The effects of PEGylation on LNP based mRNA delivery to the eye
Ryals, Renee C, Patel, Siddharth, Acosta, Chris, McKinney, Madison, Pennesi, Mark E, Sahay, Gaurav
Published in PloS one (29.10.2020)
Published in PloS one (29.10.2020)
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Journal Article
Strategies for non-viral vectors targeting organs beyond the liver
Kim, Jeonghwan, Eygeris, Yulia, Ryals, Renee C, Jozić, Antony, Sahay, Gaurav
Published in Nature nanotechnology (01.04.2024)
Published in Nature nanotechnology (01.04.2024)
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Journal Article
Lipid nanoparticles for delivery of messenger RNA to the back of the eye
Patel, Siddharth, Ryals, Renee C, Weller, Kyle K, Pennesi, Mark E, Sahay, Gaurav
Published in Journal of controlled release (10.06.2019)
Published in Journal of controlled release (10.06.2019)
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Journal Article
Targeting photoreceptors via intravitreal delivery using novel, capsid-mutated AAV vectors
Kay, Christine N, Ryals, Renee C, Aslanidi, George V, Min, Seok Hong, Ruan, Qing, Sun, Jingfen, Dyka, Frank M, Kasuga, Daniel, Ayala, Andrea E, Van Vliet, Kim, Agbandje-McKenna, Mavis, Hauswirth, William W, Boye, Sanford L, Boye, Shannon E
Published in PloS one (26.04.2013)
Published in PloS one (26.04.2013)
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Journal Article
Lipid nanoparticles with PEG-variant surface modifications mediate genome editing in the mouse retina
Gautam, Milan, Jozic, Antony, Su, Grace Li-Na, Herrera-Barrera, Marco, Curtis, Allison, Arrizabalaga, Sebastian, Tschetter, Wayne, Ryals, Renee C, Sahay, Gaurav
Published in Nature communications (13.10.2023)
Published in Nature communications (13.10.2023)
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Journal Article
Thiophene-based lipids for mRNA delivery to pulmonary and retinal tissues
Eygeris, Yulia, Gupta, Mohit, Kim, Jeonghwan, Jozic, Antony, Gautam, Milan, Renner, Jonas, Nelson, Dylan, Bloom, Elissa, Tuttle, Adam, Stoddard, Jonathan, Reynaga, Rene, Neuringer, Martha, Lauer, Andreas K, Ryals, Renee C, Sahay, Gaurav
Published in Proceedings of the National Academy of Sciences - PNAS (12.03.2024)
Published in Proceedings of the National Academy of Sciences - PNAS (12.03.2024)
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Journal Article
The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9–dependent innate immune responses in the liver
Martino, Ashley T., Suzuki, Masataka, Markusic, David M., Zolotukhin, Irene, Ryals, Renee C., Moghimi, Babak, Ertl, Hildegund C.J., Muruve, Daniel A., Lee, Brendan, Herzog, Roland W.
Published in Blood (16.06.2011)
Published in Blood (16.06.2011)
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Journal Article
Long-term Characterization of Retinal Degeneration in Royal College of Surgeons Rats Using Spectral-Domain Optical Coherence Tomography
Ryals, Renee C, Andrews, Michael D, Datta, Shreya, Coyner, Aaron S, Fischer, Cody M, Wen, Yuquan, Pennesi, Mark E, McGill, Trevor J
Published in Investigative ophthalmology & visual science (01.03.2017)
Published in Investigative ophthalmology & visual science (01.03.2017)
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Journal Article
Peptide-guided lipid nanoparticles deliver mRNA to the neural retina of rodents and nonhuman primates
Herrera-Barrera, Marco, Ryals, Renee C, Gautam, Milan, Jozic, Antony, Landry, Madeleine, Korzun, Tetiana, Gupta, Mohit, Acosta, Chris, Stoddard, Jonathan, Reynaga, Rene, Tschetter, Wayne, Jacomino, Nick, Taratula, Oleh, Sun, Conroy, Lauer, Andreas K, Neuringer, Martha, Sahay, Gaurav
Published in Science advances (13.01.2023)
Published in Science advances (13.01.2023)
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Journal Article
Preformed Vesicle Approach to LNP Manufacturing Enhances Retinal mRNA Delivery
Eygeris, Yulia, Henderson, Michael I., Curtis, Allison G., Jozić, Antony, Stoddard, Jonathan, Reynaga, Rene, Chirco, Kathleen R., Su, Grace Li‐Na, Neuringer, Martha, Lauer, Andreas K., Ryals, Renee C., Sahay, Gaurav
Published in Small (Weinheim an der Bergstrasse, Germany) (13.05.2024)
Published in Small (Weinheim an der Bergstrasse, Germany) (13.05.2024)
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Journal Article
Monomethyl Fumarate Protects the Retina From Light-Induced Retinopathy
Jiang, Dan, Ryals, Renee C, Huang, Samuel J, Weller, Kyle K, Titus, Hope E, Robb, Bryan M, Saad, Firas W, Salam, Ribal A, Hammad, Hytham, Yang, Paul, Marks, Daniel L, Pennesi, Mark E
Published in Investigative ophthalmology & visual science (01.03.2019)
Published in Investigative ophthalmology & visual science (01.03.2019)
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Journal Article
Retinal Neuroprotective Effects of Flibanserin, an FDA-Approved Dual Serotonin Receptor Agonist-Antagonist
Coyner, Aaron S, Ryals, Renee C, Ku, Cristy A, Fischer, Cody M, Patel, Rachel C, Datta, Shreya, Yang, Paul, Wen, Yuquan, Hen, René, Pennesi, Mark E
Published in PloS one (22.07.2016)
Published in PloS one (22.07.2016)
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Journal Article
The Role of ERK1/2 Activation in Sarpogrelate-Mediated Neuroprotection
Ku, Cristy A, Ryals, Renee C, Jiang, Dan, Coyner, Aaron S, Weller, Kyle K, Sinha, Wrik, Robb, Bryan M, Yang, Paul, Pennesi, Mark E
Published in Investigative ophthalmology & visual science (01.01.2018)
Published in Investigative ophthalmology & visual science (01.01.2018)
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Journal Article
Spontaneous allelic variant in deafness–blindness gene Ush1g resulting in an expanded phenotype
Vartanian, Vladimir, Krey, Jocelyn F., Chatterjee, Paroma, Curtis, Allison, Six, Makayla, Rice, Sean P. M., Jones, Sherri M., Sampath, Harini, Allen, Charles N., Ryals, Renee C., Lloyd, R. Stephen, Barr‐Gillespie, Peter G.
Published in Genes, brain and behavior (01.08.2023)
Published in Genes, brain and behavior (01.08.2023)
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Journal Article
Natural history of cone disease in the murine model of Leber congenital amaurosis due to CEP290 mutation: determining the timing and expectation of therapy
Boye, Shannon E, Huang, Wei-Chieh, Roman, Alejandro J, Sumaroka, Alexander, Boye, Sanford L, Ryals, Renee C, Olivares, Melani B, Ruan, Qing, Tucker, Budd A, Stone, Edwin M, Swaroop, Anand, Cideciyan, Artur V, Hauswirth, William W, Jacobson, Samuel G
Published in PloS one (26.03.2014)
Published in PloS one (26.03.2014)
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Journal Article
Functional and behavioral restoration of vision by gene therapy in the guanylate cyclase-1 (GC1) knockout mouse
Boye, Shannon E, Boye, Sanford L, Pang, Jijing, Ryals, Renee, Everhart, Drew, Umino, Yumiko, Neeley, Andy W, Besharse, Joseph, Barlow, Robert, Hauswirth, William W
Published in PloS one (25.06.2010)
Published in PloS one (25.06.2010)
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Journal Article
An improved protocol for generation and characterization of human-induced pluripotent stem cell-derived retinal pigment epithelium cells
Surendran, Harshini, Soundararajan, Lalitha, Reddy K, Vijay Bhaskar, Subramani, Janavi, Stoddard, Jonathan, Reynaga, Rene, Tschetter, Wayne, Ryals, Renee C., Pal, Rajarshi
Published in STAR protocols (16.12.2022)
Published in STAR protocols (16.12.2022)
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Journal Article
Sarpogrelate, a 5-HT2A Receptor Antagonist, Protects the Retina From Light-Induced Retinopathy
Tullis, Brandon E, Ryals, Renee C, Coyner, Aaron S, Gale, Michael J, Nicholson, Alex, Ku, Cristy, Regis, Dain, Sinha, Wrik, Datta, Shreya, Wen, Yuquan, Yang, Paul, Pennesi, Mark E
Published in Investigative ophthalmology & visual science (01.07.2015)
Published in Investigative ophthalmology & visual science (01.07.2015)
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Journal Article