelia Di, Doglioni, Claudio, von Kalle, Christof, Schmidt, Manfred, Cohen-Haguenauer, Odile, Naldini, Luigi, Montini, Eugenio
Published in Molecular therapy (01.04.2014)
Published in Molecular therapy (01.04.2014)
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Insulin B chain 9-23 gene transfer to hepatocytes protects from type 1 diabetes by inducing Ag-specific FoxP3+ Tregs
Akbarpour, Mahzad, Goudy, Kevin S, Cantore, Alessio, Russo, Fabio, Sanvito, Francesca, Naldini, Luigi, Annoni, Andrea, Roncarolo, Maria Grazia
Published in Science translational medicine (27.05.2015)
Published in Science translational medicine (27.05.2015)
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Myeloid cell‐based delivery of IFN‐γ reprograms the leukemia microenvironment and induces anti‐tumoral immune responses
Mucci, Adele, Antonarelli, Gabriele, Caserta, Carolina, Vittoria, Francesco Maria, Desantis, Giacomo, Pagani, Riccardo, Greco, Beatrice, Casucci, Monica, Escobar, Giulia, Passerini, Laura, Lachmann, Nico, Sanvito, Francesca, Barcella, Matteo, Merelli, Ivan, Naldini, Luigi, Gentner, Bernhard
Published in EMBO molecular medicine (07.10.2021)
Published in EMBO molecular medicine (07.10.2021)
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Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy
Jofra Hernández, Raisa, Calabria, Andrea, Sanvito, Francesca, De Mattia, Fabiola, Farinelli, Giada, Scala, Serena, Visigalli, Ilaria, Carriglio, Nicola, De Simone, Maura, Vezzoli, Michela, Cecere, Francesca, Migliavacca, Maddalena, Basso-Ricci, Luca, Omrani, Maryam, Benedicenti, Fabrizio, Norata, Rossana, Rancoita, Paola Maria Vittoria, Di Serio, Clelia, Albertini, Paola, Cristofori, Patrizia, Naldini, Luigi, Gentner, Bernhard, Montini, Eugenio, Aiuti, Alessandro, Mortellaro, Alessandra
Published in Molecular therapy (06.01.2021)
Published in Molecular therapy (06.01.2021)
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Conditioning Regimens in Long-Term Pre-Clinical Studies to Support Development of Ex Vivo Gene Therapy: Review of Nonproliferative and Proliferative Changes
Chanut, Franck J A, Sanvito, Francesca, Ferrari, Giuliana, Visigalli, Ilaria, Carriglio, Nicola, Hernandez, Raisa Jofra, Norata, Rossana, Doglioni, Claudio, Naldini, Luigi, Cristofori, Patrizia
Published in Human gene therapy (01.01.2021)
Published in Human gene therapy (01.01.2021)
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A New Model of Chronic Mycobacterium abscessus Lung Infection in Immunocompetent Mice
Riva, Camilla, Tortoli, Enrico, Cugnata, Federica, Sanvito, Francesca, Esposito, Antonio, Rossi, Marco, Colarieti, Anna, Canu, Tamara, Cigana, Cristina, Bragonzi, Alessandra, Loré, Nicola Ivan, Miotto, Paolo, Cirillo, Daniela Maria
Published in International journal of molecular sciences (09.09.2020)
Published in International journal of molecular sciences (09.09.2020)
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Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model
Visigalli, Ilaria, Delai, Stefania, Politi, Letterio S., Di Domenico, Carmela, Cerri, Federica, Mrak, Emanuela, D'Isa, Raffaele, Ungaro, Daniela, Stok, Merel, Sanvito, Francesca, Mariani, Elisabetta, Staszewsky, Lidia, Godi, Claudia, Russo, Ilaria, Cecere, Francesca, del Carro, Ubaldo, Rubinacci, Alessandro, Brambilla, Riccardo, Quattrini, Angelo, Di Natale, Paola, Ponder, Katherine, Naldini, Luigi, Biffi, Alessandra
Published in Blood (09.12.2010)
Published in Blood (09.12.2010)
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Mitochondrial Ferritin Expression in Adult Mouse Tissues
Santambrogio, Paolo, Biasiotto, Giorgio, Sanvito, Francesca, Olivieri, Stefano, Arosio, Paolo, Levi, Sonia
Published in The journal of histochemistry and cytochemistry (01.11.2007)
Published in The journal of histochemistry and cytochemistry (01.11.2007)
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Generation of Human Induced Pluripotent Stem Cell‐Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy
Meneghini, Vasco, Frati, Giacomo, Sala, Davide, De Cicco, Silvia, Luciani, Marco, Cavazzin, Chiara, Paulis, Marianna, Mentzen, Wieslawa, Morena, Francesco, Giannelli, Serena, Sanvito, Francesca, Villa, Anna, Bulfone, Alessandro, Broccoli, Vania, Martino, Sabata, Gritti, Angela
Published in Stem cells translational medicine (01.02.2017)
Published in Stem cells translational medicine (01.02.2017)
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Preclinical evidence of a direct pro-survival role of arginine deprivation in multiple myeloma
Trudu, Matteo, Oliva, Laura, Orfanelli, Ugo, Romano, Alessandra, Di Raimondo, Francesco, Sanvito, Francesca, Ponzoni, Maurilio, Cenci, Simone
Published in Frontiers in oncology (08.09.2022)
Published in Frontiers in oncology (08.09.2022)
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New TMA (4,6,4'-Trimethyl angelicin) Analogues as Anti-Inflammatory Agents in the Treatment of Cystic Fibrosis Lung Disease
Tupini, Chiara, Chilin, Adriana, Rossi, Alice, De Fino, Ida, Bragonzi, Alessandra, D'Aversa, Elisabetta, Cosenza, Lucia Carmela, Vaccarin, Christian, Sacchetti, Gianni, Borgatti, Monica, Tamanini, Anna, Dechecchi, Maria Cristina, Sanvito, Francesca, Gambari, Roberto, Cabrini, Giulio, Lampronti, Ilaria
Published in International journal of molecular sciences (21.11.2022)
Published in International journal of molecular sciences (21.11.2022)
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Smooth muscle cells in human atherosclerotic plaques secrete and proliferate in response to high mobility group box 1 protein
Porto, Annalisa, Palumbo, Roberta, Pieroni, Maurizio, Aprigliano, Gianfranco, Chiesa, Roberto, Sanvito, Francesca, Maseri, Attilio, Bianchi, Marco E
Published in The FASEB journal (01.12.2006)
Published in The FASEB journal (01.12.2006)
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CXCR4 engagement triggers CD47 internalization and antitumor immunization in a mouse model of mesothelioma
Mezzapelle, Rosanna, De Marchis, Francesco, Passera, Chiara, Leo, Manuela, Brambilla, Francesca, Colombo, Federica, Casalgrandi, Maura, Preti, Alessandro, Zambrano, Samuel, Castellani, Patrizia, Ertassi, Riccardo, Silingardi, Marco, Caprioglio, Francesca, Basso, Veronica, Boldorini, Renzo, Carretta, Angelo, Sanvito, Francesca, Rena, Ottavio, Rubartelli, Anna, Sabatino, Lina, Mondino, Anna, Crippa, Massimo P, Colantuoni, Vittorio, Bianchi, Marco E
Published in EMBO molecular medicine (07.06.2021)
Published in EMBO molecular medicine (07.06.2021)
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Native CGRP Neuropeptide and Its Stable Analogue SAX, But Not CGRP Peptide Fragments, Inhibit Mucosal HIV-1 Transmission
Mariotton, Jammy, Sams, Anette, Cohen, Emmanuel, Sennepin, Alexis, Siracusano, Gabriel, Sanvito, Francesca, Edvinsson, Lars, Delongchamps, Nicolas Barry, Zerbib, Marc, Lopalco, Lucia, Bomsel, Morgane, Ganor, Yonatan
Published in Frontiers in immunology (08.12.2021)
Published in Frontiers in immunology (08.12.2021)
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Neutrophils predominate the immune signature of cerebral thrombi in COVID-19 stroke patients
Genchi, Angela, Semerano, Aurora, Schwarz, Ghil, Dell'Acqua, Beatrice, Gullotta, Giorgia Serena, Sampaolo, Michela, Boeri, Enzo, Quattrini, Angelo, Sanvito, Francesca, Diamanti, Susanna, Bergamaschi, Andrea, Grassi, Stefano, Podini, Paola, Panni, Pietro, Michelozzi, Caterina, Simionato, Franco, Scomazzoni, Francesco, Remida, Paolo, Valvassori, Luca, Falini, Andrea, Ferrarese, Carlo, Michel, Patrik, Saliou, Guillaume, Hajdu, Steven, Beretta, Simone, Roveri, Luisa, Filippi, Massimo, Strambo, Davide, Martino, Gianvito, Bacigaluppi, Marco
Published in Acta neuropathologica communications (01.02.2022)
Published in Acta neuropathologica communications (01.02.2022)
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In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of β-thalassemia
Miccio, Annarita, Cesari, Rossano, Lotti, Francesco, Rossi, Claudia, Sanvito, Francesca, Ponzoni, Maurilio, Routledge, Samantha J.E, Chow, Cheok-Man, Antoniou, Michael N, Ferrari, Giuliana
Published in Proceedings of the National Academy of Sciences - PNAS (29.07.2008)
Published in Proceedings of the National Academy of Sciences - PNAS (29.07.2008)
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External iliac artery endofibrosis in an elite female endurance cyclist
Bilman, Victor, Rinaldi, Enrico, Sanvito, Francesca, Melissano, Germano, Chiesa, Roberto
Published in Jornal vascular brasileiro (01.01.2021)
Published in Jornal vascular brasileiro (01.01.2021)
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