Target therapy for high-risk neuroblastoma treatment: integration of regulatory and scientific tools is needed
Ceci, Adriana, Conte, Rosa, Didio, Antonella, Landi, Annalisa, Ruggieri, Lucia, Giannuzzi, Viviana, Bonifazi, Fedele
Published in Frontiers in medicine (14.07.2023)
Published in Frontiers in medicine (14.07.2023)
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Journal Article
Small-Molecule Protein-Protein Interaction Inhibitor of Oncogenic Rho Signaling
Diviani, Dario, Raimondi, Francesco, Del Vescovo, Cosmo D., Dreyer, Elisa, Reggi, Erica, Osman, Halima, Ruggieri, Lucia, Gonano, Cynthia, Cavin, Sabrina, Box, Clare L., Lenoir, Marc, Overduin, Michael, Bellucci, Luca, Seeber, Michele, Fanelli, Francesca
Published in Cell chemical biology (22.09.2016)
Published in Cell chemical biology (22.09.2016)
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Journal Article
PedCRIN tool for the biosamples management in pediatric clinical trials
Giannuzzi, Viviana, Ruggieri, Lucia, Conte, Rosa, Manfredi, Cristina, Felisi, Mariagrazia, Kubiak, Christine, Matei, Mihaela, Malik, Salma, Demotes, Jacques, Ceci, Adriana, Bonifazi, Donato
Published in Clinical and translational science (01.05.2023)
Published in Clinical and translational science (01.05.2023)
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Journal Article
Paediatric clinical research in Europe: an insight on experts’ needs and perspectives
Ruggieri, Lucia, Ceci, Adriana, Bartoloni, Franco, Elie, Valèry, Felisi, Mariagrazia, Jacqz-Aigrain, Evelyne, Lupo, Mariangela, Malik, Salma, Manfredi, Cristina, Reggiardo, Giorgio, Demotes, Jacques, Bonifazi, Donato
Published in Contemporary clinical trials communications (01.03.2021)
Published in Contemporary clinical trials communications (01.03.2021)
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Journal Article
Paediatric extrapolation: A necessary paradigm shift
Ollivier, Cécile, Mulugeta, Yeruk (Lily), Ruggieri, Lucia, Saint‐Raymond, Agnes, Yao, Lynne
Published in British journal of clinical pharmacology (01.04.2019)
Published in British journal of clinical pharmacology (01.04.2019)
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Journal Article
IMMU-15. PHASE I TRIAL OF GD2.CART-CELLS AUGMENTED WITH A CONSTITUTIVELY ACTIVE INTERLEUKIN-7 RECEPTOR (C7R) FOR TREATMENT OF HIGH-GRADE PEDIATRIC CNS TUMORS
Lin, Frank, Stuckert, Austin, Tat, Candise, Moeller, Karen, White, Mark, Ruggieri, Lucia, Zhang, Huimin, Lindsay, Holly, Baxter, Patricia, Malbari, Fatema, Aldave, Guillermo, Chintagumpala, Murali, Parsons, D Williams, Brenner, Malcolm, Heslop, Helen, Rooney, Cliona, Omer, Bilal
Published in Neuro-oncology (Charlottesville, Va.) (12.06.2023)
Published in Neuro-oncology (Charlottesville, Va.) (12.06.2023)
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Journal Article
Phase I Trial of GD2.CART Cells Augmented With Constitutive Interleukin-7 Receptor for Treatment of High-Grade Pediatric CNS Tumors
Lin, Frank Y, Stuckert, Austin, Tat, Candise, White, Mark, Ruggieri, Lucia, Zhang, Huimin, Mehta, Birju, Lapteva, Natalia, Mei, Zhuyong, Major, Angela, Thakkar, Sachin, Shum, Thomas, Parikh, Kathan, Wu, Meng-Fen, Lindsay, Holly B, Scherer, Lauren, Shekar, Meghan, Baxter, Patricia, Wang, Tao, Grilley, Bambi, Moeller, Karen, Hicks, John, Roy, Angshumoy, Anastas, Jamie, Malbari, Fatema, Aldave, Guillermo, Chintagumpala, Murali, Blaney, Susan, Parsons, D Williams, Brenner, Malcolm K, Heslop, Helen E, Rooney, Cliona M, Omer, Bilal
Published in Journal of clinical oncology (10.08.2024)
Published in Journal of clinical oncology (10.08.2024)
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Journal Article
Clinical Trial Application in Europe: What Will Change with the New Regulation?
Giannuzzi, Viviana, Altavilla, Annagrazia, Ruggieri, Lucia, Ceci, Adriana
Published in Science and engineering ethics (01.04.2016)
Published in Science and engineering ethics (01.04.2016)
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Journal Article
Magnetic resonance-guided laser interstitial thermal therapy for pediatric periventricular nodular heterotopia-related epilepsy
Ravindra, Vijay M, Lee, Sungho, Gonda, David, Patino, Ilana, Ruggieri, Lucia, Ikeda, Daniel S, Curry, Daniel J
Published in Journal of neurosurgery. Pediatrics (01.12.2021)
Published in Journal of neurosurgery. Pediatrics (01.12.2021)
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Journal Article
Comparison of neurocognitive and quality-of-life outcomes in pediatric craniopharyngioma patients treated with partial resection and radiotherapy versus gross-total resection only
Aldave, Guillermo, Okcu, M Fatih, Chintagumpala, Murali, Ruggieri, Lucia, Minard, Charles G, Malbari, Fatema, Mash, Lisa E, Paulino, Arnold C, McGovern, Susan, Ramaswamy, Uma, Whitehead, William, Kahalley, Lisa S
Published in Journal of neurosurgery. Pediatrics (01.05.2023)
Published in Journal of neurosurgery. Pediatrics (01.05.2023)
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Comparison of multimodal surgical and radiation treatment methods for pediatric craniopharyngioma: long-term analysis of progression-free survival and morbidity
Ravindra, Vijay M, Okcu, M Fatih, Ruggieri, Lucia, Frank, Thomas S, Paulino, Arnold C, McGovern, Susan L, Horne, Vincent E, Dauser, Robert C, Whitehead, William E, Aldave, Guillermo
Published in Journal of neurosurgery. Pediatrics (01.08.2021)
Published in Journal of neurosurgery. Pediatrics (01.08.2021)
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Pattern of complications and burden of disease in patients affected by beta thalassemia major
Bonifazi, Fedele, Conte, Rosa, Baiardi, Paola, Bonifazi, Donato, Felisi, Mariagrazia, Giordano, Paola, Giannuzzi, Viviana, Iacono, Angela, Padula, Rosa, Pepe, Alessia, Caterina Putti, Maria, Ruggieri, Lucia, Carlo Del Vecchio, Giovanni, Filosa, Aldo, Maggio, Aurelio, Ceci, Adriana
Published in Current medical research and opinion (03.08.2017)
Published in Current medical research and opinion (03.08.2017)
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Survey by TEDDY European Network of Excellence for Paediatric Clinical Research demonstrates potential for Europe‐wide trials
Ruggieri, Lucia, Bonifazi, Donato, Landi, Annalisa, Bonifazi, Fedele, Bartoloni, Franco, Costello, Mary, Felisi, Maria Grazia, Gasthuys, Elke, Godo, Anila, Martinon Torres, Federico, Nadal, David, Nuytinck, Lieve, Rocchi, Francesca, Turner, Mark, Ceci, Adriana
Published in Acta Paediatrica (01.03.2020)
Published in Acta Paediatrica (01.03.2020)
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Journal Article
Off-label is not always off-evidence: authorising paediatric indications for old medicines
de Wildt, Saskia N, Foeldvari, Ivan, Siapkara, Angeliki, Lepola, Pirkko, Kriström, Berit, Ruggieri, Lucia, Eichler, Irmgard, Egger, Gunter F
Published in The lancet child & adolescent health (01.06.2023)
Published in The lancet child & adolescent health (01.06.2023)
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Journal Article
An Initial Experience of Completion Hemispherotomy via Magnetic Resonance-Guided Laser Interstitial Therapy
Ravindra, Vijay M, Ruggieri, Lucia, Gadgil, Nisha, Addison, Angela P, Patino, Ilana, Gonda, David D, Chu, Jason, Whitehead, Laura, Anderson, Anne, Diaz-Medina, Gloria, Houck, Kimberly, Katyayan, Akshat, Masters, Laura, Nath, Audrey, Quach, Michael, Riviello, James John, Seto, Elaine, Sully, Krystal Elizabeth, Agurs, Latanya, Sen, Sonali, Handoko, Maureen, Coorg, Rohini, Ali, Irfan, Ikeda, Daniel, Weiner, Howard, Curry, Daniel J
Published in Stereotactic and functional neurosurgery (01.06.2023)
Published in Stereotactic and functional neurosurgery (01.06.2023)
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Pediatric neurosurgery at Texas Children's Hospital: the legacy of Dr. William R. Cheek
Gadgil, Nisha, Rao, Ganesh, Sawaya, Raymond, Yoshor, Daniel, Ruggieri, Lucia, Cormier, Natalie, Curry, Daniel J, Whitehead, William E, Aldave, Guillermo, Bauer, David F, McClugage, Samuel, Weiner, Howard L
Published in Journal of neurosurgery. Pediatrics (01.07.2021)
Published in Journal of neurosurgery. Pediatrics (01.07.2021)
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Journal Article
119 - GD2.CAR T Cells Incorporating a Constitutively Active Interleukin-7 Signal Modulator for CNS Tumors
Lin, Frank Y, Stuckert, Austin, Tat, Candise, White, Mark, Ruggieri, Lucia, Zhang, Huimin, Lindsay, Holly, Baxter, Patricia, Malbari, Fatema, Aldave, Guillermo, Chintagumpala, Murali, Brenner, Malcolm K., Heslop, Helen E., Rooney, Cliona M., Omer, Bilal
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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Journal Article
GD2.CAR T Cells Incorporating a Constitutively Active Interleukin-7 Signal Modulator for CNS Tumors
Lin, Frank Y, Stuckert, Austin, Tat, Candise, White, Mark, Ruggieri, Lucia, Zhang, Huimin, Lindsay, Holly, Baxter, Patricia, Malbari, Fatema, Aldave, Guillermo, Chintagumpala, Murali, Brenner, Malcolm K., Heslop, Helen E., Rooney, Cliona M., Omer, Bilal
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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Journal Article
Salvage sacrococcygeal resection for yolk sac tumors after chemotherapy: report of 2 cases
Ravindra, Vijay M, Ruggieri, Lucia, Vasudevan, Sanjeev A, Hicks, M John, Muscal, Jodi A, Quintanilla, Norma M, Schady, Deborah A, Aldave, Guillermo
Published in Journal of neurosurgery. Pediatrics (01.01.2020)
Published in Journal of neurosurgery. Pediatrics (01.01.2020)
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