PMU46 Impact of Assumptions Used in Cost-Effectiveness Analysis (CEA) on the Outcomes of CEA across Disease Areas
Holmes, H., Mahon, J., McGarry, L., Bromilow, T., Thorat, T., Wood, H., Rubin, J.L.
Published in Value in health (01.06.2021)
Published in Value in health (01.06.2021)
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PRS31 Modelling Survival of People with Cystic Fibrosis (PWCF) Aged ≥12 YEARS Homozygous for the F508DEL Mutation Treated with Ivacaftor/Tezacaftor/Elexacaftor and Ivacaftor (IVA/TEZ/ELX)
Vega-Hernandez, G., MacGregor, G., Lopez, A., Daly, C., Rubin, J.L.
Published in Value in health (01.06.2021)
Published in Value in health (01.06.2021)
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PRS2 Modelling Survival of People with Cystic Fibrosis (PWCF) Aged ≥12 YEARS Heterozygous for the F508DEL Mutation with a Minimal Function Mutation Treated with Ivacaftor/Tezacaftor/Elexacaftor and Ivacaftor (IVA/TEZ/ELX)
Vega-Hernandez, G., MacGregor, G., Lopez, A., Daly, C., Rubin, J.L.
Published in Value in health (01.06.2021)
Published in Value in health (01.06.2021)
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191 Lung function and health care resource utilization in patients with cystic fibrosis
Rubin-Cahill, J.L, Thayer, S, Watkins, A, Wagener, J, Hodgkins, P, Schechter, M.S
Published in Journal of cystic fibrosis (01.06.2015)
Published in Journal of cystic fibrosis (01.06.2015)
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MS1 VALIDATION OF MODELED 5-YEAR SURVIVAL OUTCOMES AMONG PATIENTS WITH CYSTIC FIBROSIS (CF) TREATED WITH THE CF TRANSMEMBRANE CONDUCTANCE REGULATOR MODULATOR (CFTRM) IVACAFTOR USING US CF FOUNDATION PATIENT REGISTRY (USCFFPR) DATA
Mcgarry, L., Lopez, A., Chandler, C., Pelligra, C., Alkhateeb, Z., Rubin, J.L., Liou, T.
Published in Value in health (01.05.2020)
Published in Value in health (01.05.2020)
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PRO117 ACCESS TO ORPHAN DRUGS IN THE UNITED KINGDOM: A REVIEW OF NICE DECISIONS FROM 2017-2018
Thorat, T., Sliman, R.C., Farinella, M., Vega, G., Jao, R., Kumar, J., Rubin, J.L.
Published in Value in health (01.11.2019)
Published in Value in health (01.11.2019)
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P067 Hospitalisations among children with cystic fibrosis aged <6 years
Thorat, T., Hassan, M., Bonafede, M., Limone, B., McGarry, L., Rubin, J.L.
Published in Journal of cystic fibrosis (01.06.2019)
Published in Journal of cystic fibrosis (01.06.2019)
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